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المؤلفون: Nicole Gusset, Caroline Stalens, Mencia de Lemus, Marie-Christine Ouillade, Eva Stumpe, Alexandre Mejat, Lori Klouvi
المصدر: Neuromuscular disorders : NMD. 31(5)
مصطلحات موضوعية: 0301 basic medicine, Gerontology, Adult, Male, Adolescent, Severity of Illness Index, Muscular Atrophy, Spinal, 03 medical and health sciences, Young Adult, 0302 clinical medicine, Disease severity, Surveys and Questionnaires, Agency (sociology), medicine, Daily living, Humans, Child, Genetics (clinical), Aged, Response rate (survey), Aged, 80 and over, business.industry, Infant, Newborn, Infant, Patient Preference, Spinal muscular atrophy, Middle Aged, SMA, medicine.disease, Alternative treatment, Clinical trial, Europe, 030104 developmental biology, Neurology, Child, Preschool, Pediatrics, Perinatology and Child Health, Quality of Life, Female, Neurology (clinical), business, 030217 neurology & neurosurgery
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::9479a236ce3289c803d3b7d88c34e91fTest
https://pubmed.ncbi.nlm.nih.gov/33752935Test -
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المؤلفون: Nicole Gusset, Ria Broekgaarden, Francoise Rouault, Patryk Marczuk, Inge Schwersenz, Vanessa Christie-Brown, Doug Henderson, Gil Bellis, Christian Cottet
المصدر: Neuromuscular disorders : NMD. 27(5)
مصطلحات موضوعية: 0301 basic medicine, Adult, medicine.medical_specialty, Adolescent, media_common.quotation_subject, Disease, 030105 genetics & heredity, Spinal Muscular Atrophies of Childhood, Cohort Studies, 03 medical and health sciences, Young Adult, 0302 clinical medicine, Quality of life (healthcare), Cost of Illness, Perception, Surveys and Questionnaires, Activities of Daily Living, medicine, Humans, Set (psychology), Child, Genetics (clinical), Disease burden, media_common, Aged, business.industry, Infant, Newborn, Infant, Spinal muscular atrophy, Middle Aged, medicine.disease, SMA, Anticipation, Psychological, Europe, Neurology, Child, Preschool, Pediatrics, Perinatology and Child Health, Well-being, Physical therapy, Quality of Life, Neurology (clinical), business, Attitude to Health, 030217 neurology & neurosurgery
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::5c11a1544616a94261515d3f3db7fc0cTest
https://pubmed.ncbi.nlm.nih.gov/28237437Test