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المؤلفون: Dana Carroll, Dario Boffelli, Seok Jin Heo, Donald B. Kohn, Tianjiao Wang, Jacob E. Corn, Jennifer R. Berman, Mark A. DeWitt, Mark C. Walters, Therese Mitros, David I. K. Martin, Fabrizia Urbinati, Wendy Magis, Denise P. Muñoz, Nicolas Bray
المصدر: Science Translational Medicine. 8
مصطلحات موضوعية: Adult, 0301 basic medicine, Hemoglobin, Sickle, CD34, Anemia, Sickle Cell, Mice, SCID, Biology, Polymorphism, Single Nucleotide, Article, Cell Line, Translational Research, Biomedical, Mice, 03 medical and health sciences, Genome editing, Mice, Inbred NOD, Animals, Humans, Guide RNA, Progenitor cell, Gene, Gene Editing, Mice, Knockout, General Medicine, Hematopoietic Stem Cells, Adult Stem Cells, Haematopoiesis, 030104 developmental biology, Mutation, Immunology, Cancer research, Heterografts, CRISPR-Cas Systems, Stem cell, Ex vivo
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::0a5540b6e98cf2a7dab8a8557175a050Test
https://doi.org/10.1126/scitranslmed.aaf9336Test -
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المؤلفون: Denise P. Muñoz, Nicolas Bray, Fabrizia Urbinati, Mark C. Walters, Jacob E. Corn, David Martin, Wendy Magis, Dana Carroll, Tianjiao Wang, Donald B. Kohn, Jennifer R. Berman, Mark A. DeWitt
مصطلحات موضوعية: Mutation, Cell, CD34, Biology, medicine.disease_cause, Molecular biology, Transplantation, Haematopoiesis, medicine.anatomical_structure, hemic and lymphatic diseases, medicine, Hemoglobin, Stem cell, Progenitor cell
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::e795ac7ea9e6fa7bf6ef86a10a9588a4Test
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المؤلفون: George Stamatoyannopoulos, Wendy Magis, Mark W. Rixon, Richard Gelinas
المصدر: Blood. 71:1108-1112
مصطلحات موضوعية: Genetics, Mutation, Hereditary persistence of fetal hemoglobin, Sequence analysis, Immunology, Nucleic acid sequence, Promoter, Cell Biology, Hematology, Biology, medicine.disease_cause, medicine.disease, Biochemistry, Molecular biology, hemic and lymphatic diseases, Fetal hemoglobin, medicine, Enhancer, Gene
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::838a5e88b151f935fdbe7fc6d9bc5b0fTest
https://doi.org/10.1182/blood.v71.4.1108.1108Test