المؤلفون: Servais, L.¹ (AUTHOR), Al-Muhaizea, M.² (AUTHOR), Farrar, M.³ (AUTHOR), Nelson, L.⁴ (AUTHOR), Prufer, A.⁵ (AUTHOR), Finkel, R.⁶ (AUTHOR), Wang, Y.⁷ (AUTHOR), Zanoteli, E.⁸ (AUTHOR), El-Khairi, M.⁹ (AUTHOR), Gerber, M.¹⁰ (AUTHOR), Gorni, K.¹⁰ (AUTHOR), Kletzl, H.¹¹ (AUTHOR), Palfreeman, L.⁹ (AUTHOR), Scalco, R.¹⁰ (AUTHOR), Bertini, E.¹² (AUTHOR)

المصدر: Neuromuscular Disorders. 2021 Supplement 1, Vol. 31, pS48-S48. 1p.

مصطلحات موضوعية: *SPINAL muscular atrophy, *CLINICAL trials, *INFANTS

المؤلفون: Baranello, G.¹, Servais, L.², Day, J.³, Deconinck, N.⁴, Mercuri, E.⁵, Klein, A.⁶, Darras, B.⁷, Masson, R.¹, Kletzl, H.⁸, Cleary, Y.⁸, Armstrong, G.⁹, Seabrook, T.⁸, Czech, C.⁸, Gerber, M.⁸, Gelblin, K.⁸, Gorni, K.⁸, Khwaja, O.⁸

المصدر: Neuromuscular Disorders. Oct2018:Supplement 2, Vol. 28, pS109-S109. 1p.

مصطلحات موضوعية: *TREATMENT of spinal muscular atrophy, *SPINAL muscular atrophy, *CLINICAL trials, *PATIENTS

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المصدر: Neuromuscular Disorders. Oct2018:Supplement 2, Vol. 28, pS108-S108. 1p.

مصطلحات موضوعية: *TREATMENT of spinal muscular atrophy, *SPINAL muscular atrophy, *CLINICAL trials, *PATIENTS