-
1
المؤلفون: Isabel Conceição, Marianne T. Sweetser, Emre Aldinc, Céline Tard, Madeline Merkel, Márcia Waddington-Cruz, Dianna Quan, David Adams, Michael Polydefkis, John L. Berk, Jing Jing Wang, Teresa Coelho, Arnt V. Kristen, Alejandra González-Duarte, Mitsuharu Ueda, Jihong Chen, Cécile Cauquil, Michelle L. Mauermann, Hartmut Schmidt
المصدر: Journal of Neurology
مصطلحات موضوعية: Adult, Male, medicine.medical_specialty, Hereditary transthyretin-mediated amyloidosis, Neurology, Orthostatic intolerance, Placebo, Transthyretin, Polyneuropathies, Double-Blind Method, Quality of life, Polyneuropathy, Internal medicine, medicine, Humans, RNA, Small Interfering, Small interfering ribonucleic acid (siRNA), Amyloid Neuropathies, Familial, Original Communication, business.industry, Amyloidosis, Correction, Autonomic nervous system diseases, Middle Aged, medicine.disease, RNAi Therapeutics, Blood pressure, Quality of Life, Patisiran, Female, Neurology (clinical), business, Body mass index
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::4a6304bdfba32573f7ed185e071e1e9fTest
https://doi.org/10.1007/s00415-019-09602-8Test -
2
المؤلفون: Marianne T. Sweetser, Gabriel J. Robbie, Xiaoping Zhang, Varun Goel, Valerie A. Clausen, Husain Attarwala
المصدر: Journal of Clinical Pharmacology
مصطلحات موضوعية: Male, patisiran, Therapeutics, Pharmacology, Placebo, 030226 pharmacology & pharmacy, small interfering ribonucleic acid (siRNA), 03 medical and health sciences, Polyneuropathies, 0302 clinical medicine, Pharmacokinetics, Double-Blind Method, pharmacokinetics (PK), Medicine, Humans, Prealbumin, Pharmacology (medical), Dosing, RNA, Small Interfering, Adverse effect, Aged, Amyloid Neuropathies, Familial, biology, Dose-Response Relationship, Drug, business.industry, Amyloidosis, Middle Aged, pharmacodynamics (PD), medicine.disease, Transthyretin, RNAi Therapeutics, Treatment Outcome, Liver, 030220 oncology & carcinogenesis, Pharmacodynamics, Liposomes, biology.protein, Nanoparticles, Administration, Intravenous, Female, exposure‐response, business, Polyneuropathy, hereditary transthyretin‐mediated amyloidosis (hATTR)
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::9565a43aa8b1fa7cdcb2fe7d26f12920Test
https://pubmed.ncbi.nlm.nih.gov/31322739Test -
3
المؤلفون: Xiaojun You, James G. Krueger, Firas Hougeir, Adam J. Friedman, Nisha Lucas, Marianne T. Sweetser, Jacob Elkins, Steven J. Greenberg, Wanda Castro-Borrero, Leon H Kircik, Peter McCroskery
المصدر: Advances in Therapy
مصطلحات موضوعية: Adult, Male, medicine.medical_specialty, Daclizumab, MedDRA, Phases of clinical research, Dermatology, Antibodies, Monoclonal, Humanized, Severity of Illness Index, Skin Diseases, Gastroenterology, 030207 dermatology & venereal diseases, 03 medical and health sciences, Multiple Sclerosis, Relapsing-Remitting, 0302 clinical medicine, Double-Blind Method, Internal medicine, Severity of illness, medicine, Humans, Pharmacology (medical), Adverse effect, Daclizumab high-yield process, Original Research, Cutaneous events, Medicine(all), business.industry, Incidence, Multiple sclerosis, Interferon beta-1a, General Medicine, Middle Aged, Interferon beta, medicine.disease, Rash, Treatment Outcome, Neurology, Immunoglobulin G, Immunology, Relapsing-remitting multiple sclerosis, Female, Safety, medicine.symptom, business, 030217 neurology & neurosurgery, medicine.drug
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::a38992de9f4f237336503be280f49005Test
https://doi.org/10.1007/s12325-016-0353-2Test -
4
المؤلفون: Marianne T. Sweetser, Ludwig Kappos, Steven Greenberg, Michael Kaufman, Alexey Boyko, Katherine Riester, Douglas L. Arnold, Gilmore O'neill, Heinz Wiendl, Krzysztof Selmaj, Jacob Elkins, John W. Rose, Eva Havrdova
المصدر: New England Journal of Medicine. 373:1418-1428
مصطلحات موضوعية: Adult, Male, medicine.medical_specialty, Daclizumab, medicine.drug_class, Phases of clinical research, Kaplan-Meier Estimate, Antibodies, Monoclonal, Humanized, Monoclonal antibody, Gastroenterology, Multiple Sclerosis, Relapsing-Remitting, Adjuvants, Immunologic, Double-Blind Method, Interferon, Internal medicine, Humans, Medicine, IL-2 receptor, business.industry, Multiple sclerosis, Interferon beta-1a, Interferon-beta, General Medicine, Middle Aged, medicine.disease, Endocrinology, Immunoglobulin G, Monoclonal, Disease Progression, Female, business, Immunosuppressive Agents, medicine.drug
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::063f9f5cd3c15f0e97211149013b459dTest
https://doi.org/10.1056/nejmoa1501481Test -
5
المؤلفون: Hartmut Schmidt, Jeeyoung Oh, Yesim Parman, Teresa Coelho, Byoung Joon Kim, Akshay Vaishnaw, Ole B. Suhr, Chih-Chao Yang, Scott D. Solomon, Pushkal Garg, Sunita Goyal, Ivailo Tournev, Andrew Strahs, John L. Berk, Pritesh Gandhi, Shahram Attarian, Violaine Planté-Bordeneuve, Alejandra González-Duarte, Arnt V. Kristen, William O'Riordan, Kon Ping Lin, Mitsuharu Ueda, Philip N. Hawkins, Michelle M. Mezei, Jared Gollob, Jihong Chen, David Adams, Saraswathy V. Nochur, Thomas H. Brannagan, Peter J. Dyck, Josep M. Campistol, Giuseppe Vita, Marianne T. Sweetser, Michael Polydefkis, Yoshiki Sekijima, Juan Buades
المساهمون: Universitat de Barcelona
المصدر: Dipòsit Digital de la UB
Universidad de Barcelona
Recercat. Dipósit de la Recerca de Catalunya
instnameمصطلحات موضوعية: Male, Tafamidis, Administration, Intravenous, Adult, Aged, Aged, 80 and over, Amyloid Neuropathies, Familial, Disease Progression, Double-Blind Method, Edema, Female, Gait Disorders, Neurologic, Humans, Infusions, Intravenous, Least-Squares Analysis, Middle Aged, Polyneuropathies, Prealbumin, Quality of Life, RNA, Small Interfering, Severity of Illness Index, Walk Test, RNAi Therapeutics, Medicine (all), 030204 cardiovascular system & hematology, chemistry.chemical_compound, 0302 clinical medicine, Clinical trials, RNA interference, biology, Amyloidosis, General Medicine, 03 medical and health sciences, medicine, business.industry, RNA, medicine.disease, Clinical trial, Transthyretin, chemistry, biology.protein, Cancer research, Amiloïdosi, Amyloid cardiomyopathy, business, human activities, 030217 neurology & neurosurgery, Assaigs clínics
وصف الملف: application/pdf
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::b94e90139b6836f8b7a776e1f046b770Test
http://hdl.handle.net/2445/138257Test -
6
المؤلفون: Marianne T. Sweetser, Kye Gilder, Jeffrey L. Kaine, Maria Greenwald, Matthew D. Linnik, William Shergy
المصدر: Arthritis & Rheumatism. 63:622-632
مصطلحات موضوعية: Adult, Male, medicine.medical_specialty, Adolescent, medicine.medical_treatment, Immunology, Arthritis, Antibodies, Monoclonal, Humanized, Placebo, Gastroenterology, Receptors, Tumor Necrosis Factor, Etanercept, Arthritis, Rheumatoid, Placebos, Antibodies, Monoclonal, Murine-Derived, Young Adult, Double-Blind Method, Rheumatology, immune system diseases, Internal medicine, medicine, Adalimumab, Humans, Immunology and Allergy, Pharmacology (medical), Infusions, Intravenous, Aged, Tumor Necrosis Factor-alpha, business.industry, Middle Aged, medicine.disease, TNF inhibitor, Surgery, Methotrexate, Antirheumatic Agents, Immunoglobulin G, Rheumatoid arthritis, Acute Disease, Drug Therapy, Combination, Female, Rituximab, business, medicine.drug
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::65fb1a7344eace7169330615794eeb89Test
https://doi.org/10.1002/art.30194Test -
7
المؤلفون: J. Theodore Phillips, Mark Novas, Vissia Viglietta, Christian Sindic, Eva Havrdova, Robert J. Fox, Michael Hutchinson, Mariko Kita, Kartik Raghupathi, Katherine Dawson, David Miller, Minhua Yang, Marianne T. Sweetser
المساهمون: UCL - SSS/IONS/CEMO - Pôle Cellulaire et moléculaire
المصدر: The New England journal of medicine, Vol. 367, no. 12, p. 1087-97 (2012)
مصطلحات موضوعية: Male, Adult, medicine.medical_specialty, Pathology, Dimethyl Fumarate, etiology, Aucun, Administration, Oral, drug therapy, pathology, Infections, Placebo, Gastroenterology, law.invention, chemistry.chemical_compound, Multiple Sclerosis, Relapsing-Remitting, Randomized controlled trial, Double-Blind Method, Fumarates, law, Internal medicine, Teriflunomide, medicine, Humans, Glatiramer acetate, Intention-to-treat analysis, Dimethyl fumarate, business.industry, Multiple sclerosis, Brain, Glatiramer Acetate, General Medicine, Middle Aged, medicine.disease, administration & dosage, adverse effects, therapeutic use, Magnetic Resonance Imaging, Intention to Treat Analysis, Clinical trial, chemistry, Female, business, Peptides, Infection, Immunosuppressive Agents, medicine.drug
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::a543316638f263a695777e838ca797abTest
https://hdl.handle.net/2078.1/124404Test