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المؤلفون: David Adams, Michael Polydefkis, Alejandra González-Duarte, Jonas Wixner, Arnt V Kristen, Hartmut H Schmidt, John L Berk, Inés Asunción Losada López, Angela Dispenzieri, Dianna Quan, Isabel M Conceição, Michel S Slama, Julian D Gillmore, Theodoros Kyriakides, Senda Ajroud-Driss, Márcia Waddington-Cruz, Michelle M Mezei, Violaine Planté-Bordeneuve, Shahram Attarian, Elizabeth Mauricio, Thomas H Brannagan, Mitsuharu Ueda, Emre Aldinc, Jing Jing Wang, Matthew T White, John Vest, Erhan Berber, Marianne T Sweetser, Teresa Coelho, Giuseppe Vita, Vincenzo Rizzo, Massimo Russo, Anna Mazzeo, Luca Gentile, Caitlin Brueckner, Victoria Lazzari, Janice Wiesman, Douglas DeLong, Jennifer Victory, James Dalton, John May, Catherine Gilmore, Saran Diallo, Emilien Delmont, Jean Pouget, Annie Verschueren, Aude-Marie Grapperon, Emmanuelle Campana-Salort, Ana Lopes, Filipa Lamas, Carlos Neves, Jose Castro, Pedro Pereira, Isabel Castro, Ana Franco, Miguel Oliveira Santos, Conceição de Azevedo Coutinho, Catarina Falcao de Campos, Antonio Hipólito Reis, Nuno Correia, Javier M Perez, Ana Martins da Silva, Cristina Alves, Marcio Cardoso, Katia Valdrez, Julia R Monte, Bernardete Pessoa, Nadia Guimaraes, Monica Freitas, Joana Ramalho, Natalia Ferreira, Daisuke Kuzume, Celine Tard, Nawal Waucquier, Isabelle Rougeaux, Sylvie Brice, Emmanuelle Kasprzyk, Elise Elrezzi, Sayah Meguig, Eric Hachulla, Clement Gauvain, Maria-Claire Migaud-Chervy, Dominique Deplanque, Elsa Jozefowicz, Loic Lebellec, Line Balaya-Gouraya, Nathalie Jehan Lacour, Halima Bournane, Nathalie Martin, Mongia Elabed, Niamey Sacko, Yasmine Boubrit, Amina Gaouar, Fetra Rakotondratafika, Marie Théaudin-Saliou, Cécile Cauquil-Michon, Celine Labeyrie, Adeline Not, Abdallah Al-Salameh, Anne-Lise Lecoq, Maeva Stephant, Andoni Echaniz-Laguna, Laurent Becquemont, Guillemette Beaudonnet, Vincent Algalarrondo, Ludivine Eliahou, Antoine Rousseau, Aissatou Signate, Emeline Berthelot, Jocelyn Inamo, Laetitia Vervoitte, Cecile Focseneanu, Thierry Gendre, Raphaele Arrouasse, Samar S. Ayache, Laura Ernande, Philippe Le Corvoisier, Hayet Salhi, Ariane Choumert, Vincent Ehinger, Julie Ruiz, Cyril Charlin, Thomas Megelin, Thomas H Brannagan III, Raisy Fayerman, Arreum Kim, Allan Paras, Leidy J Gonzalez, Steven Tsang, Fernanda Wajnsztajn, Jeffrey Shije, Christina Ulane, Inna Kleyman, Louis Weimer, Comana Cioroiu, Sakis Lambrianides, Rana Abu-Manneh, Eleni Zamba-Papanicolaou, Petros Agathangelou, Eleni Leonidou, Satoshi Tada, Akemi Fujita, Masahiro Nagai, Rina Ando, Yuko Hosokawa, Yuki Yamanishi, J. Scott Overcash, Elena Giardino, Leslie Boyer, Lien Dang, An Le, Tyler Nguyen, Lien Giang, Peter Sellers, Leyla Tran, Nghi Truong, Maita Vinas, Nicole Hrkman, Sarah Miller, David Nguyen, Ashley Smith, Helen Pu, Steve Li, Thao Vuong, Holly Dioso, Sinikka Green, Kia Lee, Hanh Chu, Michael Waters, Derya J Coskun, Karla A Zepeda, William O'Riordan, Laura Obici, Andrea Cortese, Alessandro Lozza, Giampaolo Merlini, Vittorio Rosti, Mario Sabatelli, Giulia Bisogni, Daniela Bernardo, Marco Luigetti, Andrea Di Paolantonio, Valeria Guglielmino, Angela Romano, Hans Nienhuis, Janita Bulthuis-Kuiper, Olga Gerk, Hannah Ulbricht, Lenka Taylor, Eva Meyle, Natalia Kleinschmidt, David Meyrath, Simone Noe-Schwenn, Ulrike Meng, Ralf Bauer, Fabian aus dem Siepen, Selina Hein, Tetsuya Takahashi, Tomohiko Oshita, Yoko Koujin, Shuichiro Neshige, Tomohisa Nezu, Akiko Segawa, Hiroki Ueno, Hiroyuki Morino, Josep M Campistol, Lida Maria Rodas Marin, Josep Miquel Blasco Pelicano, Lucía Galán Dávila, Marta Palacios, Vanesa Pytel Cordoba, Antonio Guerrero Sola, Alejandro Horga, Julián García Feijoo, Leopoldo Perez de Isla, Wilson Marques Júnior, Mariana Moscardini, Debora Cristina Litcanov, Ana Flavia Viera Lima, Leonardo Rodrigues, Barbara Marques Coutinho, Carolina Lavigne Moreira, Vanessa Daccach Marques, Francisco Munoz Beamud, Álvaro Gragera Martínez, Cristina Borrachero, Eugenia Cisneros Barroso, Adrián Rodríguez Rodríguez, Monica Sanz, Elena Rigo Oliver, Juan González Moreno, Jose M Gamez Martinez, Cristina Descals, Mercedes Uson, Francisco Jose Vega, Antoni Figuerola, Carles Montala, Moises Dias da Silva, Renata Gervais de Santa Rosa, Luiz Felipe Pinto, Marcus Vinicius Pinto, Amanda Cardoso Berensztejn, Fabio Barroso, Andrea Lautre, Lucas G Orellana, Maria Alejandra González-Duarte Briseño, Karla Cárdenas-Soto, Brenda Poled Jiménez López, Sandra Lorena Pérez-Castañeda, Carlos Gerardo Cantú Brito, David Rivera de la Parra, Jose Pablo Hernandez Reyes, Maria del Mar Saniger Alba, Elia Criollo Mora, Yesim Parman, Kus Jülide Rezzan, Erdi Sahin, Nail G Serbest, Hacer Durmus, Arman Cakar, Nuriye Ilknur Tugal Tutkun, Sacit Karamursel, Ali Elitok, Nermin G Sirin Inan, Emre Altinkurt, Jing Ye, Adriane C Allen, Vinay Chaudhry, Raquel Jarrett, Neil Bressler, Kathleen L Burks, Qingfeng Liu, Mohammad Khoshnoodi, Daniel P Judge, Geno Vista, Syed Mahmood Shah, Hirotoshi Hamaguchi, Junko Oda, Emi Fukase, Ikuko Taniguchi, Tetsuya Oda, Hironobu Endo, Masahiro Shimomura, Kimitaka Katanazaka, Shusuke Koto, Takahiro Nakano, Christof Scheid, Andreas Zueiter, Lars Pester, Doreen Walter, Betül Özdemir, Lukas F Frenzel, Udo Holtick, Jeeyoung Oh, Hee Jin Kim, Hyun Jin Shin, Kyomin Choi, Taro Yamashita, Teruaki Masuda, Yohei Misumi, Akihiko Ueda, Keiichi Nakahara, Akiko Yorita, Seiko Tsuruhisa, Takayuki Taniwaki, Masaya Harada, Taiga Moritaka, Naonori Sakurada, Elizabeth A Mauricio, Amber Baskin, Elliot Dimberg, Amie Fonder, Miriam Hobbs, Stephen J Russell, Peter Dyck, Wilson Gonsalves, Nelson Leung, Thomas E Witzig, Steven R Zeldenrust, Lisa Hwa, Prashant Kapoor, Shaji K Kumar, Yi Lin, John A Lust, Vincent S Rajkumar, David Dingli, Morie A Gertz, Ronald Go, Suzanne R Hayman, Samir Dalia, Esmeralda Carrillo, Peter Gorevic, Garnette Mason, Chi-Chao Chao, Ming-Jen Lee, Jen-Jen Su, Sung-Tsang Hsieh, Li-Kai Tsai, Shin-Joe Yeh, Chih-Chao Yang, Senda Ajroud-Driss Ajroud-Driss, Patricia Casey, Benjamin C Joslin, Miriam Freimer, Alison Sankey, Amanda Kenepp, Sarah Heintzman, Samantha LoRusso, Youichi Hokezu, Byoung-Joon Kim, JuHyeon Kim, Ga Yeon Lee, Eun Bin Cho, Eun-Seok Jeon, Ju-Hong Min, Jin Myoung Seok, Hye Lim Lee, Jae Hong Park, Yoshiki Sekijima, Chinatsu Miyazawa, Nagaaki Kato, Dai Kishida, Akiyo Hineno, Minori Kodaira, Tsuneaki Yoshinaga, Teruyoshi Miyahara, Akira Imai, Kazuhiko Matsumoto, Kon-Ping Lin, Yi-Chung Lee, Malin Falk, Bjorn Pilebro, Ole Suhr, Per Lindqvist, Karin Soderberg, Fatima Pedrosa-Domellöf, Intissar Anan, Erik Nordh, Ivaylo Tournev, Sashka Zhelyazkova-Glaveeva, Zheyna Cherneva, Staiko Sarafov, Teodora Chamova, Sylvia Cherninkova-Gopina, Frauke Friebel, Andree Zibert, Natasa Mihailovic, Friederike Schubert, Elena Vorona, Larissa Lahme, Anna Huesing-Kabar, Matthias Schilling, Iyad Kabar, Ana Martinez-Naharro, Liza Chacko, Oliver Cohen, Steven Law, Tamer Rezk, Helen J Lachmann, Brianna Blume, Stacy Dixon, Soon Chai Low, Soo Looi Chan, He Eng Li Lim, Khean Jin Goh, Deborah Kraus, Kristin Jack, N. Kevin Wade, Glenn Lopate, Brittany Zwijack, Julaine Florence, R. Brian Sommerville, Graeme Stewart, Julie Ryder, Linda Mekhael, Mark Taylor, Daniel Suan, Karen Wells, Paula Stone, Amenze Itoya, Mercy Owusu-Sekyere, Desmond Thai, Ilonah Chahine, Salve Pedrosa, Thi Hoa (Therese) Do
المساهمون: Repositório da Universidade de Lisboa
المصدر: The Lancet Neurology. 20:49-59
مصطلحات موضوعية: Adult, Male, medicine.medical_specialty, Drug-Related Side Effects and Adverse Reactions, 030204 cardiovascular system & hematology, Placebo, Severity of Illness Index, Polyneuropathies, 03 medical and health sciences, 0302 clinical medicine, Quality of life, Internal medicine, Outcome Assessment, Health Care, Severity of illness, medicine, Humans, Prealbumin, RNA, Small Interfering, Infusions, Intravenous, Adverse effect, Aged, Amyloid Neuropathies, Familial, business.industry, Middle Aged, medicine.disease, Interim analysis, amyloidosis, transthyretin, polyneuropathy, patisiran, OLE study, Clinical trial, Female, Neurology (clinical), business, Polyneuropathy, 030217 neurology & neurosurgery, Progressive disease
وصف الملف: application/pdf
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::ce6a19ce91101df4f11e95eb6d009161Test
https://doi.org/10.1016/s1474-4422Test(20)30368-9 -
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المؤلفون: Matthew T. White, Masahisa Katsuno, Jing Jing Wang, Taro Yamashita, Mitsuharu Ueda, Tsuneaki Yoshinaga, Yoshiki Sekijima, Marianne T. Sweetser, Gen Sobue, Yukio Ando, Haruki Koike, Xiaoping Zhang, Minori Kodaira
المصدر: Neurology and Clinical Neuroscience. 8:251-260
مصطلحات موضوعية: Pathology, medicine.medical_specialty, biology, business.industry, Amyloidosis, medicine.disease, Transthyretin, Neurology, RNA interference, medicine, biology.protein, Neurology (clinical), business, Polyneuropathy, Attr amyloidosis
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::1ce5b2f8eb0cedd5b6c483c79f2c3022Test
https://doi.org/10.1111/ncn3.12396Test -
3
المؤلفون: Isabel Conceição, Marianne T. Sweetser, Emre Aldinc, Céline Tard, Madeline Merkel, Márcia Waddington-Cruz, Dianna Quan, David Adams, Michael Polydefkis, John L. Berk, Jing Jing Wang, Teresa Coelho, Arnt V. Kristen, Alejandra González-Duarte, Mitsuharu Ueda, Jihong Chen, Cécile Cauquil, Michelle L. Mauermann, Hartmut Schmidt
المصدر: Journal of Neurology
مصطلحات موضوعية: Adult, Male, medicine.medical_specialty, Hereditary transthyretin-mediated amyloidosis, Neurology, Orthostatic intolerance, Placebo, Transthyretin, Polyneuropathies, Double-Blind Method, Quality of life, Polyneuropathy, Internal medicine, medicine, Humans, RNA, Small Interfering, Small interfering ribonucleic acid (siRNA), Amyloid Neuropathies, Familial, Original Communication, business.industry, Amyloidosis, Correction, Autonomic nervous system diseases, Middle Aged, medicine.disease, RNAi Therapeutics, Blood pressure, Quality of Life, Patisiran, Female, Neurology (clinical), business, Body mass index
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::4a6304bdfba32573f7ed185e071e1e9fTest
https://doi.org/10.1007/s00415-019-09602-8Test -
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المؤلفون: Alejandra González-Duarte, Erhan Berber, Marianne T. Sweetser, Davide Adams, Teresa Coelho, Elizabeth Mauricio, Jing Jing Wang, Marco Luigetti, Michael Polydefkis, Matthew T. White, Thomas H. Brannagan, Jonas Wixner, Hartmut Schmidt
المصدر: Journal of the Neurological Sciences. 429:117766
مصطلحات موضوعية: medicine.medical_specialty, Neurology, business.industry, Amyloidosis, medicine, In patient, Neurology (clinical), Extension (predicate logic), Open label, medicine.disease, business, Surgery
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::8685d85d0e9132d669c70b2604f03338Test
https://doi.org/10.1016/j.jns.2021.117766Test -
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المؤلفون: Teresa Coelho, John L. Berk, Isabel Conceição, Céline Tard, Madeline Merkel, Jing Jing Wang, Hartmut Schmidt, Dianna Quan, Alejandra González-Duarte, Márcia Waddington-Cruz, Cécile Cauquil, Michael Polydefkis, Mitsuharu Ueda, Michelle L. Mauermann, Arnt V. Kristen, Marianne T. Sweetser, Emre Aldinc, Jihong Chen, David Adams
المصدر: Journal of Neurology. 267:713-714
مصطلحات موضوعية: Oncology, medicine.medical_specialty, Neurology, biology, business.industry, Amyloidosis, medicine.disease, Transthyretin, RNA interference, Internal medicine, biology.protein, medicine, In patient, Neurology (clinical), business, Neuroradiology
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::fd66aab996a7cb3e1ee81afac36eb4adTest
https://doi.org/10.1007/s00415-020-09715-5Test -
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المؤلفون: Marianne T. Sweetser, Ludwig Kappos, Krzysztof Selmaj, Bhupendra Khatri, Kimberly Umans, Gavin Giovannoni, Steven J. Greenberg, Jacob Elkins, Peter McCroskery, Ralf Gold
المصدر: Multiple Sclerosis and Related Disorders. 9:36-46
مصطلحات موضوعية: Adult, Male, medicine.medical_specialty, Daclizumab, MedDRA, Antibodies, Monoclonal, Humanized, Disability Evaluation, 03 medical and health sciences, Multiple Sclerosis, Relapsing-Remitting, 0302 clinical medicine, Internal medicine, Clinical endpoint, medicine, Humans, Cumulative incidence, 030212 general & internal medicine, Adverse effect, business.industry, Multiple sclerosis, General Medicine, medicine.disease, Discontinuation, Surgery, Treatment Outcome, Neurology, Tolerability, Immunoglobulin G, Female, Neurology (clinical), business, Immunosuppressive Agents, 030217 neurology & neurosurgery, Follow-Up Studies, medicine.drug
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::8a97ba158857963aa7a83995b7e57230Test
https://doi.org/10.1016/j.msard.2016.05.010Test -
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المؤلفون: Robert J. Fox, Michael Hutchinson, Carlo Pozzilli, Eva Havrdova, K. Selmaj, Ralf Gold, David G. MacManus, Theodore Phillips, James Potts, Minhua Yang, Tarek A. Yousry, Mark Novas, Douglas L. Arnold, Nuwan Kurukulasuriya, Marianne T. Sweetser, Ludwig Kappos, Ray Zhang, Amit Bar-Or, David Miller
المصدر: Multiple Sclerosis (Houndmills, Basingstoke, England)
مصطلحات موضوعية: Oncology, Adult, Male, medicine.medical_specialty, Multiple Sclerosis, Time Factors, Dimethyl Fumarate, Treatment outcome, DEFINE, 03 medical and health sciences, chemistry.chemical_compound, 0302 clinical medicine, Internal medicine, medicine, Humans, 030212 general & internal medicine, ENDORSE, Glatiramer acetate, Expanded Disability Status Scale, Dimethyl fumarate, business.industry, Relapsing–remitting multiple sclerosis, Extension study, Multiple sclerosis, Glatiramer Acetate, medicine.disease, Interim analysis, Magnetic Resonance Imaging, Surgery, delayed-release dimethyl fumarate (DMF), Relapsing-remitting multiple sclerosis, Neurology, Neurology (clinical), Treatment Outcome, chemistry, Delayed-release dimethyl fumarate (DMF), Female, business, Original Research Papers, 030217 neurology & neurosurgery, Immunosuppressive Agents, medicine.drug
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::c1f78ef34d45e60a75761dd3357f9937Test
http://europepmc.org/articles/PMC5418934Test -
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المؤلفون: Norman Kim, Marianne T. Sweetser, Patricia Valencia, J. Theodore Phillips, Tim Thullen, Nuwan Kurukulasuriya, Lauren Oliva, Ludwig Kappos, Vissia Viglietta, Robert J. Fox, Amit Bar-Or, Jie Li, Mark Novas, Eva Havrdova, Ralf Gold
المصدر: Neurology and Therapy
مصطلحات موضوعية: medicine.medical_specialty, Neurology, Pharmacology, Multiple sclerosis, chemistry.chemical_compound, Pregnancy, Internal medicine, medicine, Women, Pregnancy outcomes, Delayed-release dimethyl fumarate, Original Research, Dimethyl fumarate, business.industry, medicine.disease, Preclinical, Postmarketing, Clinical trial, Oral agents, chemistry, Neurology (clinical), Safety, business
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::1ce364f296eb8857de18f55012f1f98aTest
http://europepmc.org/articles/PMC4685863Test -
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المؤلفون: Petra Duda, Gabriel Pardo, Howard Rossman, Fiona Forrestal, Michael Kaufman, Marianne T. Sweetser
المصدر: Journal of the Neurological Sciences. 341:22-27
مصطلحات موضوعية: Adult, Male, Time Factors, Adolescent, chemical and pharmacologic phenomena, Antibodies, Monoclonal, Humanized, complex mixtures, Immunoglobulin G, Young Adult, Multiple Sclerosis, Relapsing-Remitting, Natalizumab, Tetanus Toxoid, medicine, Humans, Immunologic Factors, biology, Tetanus, business.industry, Multiple sclerosis, Vaccination, Toxoid, Middle Aged, medicine.disease, Neurology, Immunization, Hemocyanins, Immunology, biology.protein, Female, Neurology (clinical), Antibody, business, Immunologic Memory, Keyhole limpet hemocyanin, Follow-Up Studies, medicine.drug
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::871120ac8e5ee0325e9b09f1e00d1347Test
https://doi.org/10.1016/j.jns.2014.03.035Test -
10
المؤلفون: Marianne T. Sweetser, S Solomon, PJ Gandhi, D Adams, A Gonzalez-Duarte, Kon-Ping Lin, T Coelho, Peter J. Dyck, Ole B. Suhr, Arnt V. Kristen, John L. Berk, William O'Riordan, J Vest, Chih-Chao Yang
المصدر: Canadian Journal of Neurological Sciences / Journal Canadien des Sciences Neurologiques. 46:S20
مصطلحات موضوعية: medicine.medical_specialty, medicine.diagnostic_test, biology, business.industry, Amyloidosis, Cardiomyopathy, Phases of clinical research, General Medicine, medicine.disease, Placebo, Transthyretin, Neurology, Internal medicine, medicine, biology.protein, Cardiology, End-diastolic volume, Medical history, Neurology (clinical), business, Electrocardiography
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::f74f39d438577bf614f5227ac1717aa3Test
https://doi.org/10.1017/cjn.2019.125Test