المؤلفون: Rebecca A. Crow, Kimberly A. Hart, Michael P. McDermott, Rabi Tawil, William B. Martens, Barbara E. Herr, Elaine McColl, Jennifer Wilkinson, Janbernd Kirschner, Wendy M. King, Michele Eagle, Mary W. Brown, Deborah Hirtz, Hanns Lochmuller, Volker Straub, Emma Ciafaloni, Perry B. Shieh, Stefan Spinty, Anne-Marie Childs, Adnan Y. Manzur, Lucia Morandi, Russell J. Butterfield, Iain Horrocks, Helen Roper, Kevin M. Flanigan, Nancy L. Kuntz, Jean K. Mah, Leslie Morrison, Basil T. Darras, Maja von der Hagen, Ulrike Schara, Ekkehard Wilichowski, Tiziana Mongini, Craig M. McDonald, Giuseppe Vita, Richard J. Barohn, Richard S. Finkel, Matthew Wicklund, Hugh J. McMillan, Imelda Hughes, Elena Pegoraro, W. Bryan Burnette, James F. Howard, Mathula Thangarajh, Craig Campbell, Robert C. Griggs, Kate Bushby, Michela Guglieri

المصدر: Trials, Vol 19, Iss 1, Pp 1-9 (2018)

مصطلحات موضوعية: Clinical trial, Academic-led clinical trial, Clinical trial regulations, Duchenne muscular dystrophy, Rare disease, Medicine (General), R5-920

وصف الملف: electronic resource

العلاقة: http://link.springer.com/article/10.1186/s13063-018-2645-0Test; https://doaj.org/toc/1745-6215Test

الوصول الحر: https://doaj.org/article/59fc2ba5f36543fab1efe37a189c7b3fTest

المؤلفون: Ulrike Schara, Deborah Hirtz, Mary W. Brown, James F. Howard, W. Bryan Burnette, Nancy L. Kuntz, Maja von der Hagen, Lucia Morandi, Tiziana Mongini, Janbernd Kirschner, Emma Ciafaloni, Basil T. Darras, Richard J. Barohn, Giuseppe Vita, Michela Guglieri, Robert C. Griggs, Hanns Lochmüller, Elaine McColl, Kimberly A. Hart, Adnan Y. Manzur, Anne Marie Childs, Kate Bushby, William B. Martens, Craig Campbell, Elena Pegoraro, Kevin M. Flanigan, Barbara E. Herr, Rabi Tawil, Imelda Hughes, Russell J. Butterfield, Jennifer Wilkinson, Matthew Wicklund, Richard S. Finkel, Iain Horrocks, Helen Roper, Rebecca A. Crow, Perry B. Shieh, Hugh J. McMillan, Wendy King, Michael P. McDermott, Stefan Spinty, Mathula Thangarajh, Leslie Morrison, Ekkehard Wilichowski, Volker Straub, Craig M. McDonald, Jean K. Mah, M. Eagle

المصدر: Paediatrics Publications
Trials, Vol 19, Iss 1, Pp 1-9 (2018)
Trials

مصطلحات موضوعية: Budgets, Duchenne muscular dystrophy, Research design, Time Factors, International Cooperation, Medizin, Medicine (miscellaneous), Review, Contracts, Indemnity, Clinical trial regulations, 03 medical and health sciences, Rare Diseases, 0302 clinical medicine, Procurement, Research Support as Topic, Interim, Humans, Multicenter Studies as Topic, Medicine, Pharmacology (medical), Operations management, Academic-led clinical trial, Clinical trial, Rare disease, Clinical Trials as Topic, Muscular Dystrophy, Duchenne, Patient Selection, Steroids, Treatment Outcome, Checklist, Research Design, Muscular Dystrophy, 030212 general & internal medicine, lcsh:R5-920, business.industry, Timeline, Duchenne, 3. Good health, lcsh:Medicine (General), business, 030217 neurology & neurosurgery, Diversity (business)

وصف الملف: application/pdf

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::47306a085861dced47d0a7112cefcd6fTest
https://doi.org/10.1186/s13063-018-2645-0Test

المؤلفون: Adnan Y. Manzur, Wendy King, William B. Martens, Matthew Wicklund, Mary W. Brown, Elena Pegoraro, Tiziana Mongini, Maja von der Hagen, James F. Howard, Emma Ciafaloni, Barbara E. Herr, Tracey Willis, Kimberly A. Hart, Craig Campbell, Rabi Tawil, Imelda Hughes, Richard J. Barohn, Ulrike Schara, Helen Roper, Kevin M. Flanigan, Iain Horrocks, Elaine McColl, Nancy L. Kuntz, Leslie Morrison, Robert C. Griggs, Michael P. McDermott, Stefan Spinty, Russell J. Butterfield, Giovanni Baranello, Deborah Hirtz, Giuseppe Vita, W. Bryan Burnette, Mathula Thangarajh, Basil T. Darras, Ekkehard Wilichowski, Kate Bushby, Anne-Marie Childs, Richard S. Finkel, Craig M. McDonald, Perry B. Shieh, Hugh J. McMillan, Michela Guglieri, Volker Straub, Janbernd Kirschner, Jean K. Mah, M. Eagle, Jennifer Wilkinson

المصدر: Paediatrics Publications

مصطلحات موضوعية: 0301 basic medicine, Male, Pediatrics, Duchenne muscular dystrophy, Vital Capacity, Medizin, Disability Evaluation, 0302 clinical medicine, Prednisone, Pregnenediones, Pharmacology (medical), Muscular Dystrophy, Range of Motion, Articular, Child, Deflazacort, Medicine (all), General Medicine, 3. Good health, Prednisolone, Randomized, Standards of care, Patient Satisfaction, Research Design, Child, Preschool, Heart Function Tests, Corticosteroid, hormones, hormone substitutes, and hormone antagonists, Immunosuppressive Agents, medicine.drug, Range of Motion, medicine.medical_specialty, medicine.drug_class, Article, Drug Administration Schedule, 03 medical and health sciences, Double-Blind Method, medicine, Humans, Muscle Strength, Adverse effect, Preschool, business.industry, medicine.disease, Duchenne, Clinical trial, Muscular Dystrophy, Duchenne, Regimen, 030104 developmental biology, Physical therapy, business, 030217 neurology & neurosurgery, Articular

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::bf91581fa99ab62ae2588e79ef0ddf18Test
https://europepmc.org/articles/PMC6279424Test/

المؤلفون: Florian Stehling, Claudia Schmoor, Janbernd Kirschner, G. Bernert, Simone Thiele, Bernd Reitter, Jürg Lütschg, Rudolf Korinthenberg, Gabriele Ihorst, Gert Wiegand, Maja von der Hagen, Ekkehard Wilichowski, Ulrike Schara, Elke Hobbiebrunken, Georg M. Stettner, Ulrike Grieben, Simone Weiss, Joachim Schessl, Wolfgang Müller-Felber

المصدر: The Lancet. Neurology. 9(11)

مصطلحات موضوعية: Male, medicine.medical_specialty, Duchenne muscular dystrophy, Medizin, Placebo, law.invention, 03 medical and health sciences, 0302 clinical medicine, Randomized controlled trial, Double-Blind Method, law, Prednisone, Internal medicine, medicine, Humans, Muscular dystrophy, Child, 030304 developmental biology, 0303 health sciences, business.industry, Muscle weakness, medicine.disease, Ciclosporin, 3. Good health, Surgery, Clinical trial, Muscular Dystrophy, Duchenne, Review Literature as Topic, Treatment Outcome, Cyclosporine, Neurology (clinical), medicine.symptom, business, 030217 neurology & neurosurgery, medicine.drug

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::657a9863efa0614c6516326217a050a6Test
https://pubmed.ncbi.nlm.nih.gov/21087735Test