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المؤلفون: Glenn F. Pierce, Johnny Mahlangu, Thomas Sannié, David Lillicrap, Alok Srivastava, Dawn Rottellini, Donna Coffin, Thierry VandenDriessche, K. John Pasi, Radoslaw Kaczmarek, Alain Weill
المساهمون: Basic (bio-) Medical Sciences, Division of Gene Therapy & Regenerative Medicine
المصدر: Haemophilia. 26:443-449
مصطلحات موضوعية: medicine.medical_specialty, Consensus, media_common.quotation_subject, Genetic enhancement, haemophilia, 030204 cardiovascular system & hematology, Hemophilia A, Haemophilia, 03 medical and health sciences, 0302 clinical medicine, Multidisciplinary approach, Voting, medicine, Humans, Challenges, round table, Genetics (clinical), media_common, Medicine(all), business.industry, Health technology, Gene Therapy, Genetic Therapy, Hematology, General Medicine, global, Payment, medicine.disease, Clinical trial, Round table, Family medicine, business, 030215 immunology
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::c38e32ba755156877323ace2a466b82dTest
https://doi.org/10.1111/hae.13971Test -
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المؤلفون: Bent Winding, Keiji Nogami, Guy Young, Chris Barnes, Huixing Yuan, Johannes Oldenburg, Elena Santagostino, Liane Khoo, Beatrice Nolan, Barbara A. Konkle, Joachim Fruebis, K. John Pasi, Ingrid Pabinger, Dan Rudin, Johnny Mahlangu
المصدر: Haemophilia
مصطلحات موضوعية: Adult, Male, medicine.medical_specialty, Adolescent, Recombinant Fusion Proteins, 030204 cardiovascular system & hematology, Haemophilia, Hemophilia A, Recombinant factor viii, bleed rate, 03 medical and health sciences, Young Adult, 0302 clinical medicine, Internal medicine, medicine, Clinical endpoint, Humans, Clinical Haemophilia, Child, Genetics (clinical), rFVIIIFc, Aged, extended half‐life, Factor VIII, business.industry, Hematology, General Medicine, Original Articles, Bleed, Middle Aged, medicine.disease, Confidence interval, Immunoglobulin Fc Fragments, Regimen, Fc fusion, Treatment Outcome, individualized prophylaxis, Child, Preschool, Severe haemophilia A, Original Article, Female, business, perioperative haemostasis, 030215 immunology
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::bd4022ccca7aa7b264ac7e5d898662bfTest
http://europepmc.org/articles/PMC7384031Test -
3The impact of factor infusion frequency on health-related quality of life in people with haemophilia
المؤلفون: Xin Ying Lee, Gabriel Pedra, Sonia O’Hara, John Pasi, Pia Christoffersen, Kate Khair, Jamie O'Hara
المصدر: The Journal of Haemophilia Practice. 7:102-109
مصطلحات موضوعية: Health related quality of life, 03 medical and health sciences, medicine.medical_specialty, 0302 clinical medicine, business.industry, medicine, Pharmacy, 030204 cardiovascular system & hematology, business, Intensive care medicine, Haemophilia, medicine.disease, 030215 immunology
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::c42e32d1d3f9f4b3f0a07ab50f678970Test
https://doi.org/10.17225/jhp00158Test -
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المؤلفون: K. John Pasi, P. Batty
المصدر: Expert Review of Precision Medicine and Drug Development. 4:259-262
مصطلحات موضوعية: Pharmacology, congenital, hereditary, and neonatal diseases and abnormalities, medicine.medical_specialty, business.industry, Genetic enhancement, Haemophilia A, Haemophilia, medicine.disease, Gastroenterology, Coagulation, hemic and lymphatic diseases, Internal medicine, Drug Discovery, Genetics, medicine, Molecular Medicine, Haemophilia B, business, Factor IX, medicine.drug
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::0dcccfbfcfd11cb978b0ca784b79d9f0Test
https://doi.org/10.1080/23808993.2019.1632704Test -
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المؤلفون: Tara M Robinson, Savita Rangarajan, K. John Pasi, Michael Laffan, Emily Symington, Will Lester, Bella Madan, Wing Yen Wong, Glenn F. Pierce, Xinqun Yang, Benjamin Kim, Nina Mitchell
المساهمون: Apollo - University of Cambridge Repository
المصدر: Haemophilia : the official journal of the World Federation of Hemophilia. 27(6)
مصطلحات موضوعية: FVIII, Male, congenital, hereditary, and neonatal diseases and abnormalities, medicine.medical_specialty, IMPACT, Genetic enhancement, Haemophilia A, haemophilia A, Hemorrhage, Haemophilia, Hemophilia A, Gastroenterology, PROPHYLAXIS, Hemostatics, Quality of life, QUALITY-OF-LIFE, hemic and lymphatic diseases, Internal medicine, medicine, Humans, Adverse effect, Genetics (clinical), Science & Technology, Factor VIII, business.industry, 1103 Clinical Sciences, ADULTS, Hematology, General Medicine, Genetic Therapy, medicine.disease, Confidence interval, Cardiovascular System & Hematology, Tolerability, Child, Preschool, haemostasis, Cohort, Quality of Life, business, Life Sciences & Biomedicine
وصف الملف: text/xml; application/pdf
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::0c531853ba9fa59e5941dee55d492e2dTest
https://pubmed.ncbi.nlm.nih.gov/34378280Test -
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المؤلفون: Liana Gercheva-Kyuchukova, Huy Van Nguyen, Tim Mant, Catherine Bagot, Baisong Mei, Qifeng Yu, Margaret V. Ragni, Craig Benson, Kate Madigan, Toshko Lissitchkov, K. John Pasi, Margarita Timofeeva, Pratima Chowdary, Pencho Georgiev, Vasily Mamonov
المصدر: Journal of Thrombosis and Haemostasis
مصطلحات موضوعية: Adult, Male, medicine.medical_specialty, Acetylgalactosamine, Erythema, 030204 cardiovascular system & hematology, Haemophilia, Hemophilia A, Gastroenterology, Hemophilia B, Antithrombins, fitusiran, 03 medical and health sciences, 0302 clinical medicine, Pharmacokinetics, Internal medicine, hemophilia, inhibitors, medicine, Humans, RNA, Small Interfering, Adverse effect, business.industry, HAEMOSTASIS, Antithrombin, Hematology, Original Articles, medicine.disease, antithrombin, Hemostasis, Pharmacodynamics, siRNA, Cohort, Quality of Life, Original Article, medicine.symptom, business, medicine.drug
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::d8c4dd37dee07aac554599d82ced9e17Test
https://pubmed.ncbi.nlm.nih.gov/33587824Test -
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المؤلفون: Cedric Hermans, Maria Elisa Mancuso, K. John Pasi, Beatrice Nolan
المساهمون: UCL - SSS/IREC/CARD - Pôle de recherche cardiovasculaire, UCL - (SLuc) Service d'hématologie
المصدر: European Journal of Haematology
European journal of haematology, Vol. 106, no. 6, p. 745-761 (2021)مصطلحات موضوعية: medicine.medical_specialty, immune tolerance, Recombinant Fusion Proteins, Haemophilia A, Once weekly, factor VIII‐Fc fusion protein, haemophilia A, Review Article, Haemophilia, Hemophilia A, Recombinant factor viii, 03 medical and health sciences, Therapeutic approach, 0302 clinical medicine, hemic and lymphatic diseases, half‐life, medicine, Humans, Factor VIII-Fc fusion protein, Intensive care medicine, surgical haemostasis, rFVIIIFc, Clinical Trials as Topic, Factor VIII, business.industry, Prophylaxis, Immune tolerance, Hematology, General Medicine, medicine.disease, Half-life, Immunoglobulin Fc Fragments, Fc fusion, Patient need, 030220 oncology & carcinogenesis, recombinant fusion proteins, prophylaxis, business, Dosing Frequency, 030215 immunology
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::1f5f34e0da36f347a33816459b9017d8Test
https://pubmed.ncbi.nlm.nih.gov/33650192Test -
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المؤلفون: Roshni Kulkarni, Johannes Oldenburg, Johnny Mahlangu, Hervé Chambost, Beatrice Nolan, Stephanie P’Ng, Carolyn M. Bennett, Margareth C. Ozelo, K. John Pasi, Bent Winding, Amy D. Shapiro, Huixing Yuan, Margaret V. Ragni, Joachim Fruebis, Tadashi Matsushita, Dan Rudin, Krista Fischer
المساهمون: Queen Mary's College [Chennai], University Medical Center [Utrecht], University of Pittsburgh (PITT), Pennsylvania Commonwealth System of Higher Education (PCSHE), Michigan State University System, University of Campinas [Campinas] (UNICAMP), University of Johannesburg (UJ), Indiana University - Purdue University Indianapolis (IUPUI), Indiana University System, Murdoch University, Centre recherche en CardioVasculaire et Nutrition = Center for CardioVascular and Nutrition research (C2VN), Aix Marseille Université (AMU)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Institut National de Recherche pour l’Agriculture, l’Alimentation et l’Environnement (INRAE), Our Lady's Children's Hospital Crumlin (OLCHC), Emory University [Atlanta, GA], Nagoya City University [Nagoya, Japan], Stockholm University, Sanofi US, Institut für Genetik - Universität Bonn / Institute of Genetics - University of Bonn, Universidade Estadual de Campinas = University of Campinas (UNICAMP), University of Johannesburg [South Africa] (UJ), Lucas, Nelly
المصدر: Haemophilia
Haemophilia, Wiley, 2020, 26 (6), ⟨10.1111/hae.14036⟩
Haemophilia, 2020, 26 (6), ⟨10.1111/hae.14036⟩مصطلحات موضوعية: Adult, Male, [SDV.MHEP.HEM] Life Sciences [q-bio]/Human health and pathology/Hematology, medicine.medical_specialty, Time Factors, Adolescent, Recombinant Fusion Proteins, haemophilia B, 030204 cardiovascular system & hematology, Haemophilia, Hemophilia B, bleed rate, Young Adult, 03 medical and health sciences, 0302 clinical medicine, Internal medicine, medicine, Clinical endpoint, Humans, Haemophilia B, extended half-life, Child, Genetics (clinical), Factor IX, factor IX, business.industry, [SDV.MHEP.HEM]Life Sciences [q-bio]/Human health and pathology/Hematology, Hematology, General Medicine, Middle Aged, medicine.disease, Confidence interval, Immunoglobulin Fc Fragments, 3. Good health, Fc fusion, individualized prophylaxis, Child, Preschool, rFIXFc, Female, Long term safety, business, perioperative haemostasis, 030215 immunology, Recombinant factor IX, medicine.drug
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::7cd16c5a39de08d060e95abeadfcd587Test
https://doi.org/10.1111/hae.14036Test -
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المؤلفون: K. John Pasi, Sean Platton, Daniel P. Hart, Suthesh Sivapalaratnam, Minal Dave, Vickie MacDonald, Kurtis Lee, Laura E. Green, Peter MacCallum, Louise Bowles, Nada Yartey
المصدر: The New England Journal of Medicine
New England Journal of Medicineمصطلحات موضوعية: medicine.medical_specialty, Coronavirus disease 2019 (COVID-19), 030204 cardiovascular system & hematology, Gastroenterology, 03 medical and health sciences, 0302 clinical medicine, Internal medicine, Correspondence, Coagulation testing, Medicine, Humans, In patient, 030212 general & internal medicine, Pandemics, Blood coagulation test, Lupus anticoagulant, medicine.diagnostic_test, business.industry, SARS-CoV-2, COVID-19, General Medicine, medicine.disease, Antiphospholipid Syndrome, Pneumonia, Prolonged aptt, Lupus Coagulation Inhibitor, business, circulatory and respiratory physiology, Partial thromboplastin time
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::3880c064a315713c72ba84f22c469d42Test
http://europepmc.org/articles/PMC7217555Test -
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المؤلفون: Suthesh Sivapalaratnam, Erica De Candia, Janine Collins, Anthony D. Whetton, Nihr BioResource, Rachel Reed, Wadie F. Bahou, Denis Seyres, Daniel Greene, Hanna Shalev, Anne M. Kelly, Sandra Le Quellec, Paolo Gresele, Thierry M Leblanc, Elizabeth Chalmers, Tadbir K. Bariana, Rémi Favier, John Pasi, Albert Sickmann, Kathleen Freson, Sri V V Deevi, Daniel P. Hart, Dave Lee, Ernest Turro, Rutendo Mapeta, Luigi Grassi, John K. Wu, Matthew C Sims, Sara Morais, Mattia Frontini, Barbara Zieger, Diane J. Nugent, Mallika Sekhar, Louisa Mayer, Loredana Bury, Man-Chiu Poon, Soo J. Park, William J. Astle, Frances Burden, Paquita Nurden, Jonathan Stephens, Cécile Lavenu-Bombled, Andreas Greinacher, Rachael Da Silva, Marie-Françoise Hurtaud, Jose A. Guerrero, Robert Campbell Tait, Sofia Papadia, Eva Leinoe, Antonio Rodriguez-Romera, Karyn Megy, Wendy N. Erber, Gian Marco Podda, Ron Kerr, Willem H. Ouwehand, Laxmikanth Kollipara, Marie-Christine Alessi, Keith Gomez, Harriet McKinney, Taco W. Kuijpers, Alan D. Michelson, Kate Downes, Samantha Farrow, Orna Steinberg-Shemer
مصطلحات موضوعية: Autoimmune disease, 0303 health sciences, business.industry, Autoantibody, Inflammation, Immune dysregulation, medicine.disease_cause, medicine.disease, 3. Good health, Gray platelet syndrome, 03 medical and health sciences, 0302 clinical medicine, Immune system, medicine.anatomical_structure, Megakaryocyte, Immunology, medicine, Bone marrow, medicine.symptom, business, 030304 developmental biology, 030215 immunology
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::9a3fdca8a8631fc6967e91555bbfde14Test
https://doi.org/10.1101/2020.03.23.20041467Test