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1دورية أكاديمية
المؤلفون: Michael R. Emami, Alejandro Espinoza, Courtney S. Young, Feiyang Ma, Philip K. Farahat, Philip L. Felgner, Jeffrey S. Chamberlain, Xiangmin Xu, April D. Pyle, Matteo Pellegrini, S. Armando Villalta, Melissa J. Spencer
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 30, Iss , Pp 90-102 (2023)
مصطلحات موضوعية: adeno-associated virus, innate immunity, adaptive immunity, muscular dystrophy, single-cell RNA sequencing, Luminex, Genetics, QH426-470, Cytology, QH573-671
العلاقة: http://www.sciencedirect.com/science/article/pii/S232905012300092XTest; https://doaj.org/toc/2329-0501Test; https://doaj.org/article/5f866c643097449da902b95f356bd37bTest
الإتاحة: https://doi.org/10.1016/j.omtm.2023.06.002Test
https://doaj.org/article/5f866c643097449da902b95f356bd37bTest -
2دورية أكاديمية
المؤلفون: Halli Benasutti, Joseph W. Maricelli, Jane Seto, John Hall, Christine Halbert, Jacqueline Wicki, Lydia Heusgen, Nicholas Purvis, Michael Regnier, David C. Lin, Buel D. Rodgers, Jeffrey S. Chamberlain
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 30, Iss , Pp 65-80 (2023)
مصطلحات موضوعية: gene therapy, fukutin-related protein, FKRP, limb-girdle muscular dystrophy type R9 (LGMDR9), adeno-associated viral vector (AAV), physiology, Genetics, QH426-470, Cytology, QH573-671
العلاقة: http://www.sciencedirect.com/science/article/pii/S2329050123000840Test; https://doaj.org/toc/2329-0501Test; https://doaj.org/article/a9db696fcc7143e8a0480dc385b78ddfTest
الإتاحة: https://doi.org/10.1016/j.omtm.2023.05.022Test
https://doaj.org/article/a9db696fcc7143e8a0480dc385b78ddfTest -
3دورية أكاديمية
المؤلفون: Arden B. Piepho, Jeovanna Lowe, Laurel R. Cumby, Lisa E. Dorn, Dana M. Lake, Neha Rastogi, Megan D. Gertzen, Sarah L. Sturgill, Guy L. Odom, Mark T. Ziolo, Federica Accornero, Jeffrey S. Chamberlain, Jill A. Rafael-Fortney
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 28, Iss , Pp 344-354 (2023)
مصطلحات موضوعية: muscular dystrophy, cardiomyopathy, gene therapy, fibrosis, DMD, utrophin, Genetics, QH426-470, Cytology, QH573-671
العلاقة: http://www.sciencedirect.com/science/article/pii/S2329050123000116Test; https://doaj.org/toc/2329-0501Test; https://doaj.org/article/112376132c914e0588ee19091b2c6a91Test
الإتاحة: https://doi.org/10.1016/j.omtm.2023.02.001Test
https://doaj.org/article/112376132c914e0588ee19091b2c6a91Test -
4
المؤلفون: Jeffrey S. Chamberlain, Melissa Robb, Serge Braun, Kristy J. Brown, Olivier Danos, Annie Ganot, Pedro Gonzalez-Alegre, Nina Hunter, Craig McDonald, Carl Morris, Mark Tobolowsky, Kathryn R. Wagner, Olivia Ziolkowski, Dongsheng Duan
المصدر: Human gene therapy, vol 34, iss 9-10
مصطلحات موضوعية: Male, Duchenne muscular dystrophy, Duchenne/ Becker Muscular Dystrophy, Intellectual and Developmental Disabilities (IDD), Clinical Trials and Supportive Activities, Medical Biotechnology, Clinical Sciences, microdystrophin, Regenerative Medicine, Rare Diseases, Clinical Research, Genetics, Humans, Muscular Dystrophy, Molecular Biology, Pediatric, 5.2 Cellular and gene therapies, Gene Transfer Techniques, Skeletal, Genetic Therapy, Gene Therapy, Duchenne, Brain Disorders, AAV vector, Orphan Drug, Musculoskeletal, Molecular Medicine, Muscle, Development of treatments and therapeutic interventions, Biomarkers, Biotechnology
وصف الملف: application/pdf
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::d4cd9d835233f4a077af22bfee836cfcTest
https://escholarship.org/uc/item/0v56c0vkTest -
5دورية أكاديمية
المؤلفون: Chady H. Hakim, Nathalie Clément, Lakmini P. Wasala, Hsiao T. Yang, Yongping Yue, Keqing Zhang, Kasun Kodippili, Laura Adamson-Small, Xiufang Pan, Joel S. Schneider, N. Nora Yang, Jeffrey S. Chamberlain, Barry J. Byrne, Dongsheng Duan
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 18, Iss , Pp 664-678 (2020)
مصطلحات موضوعية: adeno-associated virus, herpes simplex virus, transient transfection, micro-dystrophin, Duchenne muscular dystrophy, mdx4cv, Genetics, QH426-470, Cytology, QH573-671
العلاقة: http://www.sciencedirect.com/science/article/pii/S2329050120301534Test; https://doaj.org/toc/2329-0501Test; https://doaj.org/article/c9a8a753dbc949b9af502c5c8edc3335Test
الإتاحة: https://doi.org/10.1016/j.omtm.2020.07.004Test
https://doaj.org/article/c9a8a753dbc949b9af502c5c8edc3335Test -
6دورية أكاديمية
المؤلفون: Glen B Banks, Jeffrey S Chamberlain, Guy L Odom
المصدر: PLoS Genetics, Vol 16, Iss 11, p e1009179 (2020)
العلاقة: https://doi.org/10.1371/journal.pgen.1009179Test; https://doaj.org/toc/1553-7390Test; https://doaj.org/toc/1553-7404Test; https://doaj.org/article/72d23454fd4f4c8facce98929e058859Test
الإتاحة: https://doi.org/10.1371/journal.pgen.1009179Test
https://doaj.org/article/72d23454fd4f4c8facce98929e058859Test -
7دورية أكاديمية
المؤلفون: Chady H. Hakim, Nalinda B. Wasala, Xiufang Pan, Kasun Kodippili, Yongping Yue, Keqing Zhang, Gang Yao, Brittney Haffner, Sean X. Duan, Julian Ramos, Joel S. Schneider, N. Nora Yang, Jeffrey S. Chamberlain, Dongsheng Duan
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 6, Iss C, Pp 216-230 (2017)
مصطلحات موضوعية: AAV, DMD, micro-dystrophin, mdx, DBA/2J, nNOS, cardiomyopathy, systemic gene therapy, Duchenne muscular dystrophy, adeno-associated virus, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
العلاقة: http://www.sciencedirect.com/science/article/pii/S2329050117300815Test; https://doaj.org/toc/2329-0501Test
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8دورية أكاديمية
المؤلفون: Tahnee L. Kennedy, Simon Guiraud, Ben Edwards, Sarah Squire, Lee Moir, Arran Babbs, Guy Odom, Diane Golebiowski, Joel Schneider, Jeffrey S. Chamberlain, Kay E. Davies
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 11, Iss , Pp 92-105 (2018)
العلاقة: http://www.sciencedirect.com/science/article/pii/S2329050118301013Test; https://doaj.org/toc/2329-0501Test; https://doaj.org/article/b4cdbb1c898240c9ae805bf8b86d8caaTest
الإتاحة: https://doi.org/10.1016/j.omtm.2018.10.005Test
https://doaj.org/article/b4cdbb1c898240c9ae805bf8b86d8caaTest -
9
المصدر: Mol Ther
مصطلحات موضوعية: Male, Necrosis, Duchenne muscular dystrophy, Genetic Vectors, Degeneration (medical), Dystrophin, Mice, 03 medical and health sciences, 0302 clinical medicine, Genome editing, Drug Discovery, Genetics, medicine, Animals, Myocytes, Cardiac, Guide RNA, Muscle, Skeletal, Molecular Biology, 030304 developmental biology, Gene Editing, Pharmacology, 0303 health sciences, biology, Myocardium, Regeneration (biology), Skeletal muscle, Genetic Therapy, Dependovirus, Muscular Dystrophy, Animal, medicine.disease, Cell biology, Mice, Inbred C57BL, Muscular Dystrophy, Duchenne, Disease Models, Animal, medicine.anatomical_structure, 030220 oncology & carcinogenesis, Mutation, biology.protein, Molecular Medicine, Original Article, CRISPR-Cas Systems, medicine.symptom, RNA, Guide, Kinetoplastida
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::418b4b5a189776174b4dca1a60b402ffTest
https://doi.org/10.1016/j.ymthe.2020.11.003Test -
10دورية أكاديمية
المؤلفون: Connie S. Chamberlain, Erin E. Saether, Erdem Aktaş, Ray Vanderby
مصطلحات موضوعية: Adaptation of Tendon and Skeletal Muscle to Mechanical Loading, Orthopedics and Sports Medicine, Medicine, Health Sciences, Wound Healing and Regeneration, Rehabilitation, Multipotent Mesenchymal Stem Cells, Genetics, FOS Biological sciences, Mesenchymal Stem Cells, Wound Healing, Mesenchymal stem cell, Inflammation, Tendon, Wound healing, In vivo, Ligament, Pathology, Immunology, FOS Clinical medicine, Anatomy, Biology, Biotechnology