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المؤلفون: Laurent Gouya, D. Montgomery Bissell, David J. Kuter, Marianne T. Sweetser, Herbert L. Bonkovsky, Paolo Ventura, Paula Aguilera Peiró, Eliane Sardh, Karl E. Anderson, Jeeyoung Oh, Penelope E. Stein, Zhaowei Hua, John J. Ko, Susana Monroy
المصدر: American Journal of Gastroenterology. 116:S545-S546
مصطلحات موضوعية: Acute hepatic porphyria, medicine.medical_specialty, Hepatology, Randomized controlled trial, business.industry, law, Internal medicine, Gastroenterology, Medicine, In patient, business, Interim analysis, law.invention
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::7211b2ec87cf0d20182a2ccd4827c613Test
https://doi.org/10.14309/01.ajg.0000778212.30789.aeTest -
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المؤلفون: Matthew T. White, Michael Polydefkis, Marianne T. Sweetser, Angela Dispenzieri, John L. Berk, Jing Jing Wang, Julian D. Gillmore, Mathew S. Maurer, Alejandra González-Duarte, Seth Arum, Yoshiki Sekijima
المصدر: European Heart Journal. 41
مصطلحات موضوعية: medicine.medical_specialty, biology, business.industry, MedDRA, Mortality rate, Amyloidosis, Cardiomyopathy, Atrial fibrillation, medicine.disease, Gastroenterology, Transthyretin, Internal medicine, Cohort, medicine, biology.protein, In patient, Adverse effect, Cardiology and Cardiovascular Medicine, business, Polyneuropathy
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::b7b0521a23e3a0e4f52208d9be9a8155Test
https://doi.org/10.1093/ehjci/ehaa946.2129Test -
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المؤلفون: Taro Yamashita, Jaclyn Franklin, Laura Obici, Julian D. Gillmore, Thomas H. Brannagan, Alejandra González-Duarte, Jihong Chen, Marianne T. Sweetser, Matthias Schilling, Peter D. Gorevic, Jing Jing Wang, Céline Labeyrie, David Adams, Hartmut Schmidt, Arnt V. Kristen, Teresa Coelho, John L. Berk, Senda Ajroud-Driss
المصدر: Repositório Científico de Acesso Aberto de Portugal (Repositórios Cientìficos)
Agência para a Sociedade do Conhecimento (UMIC)-FCT-Sociedade da Informação
instacron:RCAAPمصطلحات موضوعية: Oncology, Adult, Male, medicine.medical_specialty, patisiran, Adolescent, hereditary transthyretin-mediated amyloidosis, 030204 cardiovascular system & hematology, 03 medical and health sciences, Polyneuropathies, Young Adult, 0302 clinical medicine, Quality of life, RNA interference, Internal medicine, APOLLO, Internal Medicine, Medicine, Humans, Prealbumin, Norfolk QOL-DN, In patient, RNA, Small Interfering, Aged, Aged, 80 and over, Amyloid Neuropathies, Familial, biology, business.industry, Amyloidosis, Middle Aged, medicine.disease, Placebo Effect, humanities, Multisystem disease, Transthyretin, quality of life, Mutation, biology.protein, Quality of Life, Female, business, 030217 neurology & neurosurgery
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::02d16f0eb1c0040f9c7946c39acb5c5cTest
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4
المؤلفون: Paolo Ventura, Bruce Wang, Manisha Balwani, Marianne T. Sweetser, Manish Thapar, Zhaowei Hua, Kei-ichiro Takase, Ilja Kubisch, David Cassiman
المصدر: American Journal of Gastroenterology. 116:S504-S504
مصطلحات موضوعية: Acute hepatic porphyria, medicine.medical_specialty, Hepatology, business.industry, Internal medicine, Gastroenterology, medicine, In patient, business, Disease burden
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::4edf2caa72042a5c57b9479b23d941c8Test
https://doi.org/10.14309/01.ajg.0000777784.56221.d2Test -
5
المؤلفون: Alejandra González-Duarte, Erhan Berber, Marianne T. Sweetser, Davide Adams, Teresa Coelho, Elizabeth Mauricio, Jing Jing Wang, Marco Luigetti, Michael Polydefkis, Matthew T. White, Thomas H. Brannagan, Jonas Wixner, Hartmut Schmidt
المصدر: Journal of the Neurological Sciences. 429:117766
مصطلحات موضوعية: medicine.medical_specialty, Neurology, business.industry, Amyloidosis, medicine, In patient, Neurology (clinical), Extension (predicate logic), Open label, medicine.disease, business, Surgery
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::8685d85d0e9132d669c70b2604f03338Test
https://doi.org/10.1016/j.jns.2021.117766Test -
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المؤلفون: Teresa Coelho, John L. Berk, Isabel Conceição, Céline Tard, Madeline Merkel, Jing Jing Wang, Hartmut Schmidt, Dianna Quan, Alejandra González-Duarte, Márcia Waddington-Cruz, Cécile Cauquil, Michael Polydefkis, Mitsuharu Ueda, Michelle L. Mauermann, Arnt V. Kristen, Marianne T. Sweetser, Emre Aldinc, Jihong Chen, David Adams
المصدر: Journal of Neurology. 267:713-714
مصطلحات موضوعية: Oncology, medicine.medical_specialty, Neurology, biology, business.industry, Amyloidosis, medicine.disease, Transthyretin, RNA interference, Internal medicine, biology.protein, medicine, In patient, Neurology (clinical), business, Neuroradiology
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::fd66aab996a7cb3e1ee81afac36eb4adTest
https://doi.org/10.1007/s00415-020-09715-5Test -
7
المؤلفون: Mazen Hanna, Pushkal Garg, Arnt V. Kristen, Akshay Vaishnaw, Marianne T. Sweetser, Christine Powell, Verena Karsten, Julian D. Gillmore, Rodney H. Falk, Xiaoping Zhang, Mathew S. Maurer, Philip N. Hawkins, Daniel P. Judge, Jamie Harrop, John Vest, Martha Grogan
المصدر: Cardiovascular Drugs and Therapy. 34:889-889
مصطلحات موضوعية: 0301 basic medicine, medicine.medical_specialty, Cardiomyopathy, 030204 cardiovascular system & hematology, 03 medical and health sciences, 0302 clinical medicine, Internal medicine, Medicine, Pharmacology (medical), In patient, Interventricular septum, Pharmacology, biology, business.industry, Amyloidosis, General Medicine, medicine.disease, Transthyretin, 030104 developmental biology, medicine.anatomical_structure, Multicenter study, biology.protein, Cardiology, Cardiology and Cardiovascular Medicine, business, Wall thickness, Attr amyloidosis
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::e0bc0bd56844fc2433386c22184287a6Test
https://doi.org/10.1007/s10557-020-07023-8Test -
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المؤلفون: Michael Polydefkis, Kon-Ping Lin, A Gonzalez-Duarte, PJ Gandhi, Arnt V. Kristen, D Adams, Ole B. Suhr, Apollo Study Investigators, Chih-Chao Yang, Matthew T. White, Hartmut Schmidt, Marianne T. Sweetser, Jared Gollob, T Coelho, John L. Berk, Ivaylo Tournev
المصدر: Canadian Journal of Neurological Sciences / Journal Canadien des Sciences Neurologiques. 46:S20
مصطلحات موضوعية: medicine.medical_specialty, biology, business.industry, Amyloidosis, General Medicine, Disease, medicine.disease, Placebo, 03 medical and health sciences, Transthyretin, 0302 clinical medicine, Neurology, Tolerability, 030220 oncology & carcinogenesis, Internal medicine, biology.protein, Medicine, In patient, Neurology (clinical), Dosing, business, Polyneuropathy, 030217 neurology & neurosurgery
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::942a5ce736dc3006b2aea1aa18a2b7b4Test
https://doi.org/10.1017/cjn.2019.124Test