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المؤلفون: E. Mercuri, A.M. Seferian, L. Servais, N. Deconinck, H. Stevenson, X. Ni, W. Zhang, L. East, S. Yonren, F. Muntoni, Nicolas Deconinck, Rudy Van Coster, Arnaud Vanlander, Andreea Seferian, Silvana De Lucia, Teresa Gidaro, Laura Vanden Brande, Laurent Servais, Janbernd Kirschner, Sabine Borell, Eugenio Mercuri, Claudia Brogna, Marika Pane, Lavinia Fanelli, Giulia Norcia, Francesco Muntoni, Chiara Brusa, Mary Chesshyre, Kate Maresh, Jaqueline Pitchforth, Lucia Schottlaender, Mariacristina Scoto, Arpana Silwal, Fedrica Trucco
المصدر: Neuromuscular Disorders. 33:476-483
مصطلحات موضوعية: Neurology, Pediatrics, Perinatology and Child Health, Neurology (clinical), Genetics (clinical)
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::010c398abc3705355c31db1d1dedc9efTest
https://doi.org/10.1016/j.nmd.2023.03.008Test -
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المصدر: Frontiers in Genetics, Vol 12 (2021)
مصطلحات موضوعية: matching criteria, inclusion criteria, translational research, trial design, Genetics, Molecular Medicine, QH426-470, Genetics (clinical), duchenne and becker muscular dystrophy, spinal muscular atrophy
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::199440466479084dcd056bb8d9d15c66Test
https://www.frontiersin.org/articles/10.3389/fgene.2021.759994/fullTest