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المؤلفون: Emily Symington, Glenn F. Pierce, Adam Giermasz, K. John Pasi, Stefan Tiefenbacher, Stephen J. Zoog, Mary Robinson, Savita Rangarajan, Steffen Rosen, Christian Vettermann, Donnie Mackenzie, Jaydeep K. Srimani, Benjamin Kim, Mei Huang, Terri Christianson
المصدر: Blood. 136:2524-2534
مصطلحات موضوعية: Male, congenital, hereditary, and neonatal diseases and abnormalities, Genetic enhancement, Transgene, Immunology, 030204 cardiovascular system & hematology, Pharmacology, Hemophilia A, Biochemistry, Virus, law.invention, 03 medical and health sciences, 0302 clinical medicine, Thrombin, Parvovirinae, law, hemic and lymphatic diseases, medicine, Humans, media_common.cataloged_instance, Transgenes, European union, media_common, Factor VIII, business.industry, Genetic Therapy, Cell Biology, Hematology, Dependovirus, Coagulation, Recombinant DNA, Specific activity, business, 030215 immunology, medicine.drug
وصف الملف: text
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::b7b54fc4a67379b3e101a905a194db2aTest
https://doi.org/10.1182/blood.2020005683Test -
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المؤلفون: K. John Pasi, P. Batty
المصدر: Expert Review of Precision Medicine and Drug Development. 4:259-262
مصطلحات موضوعية: Pharmacology, congenital, hereditary, and neonatal diseases and abnormalities, medicine.medical_specialty, business.industry, Genetic enhancement, Haemophilia A, Haemophilia, medicine.disease, Gastroenterology, Coagulation, hemic and lymphatic diseases, Internal medicine, Drug Discovery, Genetics, medicine, Molecular Medicine, Haemophilia B, business, Factor IX, medicine.drug
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::0dcccfbfcfd11cb978b0ca784b79d9f0Test
https://doi.org/10.1080/23808993.2019.1632704Test -
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المؤلفون: Tara M Robinson, Savita Rangarajan, K. John Pasi, Michael Laffan, Emily Symington, Will Lester, Bella Madan, Wing Yen Wong, Glenn F. Pierce, Xinqun Yang, Benjamin Kim, Nina Mitchell
المساهمون: Apollo - University of Cambridge Repository
المصدر: Haemophilia : the official journal of the World Federation of Hemophilia. 27(6)
مصطلحات موضوعية: FVIII, Male, congenital, hereditary, and neonatal diseases and abnormalities, medicine.medical_specialty, IMPACT, Genetic enhancement, Haemophilia A, haemophilia A, Hemorrhage, Haemophilia, Hemophilia A, Gastroenterology, PROPHYLAXIS, Hemostatics, Quality of life, QUALITY-OF-LIFE, hemic and lymphatic diseases, Internal medicine, medicine, Humans, Adverse effect, Genetics (clinical), Science & Technology, Factor VIII, business.industry, 1103 Clinical Sciences, ADULTS, Hematology, General Medicine, Genetic Therapy, medicine.disease, Confidence interval, Cardiovascular System & Hematology, Tolerability, Child, Preschool, haemostasis, Cohort, Quality of Life, business, Life Sciences & Biomedicine
وصف الملف: text/xml; application/pdf
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::0c531853ba9fa59e5941dee55d492e2dTest
https://pubmed.ncbi.nlm.nih.gov/34378280Test -
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المؤلفون: Cedric Hermans, Maria Elisa Mancuso, K. John Pasi, Beatrice Nolan
المساهمون: UCL - SSS/IREC/CARD - Pôle de recherche cardiovasculaire, UCL - (SLuc) Service d'hématologie
المصدر: European Journal of Haematology
European journal of haematology, Vol. 106, no. 6, p. 745-761 (2021)مصطلحات موضوعية: medicine.medical_specialty, immune tolerance, Recombinant Fusion Proteins, Haemophilia A, Once weekly, factor VIII‐Fc fusion protein, haemophilia A, Review Article, Haemophilia, Hemophilia A, Recombinant factor viii, 03 medical and health sciences, Therapeutic approach, 0302 clinical medicine, hemic and lymphatic diseases, half‐life, medicine, Humans, Factor VIII-Fc fusion protein, Intensive care medicine, surgical haemostasis, rFVIIIFc, Clinical Trials as Topic, Factor VIII, business.industry, Prophylaxis, Immune tolerance, Hematology, General Medicine, medicine.disease, Half-life, Immunoglobulin Fc Fragments, Fc fusion, Patient need, 030220 oncology & carcinogenesis, recombinant fusion proteins, prophylaxis, business, Dosing Frequency, 030215 immunology
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::1f5f34e0da36f347a33816459b9017d8Test
https://pubmed.ncbi.nlm.nih.gov/33650192Test -
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المؤلفون: K. John Pasi, David Lillicrap, Wendy Scales, Johnny Mahlangu, Steven W. Pipe, Flora Peyvandi, Claire McLintock, Alok Srivastava, Thierry VandenDriessche
المساهمون: Basic (bio-) Medical Sciences, Division of Gene Therapy & Regenerative Medicine
المصدر: Research and Practice in Thrombosis and Haemostasis
Research and Practice in Thrombosis and Haemostasis, Vol 4, Iss 4, Pp 644-651 (2020)مصطلحات موضوعية: medicine.medical_specialty, congenital, hereditary, and neonatal diseases and abnormalities, physicians, media_common.quotation_subject, Original Article: Hemostasis, knowledge gaps, Therapeutic approach, Internal medicine, Perception, hemic and lymphatic diseases, hemophilia, Health care, respondents, medicine, survey, media_common, Medicine(all), Response rate (survey), Hematology, Science & Technology, Descriptive statistics, lcsh:RC633-647.5, business.industry, International survey, lcsh:Diseases of the blood and blood-forming organs, gene therapy, Clinical trial, Peripheral Vascular Disease, Family medicine, Cardiovascular System & Cardiology, Original Article, business, Life Sciences & Biomedicine
وصف الملف: Electronic-eCollection
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::824eec794b75031ac5e6486507506fedTest
https://lirias.kuleuven.be/handle/20.500.12942/703877Test -
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المؤلفون: Roseline d'Oiron, Katarina Steen Carlsson, Radoslaw Kaczmarek, Mehdi Osooli, Alec Miners, David Perry, Paul Giangrande, Nanda Uitslager, Brian O'Mahony, John Pasi, Rosie Haldon, Françoise Boehlen, Daniel P. Hart, Miguel Crato, Gianna Franca Rivolta, Daniela Janeckova, Erik Berntorp, Maria Elisa Mancuso, Elizabete Cebura, Steve Kitchen
المصدر: European Journal of Haematology, Vol. 97 Suppl 83 (2016) pp. 3-18
مصطلحات موضوعية: ddc:616, congenital, hereditary, and neonatal diseases and abnormalities, Pediatrics, medicine.medical_specialty, Health professionals, business.industry, Hematology, General Medicine, Computer-assisted web interviewing, Treatment team, 030204 cardiovascular system & hematology, Haemophilia, medicine.disease, Patient care, 03 medical and health sciences, Pharmacoeconomics, 0302 clinical medicine, Multidisciplinary approach, hemic and lymphatic diseases, Family medicine, medicine, Disease management (health), business, 030215 immunology
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::7cdf3edc35194dfa01485c6ca39b0437Test
https://doi.org/10.1111/ejh.12760Test -
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المؤلفون: Hua Yu, Michael Laffan, Liron Walsh, Savita Rangarajan, David Perry, Glenn F. Pierce, Christian Vettermann, Wing Yen Wong, K. John Pasi, Will Lester, Bella Madan
مصطلحات موضوعية: 0301 basic medicine, Serotype, Adult, Male, medicine.medical_specialty, Genetic enhancement, VARIANT, Genetic Vectors, Hemorrhage, Antibodies, Viral, Hemophilia A, Gastroenterology, THERAPY, Virus, PROPHYLAXIS, 03 medical and health sciences, Young Adult, Medicine, General & Internal, hemic and lymphatic diseases, Internal medicine, General & Internal Medicine, medicine, MANAGEMENT, Humans, RATES, Young adult, Infusions, Intravenous, 11 Medical and Health Sciences, Factor IX, Science & Technology, Factor VIII, biology, business.industry, General Medicine, FACTOR-IX, Genetic Therapy, Dependovirus, Virus Shedding, Clinical trial, MICE, 030104 developmental biology, Cohort, DNA, Viral, biology.protein, TRIAL, Antibody, business, Life Sciences & Biomedicine, medicine.drug
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::4024b00e18bbd0f716af1b6f423e6c1dTest
http://hdl.handle.net/10044/1/57163Test -
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المؤلفون: John Pasi, A. M. Cumming, S. Keeney, Peter William Collins, Anne Goodeve
المصدر: Seminars in Thrombosis and Hemostasis. 37:488-494
مصطلحات موضوعية: congenital, hereditary, and neonatal diseases and abnormalities, Pediatrics, medicine.medical_specialty, MEDLINE, Haemophilia, Von Willebrand factor, hemic and lymphatic diseases, von Willebrand Factor, medicine, Service planning, Von Willebrand disease, Humans, Deamino Arginine Vasopressin, In patient, Desmopressin, Genetic testing, medicine.diagnostic_test, biology, Coagulants, business.industry, Hematology, medicine.disease, United Kingdom, von Willebrand Diseases, Practice Guidelines as Topic, biology.protein, Guideline Adherence, Cardiology and Cardiovascular Medicine, business, medicine.drug
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::32c49bf9a03c3d90443d33da1ec7c934Test
https://doi.org/10.1055/s-0031-1281033Test -
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المؤلفون: Jenny Goudemand, Ian R. Peake, John Pasi, Augusto B. Federici, Javier Batlle, Frank Hill, U. Budde, Claudine Mazurier, Jeroen Eikenboom, Reinhard Schneppenheim, David Habart, Anne Goodeve, K. Bertoncello, Zdena Vorlova, Dominique Meyer, F. Rodeghiero, Jørgen Ingerslev, Giancarlo Castaman, M. Bernardi, Stefan Lethagen, Alberto Tosetto, Lars Holmberg
المصدر: Journal of Thrombosis and Haemostasis. 5:715-721
مصطلحات موضوعية: Adult, Male, congenital, hereditary, and neonatal diseases and abnormalities, medicine.medical_specialty, Adolescent, Ristocetin cofactor activity, Gastroenterology, Cohort Studies, Sex Factors, Von Willebrand factor, hemic and lymphatic diseases, ABO blood group system, Internal medicine, von Willebrand Factor, Von Willebrand disease, Humans, Medicine, Child, Aged, Aged, 80 and over, biology, business.industry, Age Factors, Infant, Hematology, Middle Aged, medicine.disease, Europe, von Willebrand Diseases, Child, Preschool, Immunology, cardiovascular system, biology.protein, Female, business, circulatory and respiratory physiology
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::f84b3e61b16f787db212f2a257a09724Test
https://doi.org/10.1111/j.1538-7836.2007.02444.xTest -
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المؤلفون: Charles R. M. Hay, Frank Hill, Andrea Guilliatt, Peter William Collins, Pamela Grundy, William Lester, Derrick John Bowen, A. M. Cumming, Stephen Keeney, Said Enayat, John Pasi, Paula H B Bolton-Maggs, David Keeling
المصدر: Thrombosis and Haemostasis. 96:630-641
مصطلحات موضوعية: Male, congenital, hereditary, and neonatal diseases and abnormalities, Genotype, Genetic Linkage, DNA Mutational Analysis, Penetrance, Biology, Gene mutation, medicine.disease_cause, Von Willebrand factor, Polymorphism (computer science), hemic and lymphatic diseases, von Willebrand Factor, Von Willebrand disease, medicine, Humans, Family Health, Genetics, Mutation, Polymorphism, Genetic, Haplotype, Hematology, medicine.disease, United Kingdom, Pedigree, von Willebrand Diseases, Haplotypes, Immunology, biology.protein, Female
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::49fb43623c88217b1da3de19baf9c78cTest
https://doi.org/10.1160/th06-07-0383Test