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المؤلفون: Amy D. Shapiro, Roshni Daniel Kulkarni, Margaret V Ragni, Herve Chambost, Johnny N Mahlangu, Johannes Oldenburg, Beatrice Nolan, Margareth C Ozelo, Meredith C Foster, Annemieke Willemze, Chris Barnowski, Nisha Jain, Bent Winding, Jennifer Dumont, Stefan Lethagen, Chris Barnes, K John Pasi
المصدر: Blood Advances.
مصطلحات موضوعية: Hematology
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::9b3492f3b3a5f76dd4bbf7bdc817f3ebTest
https://doi.org/10.1182/bloodadvances.2022009230Test -
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المؤلفون: Tom Burke, Idaira Rodriguez‐Santana, Pratima Chowdary, Randall Curtis, Kate Khair, Michael Laffan, Paul Mclaughlin, Declan Noone, Brian O'Mahony, John Pasi, Mark Skinner, Jamie O'Hara
المصدر: Haemophilia : the official journal of the World Federation of HemophiliaREFERENCES.
مصطلحات موضوعية: Hematology, General Medicine, Genetics (clinical)
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::35794d1084a176cc6c32bfbf26f9b34fTest
https://pubmed.ncbi.nlm.nih.gov/36574369Test -
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المؤلفون: Emily Symington, Glenn F. Pierce, Adam Giermasz, K. John Pasi, Stefan Tiefenbacher, Stephen J. Zoog, Mary Robinson, Savita Rangarajan, Steffen Rosen, Christian Vettermann, Donnie Mackenzie, Jaydeep K. Srimani, Benjamin Kim, Mei Huang, Terri Christianson
المصدر: Blood. 136:2524-2534
مصطلحات موضوعية: Male, congenital, hereditary, and neonatal diseases and abnormalities, Genetic enhancement, Transgene, Immunology, 030204 cardiovascular system & hematology, Pharmacology, Hemophilia A, Biochemistry, Virus, law.invention, 03 medical and health sciences, 0302 clinical medicine, Thrombin, Parvovirinae, law, hemic and lymphatic diseases, medicine, Humans, media_common.cataloged_instance, Transgenes, European union, media_common, Factor VIII, business.industry, Genetic Therapy, Cell Biology, Hematology, Dependovirus, Coagulation, Recombinant DNA, Specific activity, business, 030215 immunology, medicine.drug
وصف الملف: text
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::b7b54fc4a67379b3e101a905a194db2aTest
https://doi.org/10.1182/blood.2020005683Test -
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المؤلفون: Glenn F. Pierce, Johnny Mahlangu, Thomas Sannié, David Lillicrap, Alok Srivastava, Dawn Rottellini, Donna Coffin, Thierry VandenDriessche, K. John Pasi, Radoslaw Kaczmarek, Alain Weill
المساهمون: Basic (bio-) Medical Sciences, Division of Gene Therapy & Regenerative Medicine
المصدر: Haemophilia. 26:443-449
مصطلحات موضوعية: medicine.medical_specialty, Consensus, media_common.quotation_subject, Genetic enhancement, haemophilia, 030204 cardiovascular system & hematology, Hemophilia A, Haemophilia, 03 medical and health sciences, 0302 clinical medicine, Multidisciplinary approach, Voting, medicine, Humans, Challenges, round table, Genetics (clinical), media_common, Medicine(all), business.industry, Health technology, Gene Therapy, Genetic Therapy, Hematology, General Medicine, global, Payment, medicine.disease, Clinical trial, Round table, Family medicine, business, 030215 immunology
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::c38e32ba755156877323ace2a466b82dTest
https://doi.org/10.1111/hae.13971Test -
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المؤلفون: Bent Winding, Keiji Nogami, Guy Young, Chris Barnes, Huixing Yuan, Johannes Oldenburg, Elena Santagostino, Liane Khoo, Beatrice Nolan, Barbara A. Konkle, Joachim Fruebis, K. John Pasi, Ingrid Pabinger, Dan Rudin, Johnny Mahlangu
المصدر: Haemophilia
مصطلحات موضوعية: Adult, Male, medicine.medical_specialty, Adolescent, Recombinant Fusion Proteins, 030204 cardiovascular system & hematology, Haemophilia, Hemophilia A, Recombinant factor viii, bleed rate, 03 medical and health sciences, Young Adult, 0302 clinical medicine, Internal medicine, medicine, Clinical endpoint, Humans, Clinical Haemophilia, Child, Genetics (clinical), rFVIIIFc, Aged, extended half‐life, Factor VIII, business.industry, Hematology, General Medicine, Original Articles, Bleed, Middle Aged, medicine.disease, Confidence interval, Immunoglobulin Fc Fragments, Regimen, Fc fusion, Treatment Outcome, individualized prophylaxis, Child, Preschool, Severe haemophilia A, Original Article, Female, business, perioperative haemostasis, 030215 immunology
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::bd4022ccca7aa7b264ac7e5d898662bfTest
http://europepmc.org/articles/PMC7384031Test -
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المؤلفون: Tara M Robinson, Savita Rangarajan, K. John Pasi, Michael Laffan, Emily Symington, Will Lester, Bella Madan, Wing Yen Wong, Glenn F. Pierce, Xinqun Yang, Benjamin Kim, Nina Mitchell
المساهمون: Apollo - University of Cambridge Repository
المصدر: Haemophilia : the official journal of the World Federation of Hemophilia. 27(6)
مصطلحات موضوعية: FVIII, Male, congenital, hereditary, and neonatal diseases and abnormalities, medicine.medical_specialty, IMPACT, Genetic enhancement, Haemophilia A, haemophilia A, Hemorrhage, Haemophilia, Hemophilia A, Gastroenterology, PROPHYLAXIS, Hemostatics, Quality of life, QUALITY-OF-LIFE, hemic and lymphatic diseases, Internal medicine, medicine, Humans, Adverse effect, Genetics (clinical), Science & Technology, Factor VIII, business.industry, 1103 Clinical Sciences, ADULTS, Hematology, General Medicine, Genetic Therapy, medicine.disease, Confidence interval, Cardiovascular System & Hematology, Tolerability, Child, Preschool, haemostasis, Cohort, Quality of Life, business, Life Sciences & Biomedicine
وصف الملف: text/xml; application/pdf
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::0c531853ba9fa59e5941dee55d492e2dTest
https://pubmed.ncbi.nlm.nih.gov/34378280Test -
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المؤلفون: Pratima Chowdary, Margareta Holmström, Johnny N. Mahlangu, Margaret C. Ozelo, Ingrid Pabinger, K. John Pasi, Margaret V. Ragni, Amy Shapiro, Chris Barnowski, Stefan Lethagen
المصدر: Research and Practice in Thrombosis and Haemostasis. 6:e12760
مصطلحات موضوعية: factor IX fc fusion protein, factor VIII Fc fusion protein, hemophilia A, hemophilia B, recombinant fusion proteins, safety, surgical procedures, Pediatrik, Hematology, Pediatrics
وصف الملف: application/pdf
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::8a1dbc299e18ee716a32cfbf794b52b0Test
https://doi.org/10.1002/rth2.12760Test -
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المؤلفون: John Pasi, Cédric Hermans, Zalmai Hakimi, Jameel Nazir, Samuel Aballéa, Monia Ezzalfani, Francis Fatoye
المساهمون: UCL - SSS/IREC/CARD - Pôle de recherche cardiovasculaire, UCL - (SLuc) Centre de malformations vasculaires congénitales, UCL - (SLuc) Service d'hématologie
المصدر: Therapeutic advances in hematology, Vol. 13, no. 1, p. [1-9] (2022)
مصطلحات موضوعية: health-related quality of life, factor VIII Fc fusion protein, patient-reported outcomes, hemophilia, treatment outcome, pain, Hematology
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::76b3be15becfd148e4a00838f8029577Test
https://pubmed.ncbi.nlm.nih.gov/35237394Test -
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المؤلفون: John Pasi, Desmond Creagh, D. J. Perry, Ruth Pink, Gregory M. Hayes, Amanda Clark, Sylvia Fong, Sophia Stanford, Gillian C. Lowe, Savita Rangarajan, Kandiah Chandrakumaran, Nicola Curry
المصدر: Research and Practice in Thrombosis and Haemostasis
مصطلحات موضوعية: Original Articles: Haemostasis, Serotype, seroprevalence, biology, business.industry, Genetic enhancement, adeno‐associated viral vectors, Hematology, Virus, Viral vector, Cohort, Immunology, biology.protein, Seroprevalence, Medicine, Original Article, hemophilia A, Vector (molecular biology), Antibody, business
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::2476659e13f941e87501a741ca0983e5Test
https://doi.org/10.1002/rth2.12177Test -
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المؤلفون: Roshni Kulkarni, Amy D. Shapiro, Bent Winding, Johan Szamosi, Margareth C. Ozelo, K. John Pasi, Stefan Lethagen, Christopher Barnowski
المصدر: Research and Practice in Thrombosis and Haemostasis
مصطلحات موضوعية: medicine.medical_specialty, 030204 cardiovascular system & hematology, 03 medical and health sciences, 0302 clinical medicine, Interquartile range, Internal medicine, medicine, Dosing interval, In patient, Factor IX, Original Articles: Haemostasis, factor IX, business.industry, Brief Report, clinical trial, Hematology, Bleed, Interim analysis, Clinical trial, 030220 oncology & carcinogenesis, Population study, hemophilia B, recombinant fusion proteins, prophylaxis, business, medicine.drug
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::0b34eec4cf2d99c7830a720ab8d925d8Test
http://europepmc.org/articles/PMC6332734Test