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1
المساهمون: National Research Foundation (South Africa), University of KwaZulu-Natal, Ministerio de Ciencia, Innovación y Universidades (España), Agencia Estatal de Investigación (España), Generalitat de Catalunya, Al Musaimi, Othman [0000-0003-2421-1825], Al Shaer, Danah [0000-0001-8488-2706], Albericio, Fernando [0000-0002-8946-0462], de la Torre, Beatriz G. [0000-0001-8521-9172], Al Musaimi, Othman, Al Shaer, Danah, Albericio, Fernando, de la Torre, Beatriz G.
المصدر: Pharmaceuticals, Vol 14, Iss 145, p 145 (2021)
Pharmaceuticals
Digital.CSIC. Repositorio Institucional del CSIC
instnameمصطلحات موضوعية: 0301 basic medicine, 68Ga-PSMA-11, Ga-68-PSMA-11, Oligonucleotides, Pharmaceutical Science, lcsh:Medicine, lcsh:RS1-441, Chemistry, Medicinal, Review, International trade, belantamab mafodotin-blmf, drugs, 0302 clinical medicine, 64Cu-DOTATATE, Belantamab mafodotin-blmf, Viltolarsen, Drug Discovery, Pandemic, Global health, viltolarsen, Pharmacology & Pharmacy, media_common, oligonucleotides, setmelanotide, Setmelanotide, Authorization, lumasiran, 030220 oncology & carcinogenesis, Molecular Medicine, 1115 Pharmacology and Pharmaceutical Sciences, Life Sciences & Biomedicine, FDA, Drug, 2019-20 coronavirus outbreak, Coronavirus disease 2019 (COVID-19), Severe acute respiratory syndrome coronavirus 2 (SARS-CoV-2), media_common.quotation_subject, Cu-64-DOTATATE, Food and drug administration, lcsh:Pharmacy and materia medica, 03 medical and health sciences, Science & Technology, business.industry, lcsh:R, 030104 developmental biology, peptides, Business, Peptides
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::a342a2d01bcf1073cddc0bf3dabe5a82Test
http://hdl.handle.net/10044/1/94838Test -
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المؤلفون: Toshifumi Yokota, Rika Maruyama
المصدر: Journal of Personalized Medicine, Vol 10, Iss 129, p 129 (2020)
Journal of Personalized Medicineمصطلحات موضوعية: 010407 polymers, Genetic Medicine, amyotrophic lateral sclerosis (ALS), Duchenne muscular dystrophy, Medicine (miscellaneous), lcsh:Medicine, golodirsen, Bioinformatics, Eteplirsen, 01 natural sciences, 03 medical and health sciences, medicine, viltolarsen, eteplirsen, Muscular dystrophy, next-generation sequencing (NGS), 030304 developmental biology, 0303 health sciences, business.industry, Gene replacement therapy, lcsh:R, phosphorodiamidate morpholino oligomers (PMOs), multiplex ligation amplification (MLPA), medicine.disease, Exon skipping, 0104 chemical sciences, Editorial, Antisense oligonucleotides, CRISPR (clustered regularly interspaced short palindromic repeat)/Cas9 (CRISPR associated protein 9)-mediated genome editing, Personalized medicine, business, Duchenne/Becker muscular dystrophy (DMD/BMD), exon skipping
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::9eabf38a6b83fc945e8815bea8262ec1Test
https://www.mdpi.com/2075-4426/10/3/129Test -
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المؤلفون: Omar Sheikh, Toshifumi Yokota
المصدر: Journal of Personalized Medicine, Vol 10, Iss 111, p 111 (2020)
Journal of Personalized Medicineمصطلحات موضوعية: musculoskeletal diseases, Sanger sequencing, congenital, hereditary, and neonatal diseases and abnormalities, Duchenne muscular dystrophy, lcsh:Medicine, Medicine (miscellaneous), exon-skipping therapies, Review, golodirsen, Eteplirsen, medicine.disease_cause, multiplex ligation probe amplification (MLPA), 03 medical and health sciences, 0302 clinical medicine, comparative genomic hybridization array (CGH), medicine, viltolarsen, eteplirsen, multiplex polymerase chain reaction (PCR), Multiplex ligation-dependent probe amplification, Muscular dystrophy, next-generation sequencing (NGS), 030304 developmental biology, Genetic testing, Genetics, 0303 health sciences, Mutation, medicine.diagnostic_test, biology, business.industry, lcsh:R, medicine.disease, Duchenne muscular dystrophy (DMD), biology.protein, Personalized medicine, business, Dystrophin, 030217 neurology & neurosurgery
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::cf026a6c6bce5fbba3b9d82ff140ac6eTest
https://doi.org/10.3390/jpm10030111Test