المؤلفون: Edward M. Kaye, K. Berry, Nathalie Goemans, Lindsay N. Alfano, Eugenio Mercuri, James Shao, Linda Lowes, Jerry R. Mendell

المصدر: Annals of Neurology. 79:257-271

مصطلحات موضوعية: 0301 basic medicine, medicine.medical_specialty, business.industry, Duchenne muscular dystrophy, medicine.disease, Placebo, Eteplirsen, Exon skipping, Pulmonary function testing, Surgery, 03 medical and health sciences, 030104 developmental biology, 0302 clinical medicine, Neurology, Internal medicine, Ambulatory, medicine, Respiratory muscle, Neurology (clinical), Muscular dystrophy, business, 030217 neurology & neurosurgery

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::1e574246330f394154357efdef7a73caTest
https://doi.org/10.1002/ana.24555Test

المؤلفون: Gunnar M. Buyse, Marleen Van den Hauwe, Thomas Meier, Nathalie Goemans

المصدر: Pediatric Pulmonology. 48:912-920

مصطلحات موضوعية: Pulmonary and Respiratory Medicine, medicine.medical_specialty, education.field_of_study, Vital capacity, business.industry, Duchenne muscular dystrophy, Population, medicine.disease, Placebo, Surgery, FEV1/FVC ratio, Internal medicine, Concomitant, Pediatrics, Perinatology and Child Health, medicine, Cardiology, Idebenone, Respiratory function, business, education, medicine.drug

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::49968df2208de4a9df7347f998cba24fTest
https://doi.org/10.1002/ppul.22688Test

المؤلفون: Gunnar M. Buyse, Imelda J. M. de Groot, Daisy Thijs, Berten Ceulemans, Ulrike Schara, Marleen Van den Hauwe, Nathalie Goemans, Thomas Meier, Luc Mertens

المصدر: Neuromuscular disorders
Neuromuscular Disorders, 21, 396-405
Neuromuscular Disorders, 21, 6, pp. 396-405

مصطلحات موضوعية: Male, musculoskeletal diseases, medicine.medical_specialty, Human Movement & Fatigue DCN 1: Perception and Action [NCEBP 10], Adolescent, Ubiquinone, Duchenne muscular dystrophy, Vital Capacity, Placebo-controlled study, Medizin, Placebo, Antioxidants, law.invention, Randomized controlled trial, Double-Blind Method, law, Forced Expiratory Volume, Natriuretic Peptide, Brain, medicine, Idebenone, Humans, Respiratory function, Longitudinal Studies, Muscle Strength, Child, Genetics (clinical), Dose-Response Relationship, Drug, business.industry, Troponin I, medicine.disease, Surgery, Clinical trial, Muscular Dystrophy, Duchenne, Treatment Outcome, Neurology, Tolerability, Anesthesia, Pediatrics, Perinatology and Child Health, Disease Progression, Human Movement & Fatigue Perception and Action [NCEBP 10], Neurology (clinical), Human medicine, business, medicine.drug

وصف الملف: pdf

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::58169882307d3fa2793715c30e602010Test
https://hdl.handle.net/2066/95981Test

المؤلفون: E. Bertini, Anna Lusakowska, L. H. van den Berg, W. Hauke, Bruno Scherrer, P. Berna, C. André, Janbernd Kirschner, Nathalie Goemans, Eugenio Mercuri, Gianluca Vita, M. Mayer, Brigitte Estournet, Brigitte Chabrol, M. Walter, R. Pruss, S. Fontaine-Carbonel, Ulrike Schara, Ksenija Gorni, Claudio Bruno, Wolfgang Müller-Felber, Francesco Muntoni, Nicolas Deconinck, H. Roper, François Rivier, G. Comi, Jean-Marie Cuisset, Eric Dessaud, Hanns Lochmüller, V. Cuvier

المصدر: Neuromuscular Disorders. 24:920-921

مصطلحات موضوعية: medicine.medical_specialty, business.industry, Spinal muscular atrophy, medicine.disease, Placebo, SMA, Surgery, Pulmonary function testing, Clinical trial, chemistry.chemical_compound, Neurology, chemistry, Anesthesia, Pediatrics, Perinatology and Child Health, medicine, Clinical endpoint, Olesoxime, Neurology (clinical), Adverse effect, business, Genetics (clinical)

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::64e01fd40621b2987e5b259c21980ef2Test
https://doi.org/10.1016/j.nmd.2014.06.418Test

المؤلفون: T. Voit, C. Wardell, Nathalie Goemans, G. Campion, Eugenio Mercuri, R. Wilson, C. McDonald

المصدر: Neuromuscular Disorders. 24:922

مصطلحات موضوعية: Moderate to severe, medicine.medical_specialty, education.field_of_study, Proteinuria, business.industry, Disease progression, Population, Phases of clinical research, Placebo, Gastroenterology, Surgery, Walking distance, Neurology, Internal medicine, Pediatrics, Perinatology and Child Health, Medicine, Neurology (clinical), medicine.symptom, business, education, Mild disease, Genetics (clinical)

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::b5385ac1d904ef9910e18ec3d2d93465Test
https://doi.org/10.1016/j.nmd.2014.06.422Test

المؤلفون: Hermien E. Kan, G. Campion, Erik H. Niks, B.H.A. Wokke, Nathalie Goemans, J.J.G. Verschuuren, Melissa T. Hooijmans

المصدر: Neuromuscular Disorders. 24:852

مصطلحات موضوعية: Muscle tissue, medicine.medical_specialty, business.industry, Duchenne muscular dystrophy, Urology, medicine.disease, Placebo, Exon skipping, Surgery, medicine.anatomical_structure, Neurology, Tibialis anterior muscle, Pediatrics, Perinatology and Child Health, medicine, Clinical endpoint, Biomarker (medicine), Neurology (clinical), business, Genetics (clinical), Drisapersen

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::a4191817da722bd72af1ea7da116a235Test
https://doi.org/10.1016/j.nmd.2014.06.199Test