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1دورية أكاديمية
المصدر: Frontiers in Neurology, Vol 14 (2023)
مصطلحات موضوعية: Duchene muscular dystrophy (DMD), vamorolone, neuromuscular, glucocorticoids, steroid naïve, Neurology. Diseases of the nervous system, RC346-429
وصف الملف: electronic resource
العلاقة: https://www.frontiersin.org/articles/10.3389/fneur.2023.1107474/fullTest; https://doaj.org/toc/1664-2295Test
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2دورية أكاديمية
المؤلفون: Susan Keam
مصطلحات موضوعية: Medicine, vamorolone, First Approval, Adis Drug Review, Adis Insight Report, dissociative corticosteroid, Duchenne Muscular Dystrophy
الإتاحة: https://doi.org/10.6084/m9.figshare.24654435.v1Test
https://figshare.com/articles/online_resource/Vamorolone_First_Approval/24654435Test -
3دورية أكاديمية
المؤلفون: Mukesh Kumar, Venugopalan Y Vishnu
المصدر: Journal of Current Research in Scientific Medicine, Vol 5, Iss 2, Pp 78-84 (2019)
مصطلحات موضوعية: duchenne muscular dystrophy, exon skipping, nusinersen, recent advances, risdiplam, spinal muscular atrophy, vamorolone, zolgensma, Medicine
وصف الملف: electronic resource
العلاقة: http://www.jcrsmed.org/article.asp?issn=2455-3069;year=2019;volume=5;issue=2;spage=78;epage=84;aulast=KumarTest; https://doaj.org/toc/2455-3069Test
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4دورية أكاديمية
المؤلفون: Hoffman, Eric P., Schwartz, Benjamin D., Mengle-Gaw, Laurel J., Smith, Edward C., Castro, Diana, Mah, Jean K., McDonald, Craig M., Kuntz, Nancy L., Finkel, Richard S., Guglieri, Michela, Bushby, Katharine, Tulinius, Mar, Nevo, Yoram, Ryan, Monique M., Webster, Richard, Smith, Andrea L., Morgenroth, Lauren P., Arrieta, Adrienne, Shimony, Maya, Siener, Catherine, Jaros, Mark, Shale, Phil, McCall, John M., Nagaraju, Kanneboyina, van den Anker, John, Conklin, Laurie S., Cnaan, Avital, Gordish-Dressman, Heather, Damsker, Jesse M., Clemens, Paula R.
مصطلحات موضوعية: Clinical trials Observational study (Cohort, Case control), Class IV, Muscle disease, Duchenne muscular dystrophy, vamorolone
جغرافية الموضوع: United States, United Kingdom, Sweden, Israel, Australia
الوقت: Canada
العلاقة: Hoffman EP, Schwartz BD, Mengle-Gaw LJ, Smith EC, Castro D, Mah JK, McDonald CM, Kuntz NL, Finkel RS, Guglieri M, Bushby K, Tulinius M, Nevo Y, Ryan MM, Webster R, Smith AL, Morgenroth LP, Arrieta A, Shimony M, Siener C, Jaros M, Shale P, McCall JM, Nagaraju K, van den Anker J, Conklin LS, Cnaan A, Gordish-Dressman H, Damsker JM, Clemens PR (2019) Vamorolone trial in Duchenne muscular dystrophy shows dose-related improvement of muscle function. Neurology.; http://hdl.handle.net/10255/dryad.208749Test
الإتاحة: https://doi.org/10.5061/dryad.1rd4hc7Test
https://doi.org/10.5061/dryad.1rd4hc7/2Test
https://doi.org/10.1212/WNL.0000000000008168Test
http://hdl.handle.net/10255/dryad.208749Test