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1دورية أكاديمية
المؤلفون: Michela Lisjak, Alessia De Caneva, Thibaut Marais, Elena Barbon, Maria Grazia Biferi, Fabiola Porro, Adi Barzel, Lorena Zentilin, Mark A. Kay, Federico Mingozzi, Andrés F. Muro
المصدر: Frontiers in Genome Editing, Vol 4 (2022)
مصطلحات موضوعية: GeneRide, albumin gene targeting, mouse model, coagulation factor IX, tail clip test, CRISPR/SaCas9, Biotechnology, TP248.13-248.65, Genetics, QH426-470
وصف الملف: electronic resource
العلاقة: https://www.frontiersin.org/articles/10.3389/fgeed.2022.785698/fullTest; https://doaj.org/toc/2673-3439Test
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2صورة
المؤلفون: Michela Lisjak, Alessia De Caneva, Thibaut Marais, Elena Barbon, Maria Grazia Biferi, Fabiola Porro, Adi Barzel, Lorena Zentilin, Mark A. Kay, Federico Mingozzi, Andrés F. Muro
مصطلحات موضوعية: Genetics, Molecular Biology, Genetic Engineering, Molecular Medicine, Gene and Molecular Therapy, GeneRide, albumin gene targeting, mouse model, coagulation factor IX, tail clip test, CRISPR/SaCas9
الإتاحة: https://doi.org/10.3389/fgeed.2022.785698.s001Test
https://figshare.com/articles/figure/Image1_Promoterless_Gene_Targeting_Approach_Combined_to_CRISPR_Cas9_Efficiently_Corrects_Hemophilia_B_Phenotype_in_Neonatal_Mice_tiff/19343618Test -
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المؤلفون: Michela Lisjak, Alessia De Caneva, Thibaut Marais, Elena Barbon, Maria Grazia Biferi, Fabiola Porro, Adi Barzel, Lorena Zentilin, Mark A. Kay, Federico Mingozzi, Andrés F. Muro
مصطلحات موضوعية: Genetics, Molecular Biology, Genetic Engineering, Molecular Medicine, Gene and Molecular Therapy, GeneRide, albumin gene targeting, mouse model, coagulation factor IX, tail clip test, CRISPR/SaCas9
الإتاحة: https://doi.org/10.3389/fgeed.2022.785698.s006Test
https://figshare.com/articles/dataset/Table1_Promoterless_Gene_Targeting_Approach_Combined_to_CRISPR_Cas9_Efficiently_Corrects_Hemophilia_B_Phenotype_in_Neonatal_Mice_pdf/19343648Test