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1دورية أكاديمية
المؤلفون: Craven, Claudia L, Gissen, Paul, Bower, Rebecca, Lee, Laura, Aquilina, Kristian, Thompson, Dominic NP
المصدر: Journal of Neurosurgery: Pediatrics , 29 (1) pp. 115-121. (2022)
مصطلحات موضوعية: Cerliponase alfa, intracerebroventricular, drug delivery, neurosurgery, neuronal ceroid lipofuscinosis, ventricular access devices, punctures, complications, surgical technique
وصف الملف: text
العلاقة: https://discovery.ucl.ac.uk/id/eprint/10145763/2/Gissen_Battens%20manuscript.pdfTest; https://discovery.ucl.ac.uk/id/eprint/10145763Test/
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2دورية أكاديمية
المؤلفون: Iwan, Katharina, Patel, Nina, Heslegrave, Amanda, Borisova, Mina, Lee, Laura, Bower, Rebecca, Mole, Sara E, Mills, Philippa B, Zetterberg, Henrik, Mills, Kevin, Gissen, Paul, Heywood, Wendy E
المصدر: F1000Research , 10 , Article 614. (2021)
مصطلحات موضوعية: Neuronal Ceroid lipofuscinosis, Enzyme replacement therapy, Neurofilament light
وصف الملف: text
العلاقة: https://discovery.ucl.ac.uk/id/eprint/10143137/1/Heywood_Cerebrospinal%20fluid%20neurofilament%20light%20chain%20levels%20in%20CLN2%20disease%20patients%20treated%20with%20enzyme%20replacement%20therapy%20normalise%20after%20two%20years%20on%20treatment_VoR.pdfTest; https://discovery.ucl.ac.uk/id/eprint/10143137Test/
الإتاحة: https://discovery.ucl.ac.uk/id/eprint/10143137/1/Heywood_Cerebrospinal%20fluid%20neurofilament%20light%20chain%20levels%20in%20CLN2%20disease%20patients%20treated%20with%20enzyme%20replacement%20therapy%20normalise%20after%20two%20years%20on%20treatment_VoR.pdfTest
https://discovery.ucl.ac.uk/id/eprint/10143137Test/