المؤلفون: JARVIS, LISA

المصدر: C&EN Global Enterprise. 5/7/2018, Vol. 96 Issue 19, p13-13. 1/3p.

مصطلحات موضوعية: AUTOPHAGY, LYSOSOMAL storage diseases, GENETIC disorders

المؤلفون: JARVIS, LISA M.

المصدر: Chemical & Engineering News. 5/13/2013, Vol. 91 Issue 19, p10-23. 12p.

مصطلحات موضوعية: LYSOSOMAL storage diseases, GENETIC disorders, LYSOSOMES

People: LEIDER, Justin, LEIDER, Jason

المؤلفون: Krader, Cheryl Guttman, Shovlin, Joseph P. jpshovlin@gmail.com

المصدر: Optometry Times. Apr2012, Vol. 4 Issue 4, p10-10. 1p.

مصطلحات موضوعية: *OPTOMETRISTS, *LYSOSOMAL storage diseases, *CORNEA diseases, *EYE diseases, *DIAGNOSTIC errors, *DIFFERENTIAL diagnosis, *DIAGNOSIS

المصدر: Worldwide Biotech. Aug2018, Vol. 30 Issue 8, pN.PAG-N.PAG. 1p.

مصطلحات موضوعية: *INVESTMENTS, *PHARMACEUTICAL industry, LYSOSOMAL storage diseases, THERAPEUTICS, DRUG development

الشركة/الكيان: BIOGENERATION Ltd.

المصدر: Biotech Business. Mar2018, Vol. 31 Issue 3, p3-N.PAG. 3p.

مصطلحات موضوعية: ORPHAN drugs, LYSOSOMAL storage diseases, NERVOUS system, AUTOSOMAL recessive polycystic kidney, NEURONAL ceroid-lipofuscinosis

الشركة/الكيان: UNITED States. Food & Drug Administration , ABEONA Therapeutics Inc.

المؤلفون: KNUTSEN, REBECCA MAYER

المصدر: Medical Marketing & Media. Mar2016, Vol. 51 Issue 3, p42-44. 3p.

مصطلحات موضوعية: DRUG development, PULMONARY hypertension treatment, PARATHYROID hormone, THERAPEUTICS, LYSOSOMAL storage diseases

الشركة/الكيان: UNITED States. Food & Drug Administration , ACTELION AG , SHIRE AG

المصدر: Biotech Business. Jun2017, Vol. 30 Issue 6, p4-5. 2p.

مصطلحات موضوعية: GENE therapy, GM1 gangliosidosis, GANGLIOSIDES, PHENOTYPES, LYSOSOMAL storage diseases