دورية أكاديمية
P005: Head-to-head trial of pegunigalsidase alfa vs agalsidase beta in Fabry disease: Phase 3 randomized, double-blind, BALANCE Study 2-year results
العنوان: | P005: Head-to-head trial of pegunigalsidase alfa vs agalsidase beta in Fabry disease: Phase 3 randomized, double-blind, BALANCE Study 2-year results |
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المؤلفون: | John Bernat, Eric Wallace, Ozlem Goker-Alpan, William Wilcox, Myrl Holida, Nicola Longo, Derralynn Hughes, Pilar Giraldo, Maria Molnar, Damara Ortiz, Robert Hopkin, Camilla Tondel, Ales Linhart, Patrick Deegan, Ana Jovanovic, Michael Muriello, Bruce Barshop, Virginia Kimonis, Bojan Vujkovac, Albina Nowak, Tarekegn Hiwot, Antonio Pisani, Dominique Germain, Ilkka Kantola, Jasmine Knoll, Ankit Mehta, Stephen Waldek, Einat Almon, Sari Alon, Raul Chertkoff, Rossana Rocco, David Warnock |
المصدر: | Genetics in Medicine Open, Vol 1, Iss 1, Pp 100015- (2023) |
بيانات النشر: | Elsevier, 2023. |
سنة النشر: | 2023 |
المجموعة: | LCC:Genetics LCC:Medicine |
مصطلحات موضوعية: | Genetics, QH426-470, Medicine |
نوع الوثيقة: | article |
وصف الملف: | electronic resource |
اللغة: | English |
تدمد: | 2949-7744 |
العلاقة: | http://www.sciencedirect.com/science/article/pii/S2949774423000158Test; https://doaj.org/toc/2949-7744Test |
DOI: | 10.1016/j.gimo.2023.100015 |
الوصول الحر: | https://doaj.org/article/343c76656a104fd8b64b93bc346cad1bTest |
رقم الانضمام: | edsdoj.343c76656a104fd8b64b93bc346cad1b |
قاعدة البيانات: | Directory of Open Access Journals |
تدمد: | 29497744 |
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DOI: | 10.1016/j.gimo.2023.100015 |