P4.50 Results of prolonged follow-up of late-onset Pompe disease treated with alglucosidase alfa (Myozyme)

التفاصيل البيبلوغرافية
العنوان: P4.50 Results of prolonged follow-up of late-onset Pompe disease treated with alglucosidase alfa (Myozyme)
المؤلفون: P. Laforêt, J.Y. Hogrel, K. Laloui, Robert-Yves Carlier, A. Levy, Anne-Laure Bedat-Millet, I. Durieu, N. Pellegrini, Christine Payan, Claire Wary, Bruno Eymard, Alain Furby, Isabelle Pénisson-Besnier, David Orlikowski, J. Praline, N. Guffon-Fouilhoux
المصدر: Neuromuscular Disorders. 20:673-674
بيانات النشر: Elsevier BV, 2010.
سنة النشر: 2010
مصطلحات موضوعية: Gynecology, medicine.medical_specialty, Neurology, business.industry, Pediatrics, Perinatology and Child Health, medicine, Late onset, Neurology (clinical), business, Alglucosidase alfa, Genetics (clinical), medicine.drug
الوصف: Results of Prolonged Follow-Up of Late-Onset Pompe Disease Treated with Alglucosidase Alfa (Myozyme) P. Laforet; C. Payan; K. Laloui; J-Y. Hogrel; C. Wary; R. Carlier; N. Pellegrini; A-L. Bedat-Millet; . Durieu; A. Furby; I. Penisson-Besnier; J. Praline; D. Orlikowski; N. Guffon-Fouilhoux; A. Levy; and B. Eymard Groupe Hospitalier Pitie-Salpetriere, Assistance Publique-Hopitaux de Paris, Centre de reference de pathologie neuromusculaire Paris-Est, Paris; Institut de Myologie, Hopital Pitie-Salpetriere, Paris; CEA, FBM, MIRCen, IdM NMR Laboratory, Paris; Hopital Raymond Poincare, Garches, Assistance Publique-Hopitaux de Paris; Centre hospitalier de de Rouen; Groupe Hospitalier Lyon Sud; Centre hospitalier de St-Etienne; Centre ospitalier d’Angers; Hopital de Tours; Hopital Edouard Herriot-Centre de Reference des Maladies Hereditaires du Metabolisme de Lyon; Centre hospitalier de Rouen, France
تدمد: 0960-8966
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::6575d92196223f22186af8fa895c0621Test
https://doi.org/10.1016/j.nmd.2010.07.246Test
حقوق: CLOSED
رقم الانضمام: edsair.doi...........6575d92196223f22186af8fa895c0621
قاعدة البيانات: OpenAIRE