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المؤلفون: Fabian Model, Ludwig Kappos, Stephen L. Hauser, Heidemarie Kletzl, Ekaterina Gibiansky, Andreas Günther, Claire Petry, Ann Herman, Francois Mercier, Yumi Yamamoto, Qing Wang
المصدر: British Journal of Clinical Pharmacology
British journal of clinical pharmacology, vol 87, iss 6مصطلحات موضوعية: Phases of clinical research, Relapsing-Remitting, Neurodegenerative, 030226 pharmacology & pharmacy, Gastroenterology, 0302 clinical medicine, population analysis, Monoclonal, Medicine, Pharmacology (medical), 030212 general & internal medicine, Pharmacology & Pharmacy, Humanized, education.field_of_study, Pharmacology and Pharmaceutical Sciences, Multiple Sclerosis, Chronic Progressive, Chronic Progressive, Original Article, medicine.drug, medicine.medical_specialty, Multiple Sclerosis, pharmacokinetic-pharmacodynamic, Population, Primary Progressive Multiple Sclerosis, Antibodies, Monoclonal, Humanized, Autoimmune Disease, Antibodies, 03 medical and health sciences, Multiple Sclerosis, Relapsing-Remitting, Pharmacokinetics, Internal medicine, pharmacokinetic–pharmacodynamic, pharmacodynamics, Humans, Immunologic Factors, In patient, education, Pharmacology, business.industry, Multiple sclerosis, neurology, pharmacokinetic–, Neurosciences, Original Articles, medicine.disease, Brain Disorders, pharmacodynamic, Pharmacodynamics, Ocrelizumab, business
وصف الملف: application/pdf
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::8811580eb5543d689634ed86d7b68a05Test
http://europepmc.org/articles/PMC8247316Test -
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المؤلفون: Maria Mazurkiewicz-Bełdzińska, Marianne Gerber, Heidemarie Kletzl, R. Masson, Andrea Klein, Edmar Zanoteli, Ksenija Gorni, Basil T. Darras, Kristy Rose, Giovanni Baranello, Laurent Servais, H. Xiong, D. Vlodavets, A. Dodman, M. El-Khairi, Renata S. Scalco
المصدر: Abstracts of the 46th Annual Meeting of the Society for Neuropediatrics.
مصطلحات موضوعية: business.industry, Anesthesia, medicine, Spinal muscular atrophy, medicine.disease, SMA, business
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::89e5acac415f97f435c35a50acd74960Test
https://doi.org/10.1055/s-0041-1739636Test -
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المؤلفون: Leon Aarons, Heidemarie Kletzl, Yumi Cleary, Michael Gertz, Andreas Günther, Katja Heinig, Aleksandra Galetin, Kayode Ogungbenro, Paul Grimsey
المصدر: Fukushima (Cleary), Y, Gertz, M, Grimsey, P, Günther, A, Heinig, K, Ogungbenro, K, Aarons, L, Galetin, A & Kletzl, H 2021, ' Model-based drug-drug interaction extrapolation strategy from adults to children – risdiplam in pediatric patients with spinal muscular atrophy ', Clinical Pharmacology & Therapeutics . https://doi.org/10.1002/cpt.2384Test
مصطلحات موضوعية: Adult, Male, Oncology, Physiologically based pharmacokinetic modelling, medicine.medical_specialty, Adolescent, CYP3A, Midazolam, Models, Biological, Muscular Atrophy, Spinal, Young Adult, Pharmacokinetics, In vivo, Internal medicine, Humans, Medicine, Drug Interactions, Pharmacology (medical), Child, Pharmacology, business.industry, Infant, Newborn, Area under the curve, Infant, Spinal muscular atrophy, SMA, medicine.disease, Pyrimidines, Neuromuscular Agents, Child, Preschool, Cytochrome P-450 CYP3A Inhibitors, Female, business, Azo Compounds, medicine.drug
وصف الملف: application/pdf
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::60d9913e9af5e9910daa01792db02396Test
https://www.research.manchester.ac.uk/portal/en/publications/modelbased-drugdrug-interaction-extrapolation-strategy-from-adults-to-children--risdiplam-in-pediatric-patients-with-spinal-muscular-atrophyTest(c85742c4-c14d-419d-9311-c599b740e7f5).html -
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المؤلفون: Heidemarie Kletzl, D. Vlodavets, Marianne Gerber, Sabine Fuerst-Recktenwald, Maria Mazurkiewicz-Bełdzińska, Basil T. Darras, M. El-Khairi, Giovanni Baranello, Ksenija Gorni, Renata S. Scalco, Riccardo Masson, H. Xiong, Kristy Rose, Edmar Zanoteli, Laurent Servais
المصدر: Web of Science
مصطلحات موضوعية: Pediatrics, medicine.medical_specialty, business.industry, Gross motor skill, Spinal muscular atrophy, medicine.disease, Sitting, SMA, Bayley Scales of Infant Development, 03 medical and health sciences, 0302 clinical medicine, 030228 respiratory system, Tolerability, medicine, Clinical endpoint, 030212 general & internal medicine, Toddler, business
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::ac31266581f9dd75f3911be295696a45Test
https://doi.org/10.1183/13993003.congress-2020.1172Test -
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المؤلفون: M. Al-Muhaizea, A. Prufer, Marianne Gerber, Y. Wang, Leslie Nelson, Edmar Zanoteli, Richard S. Finkel, Michelle A. Farrar, L. Servais, Renata S Scalco, Heidemarie Kletzl, E. Bertini, M. El-Khairi, Ksenija Gorni, L. Palfreeman
المصدر: Neuromuscular Disorders. 31:S48
مصطلحات موضوعية: Pathology, medicine.medical_specialty, biology, business.industry, Spinal muscular atrophy, Rainbowfish, medicine.disease, biology.organism_classification, SMA, Neurology, Pediatrics, Perinatology and Child Health, medicine, Neurology (clinical), business, Genetics (clinical)
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::e526d2e30c62cb67f40bf5f07beb4359Test
https://doi.org/10.1016/j.nmd.2021.07.021Test -
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المؤلفون: Heidemarie Kletzl, Odile Boespflug-Tanguy, Nicolas Deconinck, Riccardo Masson, D. Vlodavets, Giovanni Baranello, J. Day, Kristy Rose, H. Xiong, Edmar Zanoteli, Ksenija Gorni, Eugenio Mercuri, E. Gaki, L. Servais, A. Dodman, M. El-Khairi, Marianne Gerber, Basil T. Darras, Andrea Klein, Maria Mazurkiewicz-Bełdzińska
المصدر: Neuromuscular Disorders. 31:S134
مصطلحات موضوعية: Pathology, medicine.medical_specialty, Neurology, business.industry, Pediatrics, Perinatology and Child Health, medicine, Neurology (clinical), Spinal muscular atrophy, medicine.disease, SMA, business, Genetics (clinical)
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::3a82a7c5134952d977f87858d3968a50Test
https://doi.org/10.1016/j.nmd.2021.07.303Test -
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المؤلفون: Heidemarie Kletzl, A. Höflich, Friedrich Metzger, Eginhard Schick, Christoph Wandel, Norbert Bleich, C. Höflich, R.F. Staack, Andreas Guenther, Jan Frystyk
المصدر: Kletzl, H, Guenther, A, Höflich, A, Höflich, C, Frystyk, J, Staack, R F, Schick, E, Wandel, C, Bleich, N & Metzger, F 2017, ' First-in-man study with a novel PEGylated recombinant human insulin-like growth factor-I ', Growth Hormone & I G F Research, vol. 33, pp. 9-16 . https://doi.org/10.1016/j.ghir.2017.01.001Test
مصطلحات موضوعية: Male, 0301 basic medicine, medicine.medical_specialty, Maximum Tolerated Dose, Erythema, Endocrinology, Diabetes and Metabolism, Hypoglycemia, Polyethylene Glycols, 03 medical and health sciences, Subcutaneous injection, 0302 clinical medicine, Endocrinology, Double-Blind Method, Pharmacokinetics, Internal medicine, medicine, Humans, Tissue Distribution, Insulin-Like Growth Factor I, Growth Substances, First-in-man study, Dose-Response Relationship, Drug, business.industry, Prognosis, medicine.disease, Recombinant Proteins, 030104 developmental biology, Tolerability, Pharmacodynamics, PEGylation, Female, medicine.symptom, business, 030217 neurology & neurosurgery
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::830323b68af1ea8d8ea70fdc93cf9300Test
https://doi.org/10.1016/j.ghir.2017.01.001Test -
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المؤلفون: Lauren Boak, Omar Khwaja, Daniel Umbricht, Christophe Grundschober, James T. McCracken, Eric Hollander, Heidemarie Kletzl, Lisa Squassante, Marta del Valle Rubido, Frederick Shic, Jana Noeldeke, Lawrence Scahill, Paulo Fontoura
المصدر: Neuropsychopharmacology
مصطلحات موضوعية: Adult, Male, 0301 basic medicine, Receptors, Vasopressin, Vasopressin, medicine.medical_specialty, Indoles, Adolescent, Autism Spectrum Disorder, medicine.drug_class, Pharmacology, High functioning, law.invention, Young Adult, 03 medical and health sciences, Cognition, 0302 clinical medicine, Double-Blind Method, Randomized controlled trial, law, medicine, Humans, Spiro Compounds, Psychiatry, Receptor, Psychotropic Drugs, Cross-Over Studies, Mechanism (biology), Communication, Middle Aged, medicine.disease, Receptor antagonist, Crossover study, Psychiatry and Mental health, Treatment Outcome, 030104 developmental biology, Social Perception, Autism spectrum disorder, Original Article, Corrigendum, Psychology, 030217 neurology & neurosurgery, Preliminary Data
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::3bb3089c290e8c76df240cee68616bffTest
https://doi.org/10.1038/npp.2016.232Test -
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المؤلفون: D. Vlodavets, Kristy Rose, Edmar Zanoteli, L. Servais, Renata S Scalco, Andrea Klein, Heidemarie Kletzl, Marianne Gerber, Basil T. Darras, M. El-Khairi, Maria Mazurkiewicz-Bełdzińska, Riccardo Masson, J. Day, Giovanni Baranello, Ksenija Gorni, Eugenio Mercuri, O. Bloespflug-Tanguy, H. Xiong, Nicolas Deconinck, A. Dodman
المصدر: Neuromuscular Disorders. 30:S126
مصطلحات موضوعية: Neurology, business.industry, Anesthesia, Pediatrics, Perinatology and Child Health, medicine, Neurology (clinical), Spinal muscular atrophy, medicine.disease, SMA, business, Genetics (clinical)
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::83865779a0847b36f213b06279b35686Test
https://doi.org/10.1016/j.nmd.2020.08.270Test -
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المؤلفون: Agnès Poirier, Lutz Mueller, Heidemarie Kletzl, Chien-Ping Ko, Stefan Kustermann, Omar Khwaja, Hasane Ratni, Zhihua Feng, Johan Bylund, Bjoern Jacobsen, Michael Reutlinger, Melanie Guérard, Emmanuel Pinard, Sergey Paushkin, John D. Baird, Nikolai Naryshkin, Stefanie Bendels, Anne Marquet, Nora Denk, Xin Zhao, Philippe Jablonski, Martin Ebeling, Luke Green, Friedrich Metzger, Andreas Zeller, Barbara Mueller, Karen S. Chen, Marla Weetall
المصدر: Journal of medicinal chemistry. 61(15)
مصطلحات موضوعية: 0301 basic medicine, Drug discovery, Chemistry, Gene splicing, RNA Splicing, Survival of motor neuron, Spinal muscular atrophy, medicine.disease, Bioinformatics, SMA, Clinical trial, Muscular Atrophy, Spinal, Survival of Motor Neuron 2 Protein, 03 medical and health sciences, 030104 developmental biology, Pyrimidines, RNA splicing, Drug Discovery, medicine, Molecular Medicine, Animals, Humans, Dosing, Safety, Azo Compounds
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::7d9e69d504357bfed8927794453d1858Test
https://pubmed.ncbi.nlm.nih.gov/30044619Test