نتائج البحث - "Marianne T Sweetser"

المصدر: Orphanet Journal of Rare Diseases
Repositório Científico de Acesso Aberto de Portugal
Repositório Científico de Acesso Aberto de Portugal (RCAAP)
instacron:RCAAP
Orphanet Journal of Rare Diseases, Vol 15, Iss 1, Pp 1-10 (2020)

مصطلحات موضوعية: Tafamidis, medicine.medical_specialty, Neurologi, Cardiomyopathy, lcsh:Medicine, 030204 cardiovascular system & hematology, Gastroenterology, 03 medical and health sciences, chemistry.chemical_compound, RNA interference, 0302 clinical medicine, NA interference, Polyneuropathy, Internal medicine, medicine, Humans, Prealbumin, ATTR amyloidosis, Pharmacology (medical), RNA, Small Interfering, Adverse effect, Genetics (clinical), Amyloid Neuropathies, Familial, biology, business.industry, Research, Amyloidosis, lcsh:R, General Medicine, medicine.disease, Discontinuation, Transthyretin, Neurology, chemistry, Concomitant, Quality of Life, Patisiran, biology.protein, business, 030217 neurology & neurosurgery

وصف الملف: application/pdf

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::4ab76833c3c740a5a556579909bdfbdaTest
https://doi.org/10.1186/s13023-020-01399-4Test

6

Quality of life outcomes in APOLLO, the phase 3 trial of the RNAi therapeutic patisiran in patients with hereditary transthyretin-mediated amyloidosis

المؤلفون: Taro Yamashita, Jaclyn Franklin, Laura Obici, Julian D. Gillmore, Thomas H. Brannagan, Alejandra González-Duarte, Jihong Chen, Marianne T. Sweetser, Matthias Schilling, Peter D. Gorevic, Jing Jing Wang, Céline Labeyrie, David Adams, Hartmut Schmidt, Arnt V. Kristen, Teresa Coelho, John L. Berk, Senda Ajroud-Driss

المصدر: Repositório Científico de Acesso Aberto de Portugal (Repositórios Cientìficos)
Agência para a Sociedade do Conhecimento (UMIC)-FCT-Sociedade da Informação
instacron:RCAAP

مصطلحات موضوعية: Oncology, Adult, Male, medicine.medical_specialty, patisiran, Adolescent, hereditary transthyretin-mediated amyloidosis, 030204 cardiovascular system & hematology, 03 medical and health sciences, Polyneuropathies, Young Adult, 0302 clinical medicine, Quality of life, RNA interference, Internal medicine, APOLLO, Internal Medicine, Medicine, Humans, Prealbumin, Norfolk QOL-DN, In patient, RNA, Small Interfering, Aged, Aged, 80 and over, Amyloid Neuropathies, Familial, biology, business.industry, Amyloidosis, Middle Aged, medicine.disease, Placebo Effect, humanities, Multisystem disease, Transthyretin, quality of life, Mutation, biology.protein, Quality of Life, Female, business, 030217 neurology & neurosurgery

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::02d16f0eb1c0040f9c7946c39acb5c5cTest

7

Global open-label extension: 24-month data of patisiran in patients with HATTR amyloidosis

المؤلفون: Alejandra González-Duarte, Erhan Berber, Marianne T. Sweetser, Davide Adams, Teresa Coelho, Elizabeth Mauricio, Jing Jing Wang, Marco Luigetti, Michael Polydefkis, Matthew T. White, Thomas H. Brannagan, Jonas Wixner, Hartmut Schmidt

المصدر: Journal of the Neurological Sciences. 429:117766

مصطلحات موضوعية: medicine.medical_specialty, Neurology, business.industry, Amyloidosis, medicine, In patient, Neurology (clinical), Extension (predicate logic), Open label, medicine.disease, business, Surgery

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::8685d85d0e9132d669c70b2604f03338Test
https://doi.org/10.1016/j.jns.2021.117766Test

8

Correction to: Analysis of autonomic outcomes in APOLLO, a phase III trial of the RNAi therapeutic patisiran in patients with hereditary transthyretin-mediated amyloidosis

المؤلفون: Teresa Coelho, John L. Berk, Isabel Conceição, Céline Tard, Madeline Merkel, Jing Jing Wang, Hartmut Schmidt, Dianna Quan, Alejandra González-Duarte, Márcia Waddington-Cruz, Cécile Cauquil, Michael Polydefkis, Mitsuharu Ueda, Michelle L. Mauermann, Arnt V. Kristen, Marianne T. Sweetser, Emre Aldinc, Jihong Chen, David Adams

المصدر: Journal of Neurology. 267:713-714

مصطلحات موضوعية: Oncology, medicine.medical_specialty, Neurology, biology, business.industry, Amyloidosis, medicine.disease, Transthyretin, RNA interference, Internal medicine, biology.protein, medicine, In patient, Neurology (clinical), business, Neuroradiology

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::fd66aab996a7cb3e1ee81afac36eb4adTest
https://doi.org/10.1007/s00415-020-09715-5Test

9

Patisiran Pharmacokinetics, Pharmacodynamics, and Exposure-Response Analyses in the Phase 3 APOLLO Trial in Patients With Hereditary Transthyretin-Mediated (hATTR) Amyloidosis

المؤلفون: Marianne T. Sweetser, Gabriel J. Robbie, Xiaoping Zhang, Varun Goel, Valerie A. Clausen, Husain Attarwala

المصدر: Journal of Clinical Pharmacology

مصطلحات موضوعية: Male, patisiran, Therapeutics, Pharmacology, Placebo, 030226 pharmacology & pharmacy, small interfering ribonucleic acid (siRNA), 03 medical and health sciences, Polyneuropathies, 0302 clinical medicine, Pharmacokinetics, Double-Blind Method, pharmacokinetics (PK), Medicine, Humans, Prealbumin, Pharmacology (medical), Dosing, RNA, Small Interfering, Adverse effect, Aged, Amyloid Neuropathies, Familial, biology, Dose-Response Relationship, Drug, business.industry, Amyloidosis, Middle Aged, pharmacodynamics (PD), medicine.disease, Transthyretin, RNAi Therapeutics, Treatment Outcome, Liver, 030220 oncology & carcinogenesis, Pharmacodynamics, Liposomes, biology.protein, Nanoparticles, Administration, Intravenous, Female, exposure‐response, business, Polyneuropathy, hereditary transthyretin‐mediated amyloidosis (hATTR)

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::9565a43aa8b1fa7cdcb2fe7d26f12920Test
https://pubmed.ncbi.nlm.nih.gov/31322739Test

10

Association of Patisiran, an RNA Interference Therapeutic, With Regional Left Ventricular Myocardial Strain in Hereditary Transthyretin Amyloidosis The APOLLO Study

المؤلفون: Verena Karsten, Brian Claggett, David Adams, Rodney H. Falk, John Vest, Scott D. Solomon, Marianne T. Sweetser, Arnt V. Kristen, Jihong Chen, Amil M. Shah, Richard Riese, Masatoshi Minamisawa, Angela Dispenzieri, Giampaolo Merlini, Michel Slama

المساهمون: Harvard Medical School [Boston] (HMS), Shinshu University Hospital, Brigham & Women’s Hospital [Boston] (BWH), AP-HP Hôpital Bicêtre (Le Kremlin-Bicêtre), Petites Molécules de neuroprotection, neurorégénération et remyélinisation, Université Paris-Sud - Paris 11 (UP11)-Institut National de la Santé et de la Recherche Médicale (INSERM), Heidelberg University Hospital [Heidelberg], Università degli Studi di Pavia = University of Pavia (UNIPV), AP-HP - Hôpital Bichat - Claude Bernard [Paris], Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP), Mayo Clinic [Rochester], Alnylam Pharmaceuticals [Cambridge, MA, USA], DESSAIVRE, Louise

المصدر: JAMA Cardiology
JAMA Cardiology, 2019, 4 (5), pp.466-472. ⟨10.1001/jamacardio.2019.0849⟩

مصطلحات موضوعية: Male, medicine.medical_specialty, Heart Ventricles, [SDV]Life Sciences [q-bio], 030204 cardiovascular system & hematology, Placebo, Ventricular Function, Left, law.invention, Placebos, 03 medical and health sciences, Basal (phylogenetics), Polyneuropathies, 0302 clinical medicine, Randomized controlled trial, law, Interquartile range, Internal medicine, medicine, Humans, Prealbumin, 030212 general & internal medicine, RNA, Small Interfering, Infusions, Intravenous, Aged, Amyloid Neuropathies, Familial, business.industry, Amyloidosis, Brief Report, Myocardium, Case-control study, Middle Aged, medicine.disease, Europe, [SDV] Life Sciences [q-bio], Cardiac amyloidosis, Case-Control Studies, North America, Cardiology, Female, Cardiology and Cardiovascular Medicine, business, Polyneuropathy

الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::354ebf51fa5e1986c4992b77d21e916fTest
https://hal-u-picardie.archives-ouvertes.fr/hal-03584074Test

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