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1دورية أكاديمية
المؤلفون: Lee Sweeney, H, Finanger, Erika, Neil Knierbein, Erin, Wagner, Kathryn, Mathews, Katherine, Marks, Warren, Statland, Jeffrey, Nance, Jessica, McMillan, Hugh, McCullagh, Gary, Tian, Cuixia, Ryan, Monique, ORourke, Declan, Müller-Felber, Wolfgang, Tulinius, Mar, Burnette, W, Nguyen, Cam-Tu, Vijayakumar, Kayal, Johannsen, Jessika, Phan, Han, Eagle, Michelle, MacDougall, James, Mancini, Maria, Donovan, Joanne, Finkel, Richard, McDonald, Craig
المصدر: Journal of Neuromuscular Diseases. 8(5)
مصطلحات موضوعية: CAT-1004, Duchenne muscular dystrophy, NF-κB, age effects, edasalonexent, Administration, Oral, Arachidonic Acids, Child, Child, Preschool, Double-Blind Method, Humans, Male, Muscular Dystrophy, Duchenne, NF-kappa B, Salicylamides
وصف الملف: application/pdf
الوصول الحر: https://escholarship.org/uc/item/1zj592rqTest
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2دورية أكاديمية
المؤلفون: Blaschek, Astrid, Rodrigues, Martin, Rawer, Rainer, Müller, Christine, Ille, Lena, Schröder, Sebastian, Idriess, Mohamed, Müller-Felber, Wolfgang, Vill, Katharina
المصدر: Neuropediatrics; 2021, Vol. 52 Issue 6, p455-461, 7p
مصطلحات موضوعية: DUCHENNE muscular dystrophy, GROUND reaction forces (Biomechanics), MOTION analysis, PHYSICAL measurements, SUPINE position, JUMPER'S knee
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3دورية أكاديمية
المؤلفون: Saffari, Afshin, Cannet, Claire, Blaschek, Astrid, Hahn, Andreas, Hoffmann, Georg F., Johannsen, Jessika, Kirsten, Romy, Kockaya, Musa, Kölker, Stefan, Müller-Felber, Wolfgang, Roos, Andreas, Schäfer, Hartmut, Schara, Ulrike, Spraul, Manfred, Trefz, Friedrich K., Vill, Katharina, Wick, Wolfgang, Weiler, Markus, Okun, Jürgen G., Ziegler, Andreas
المصدر: Orphanet Journal of Rare Diseases; 10/20/2021, Vol. 16 Issue 1, p1-16, 16p
مصطلحات موضوعية: SPINAL muscular atrophy, DUCHENNE muscular dystrophy, NEUROMUSCULAR diseases, NEWBORN screening, GENETIC testing, URINE
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4دورية أكاديمية
المؤلفون: Blaschek, Astrid, Rodrigues, Martin, Ille, Lena, Idriess, Mohammed, Well, Therese, Warken, Birgit, Müller, Christine, Hannibal, Iris, Tacke, Moritz, Müller-Felber, Wolfgang, Vill, Katharina
المصدر: Neuropediatrics; 2020, Vol. 51 Issue 5, p342-348, 7p
مصطلحات موضوعية: DUCHENNE muscular dystrophy, SPINAL muscular atrophy, FATIGUE (Physiology)
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5دورية أكاديمية
المؤلفون: Vill, Katharina, Ille, Lena, Schroeder, Sebastian A., Blaschek, Astrid, Müller-Felber, Wolfgang
المصدر: European Journal of Paediatric Neurology; Nov2015, Vol. 19 Issue 6, p640-646, 7p
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6دورية أكاديمية
المؤلفون: Müller-Felber, Wolfgang1 (AUTHOR) wolfgang.mueller-felber@med.uni-muenchen.de
المصدر: Neuropediatrics. 2019, Vol. 50 Issue 6, p412-412. 1p.
مصطلحات موضوعية: *NEUROMUSCULAR diseases, *DUCHENNE muscular dystrophy, *MYASTHENIA gravis, *SPINAL muscular atrophy
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7دورية أكاديمية
المؤلفون: Mercuri, Eugenio1,2 (AUTHOR) eugeniomaria.mercuri@policlinicogemelli.it, Vilchez, Juan J3 (AUTHOR), Boespflug-Tanguy, Odile4,5 (AUTHOR), Zaidman, Craig M6 (AUTHOR), Mah, Jean K7 (AUTHOR), Goemans, Nathalie8 (AUTHOR), Müller-Felber, Wolfgang9 (AUTHOR), Niks, Erik H10,11 (AUTHOR), Schara-Schmidt, Ulrike12 (AUTHOR), Bertini, Enrico13 (AUTHOR), Comi, Giacomo P14,15 (AUTHOR), Mathews, Katherine D16,17 (AUTHOR), Servais, Laurent18,19,20 (AUTHOR), Vandenborne, Krista21,22 (AUTHOR), Johannsen, Jessika23 (AUTHOR), Messina, Sonia24 (AUTHOR), Spinty, Stefan25 (AUTHOR), McAdam, Laura26 (AUTHOR), Selby, Kathryn27 (AUTHOR), Byrne, Barry28 (AUTHOR)
المصدر: Lancet Neurology. Apr2024, Vol. 23 Issue 4, p393-403. 11p.
مصطلحات موضوعية: *DUCHENNE muscular dystrophy, *CLINICAL trials, *FACIOSCAPULOHUMERAL muscular dystrophy, *NUCLEAR magnetic resonance spectroscopy, *VASTUS lateralis, *HISTONE deacetylase inhibitors, *CLINICAL trials monitoring
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8دورية أكاديمية
المؤلفون: Dittrich, Sven, Graf, Erika, Trollmann, Regina, Neudorf, Ulrich, Schara, Ulrike, Heilmann, Antje, von der Hagen, Maja, Stiller, Brigitte, Kirschner, Janbernd, Pozza, Robert Dalla, Müller-Felber, Wolfgang, Weiss, Katja, von Au, Katja, Khalil, Markus, Motz, Reinald, Korenke, Christoph, Lange, Martina, Wilichowski, Ekkehard, Pattathu, Joseph, Ebinger, Friedrich
المصدر: Orphanet Journal of Rare Diseases; 5/10/2019, Vol. 14 Issue 1, pN.PAG-N.PAG, 1p
مصطلحات موضوعية: ENALAPRIL, METOPROLOL, LEFT ventricular hypertrophy, DUCHENNE muscular dystrophy, RANDOMIZED controlled trials