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المصدر: Methods in molecular biology (Clifton, N.J.). 2429
مصطلحات موضوعية: Gene Editing, Mice, Hematopoietic Stem Cell Transplantation, Animals, CRISPR-Cas Systems, Hematopoietic Stem Cells, Transplantation, Autologous
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=pmid________::f37000b493dbbf652092021a66bc6c91Test
https://pubmed.ncbi.nlm.nih.gov/35507170Test -
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المؤلفون: Nithin Sam Ravi, Beeke Wienert, Stacia K Wyman, Henry William Bell, Anila George, Gokulnath Mahalingam, Jonathan T Vu, Kirti Prasad, Bhanu Prasad Bandlamudi, Nivedhitha Devaraju, Vignesh Rajendiran, Nazar Syedbasha, Aswin Anand Pai, Yukio Nakamura, Ryo Kurita, Muthuraman Narayanasamy, Poonkuzhali Balasubramanian, Saravanabhavan Thangavel, Srujan Marepally, Shaji R Velayudhan, Alok Srivastava, Mark A DeWitt, Merlin Crossley, Jacob E Corn, Kumarasamypet M Mohankumar
المصدر: eLife. 11
مصطلحات موضوعية: beta-hemoglobinopathies, chromosomes, base editing, globin regulation, Anemia, Sickle Cell, CD34+HSPCs, beta-Globins, hpfh mutations, HBGpromoter, General Biochemistry, Genetics and Molecular Biology, Cell Line, Large deletions, Promoter Regions, beta-thalassemia, Cytosine, Rare Diseases, Genetic, crispr/cas9, Stem Cell Research - Nonembryonic - Human, genomics, Humans, Point Mutation, 2.1 Biological and endogenous factors, gamma-Globins, Clustered Regularly Interspaced Short Palindromic Repeats, genetics, Aetiology, Promoter Regions, Genetic, Cas9, Fetal Hemoglobin, Beta hemoglobinopathies, Gene Editing, Sickle Cell Disease, General Immunology and Microbiology, Adenine, General Neuroscience, beta-Thalassemia, Anemia, Hematology, General Medicine, Hematopoietic Stem Cells, Stem Cell Research, Sickle Cell, CRISPR, gene expression, cd34+ hspcs, Biochemistry and Cell Biology, CRISPR-Cas Systems
وصف الملف: application/pdf
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::4f78cde1e11fa893229a5ef068cfa673Test
https://doi.org/10.7554/elife.65421Test