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1دورية أكاديمية
المؤلفون: Paul-Smith, MC, Bell, RV, Alton, WE, Alton, EWFW, Griesenbach, U
المساهمون: Medical Research Council (MRC), Cystic Fibrosis Trust
المصدر: 658 ; 649
مصطلحات موضوعية: Science & Technology, Life Sciences & Biomedicine, Pharmacology & Pharmacy, Cystic fibrosis, gene therapy, lung, viral vector, non-viral vector, TRANSMEMBRANE CONDUCTANCE REGULATOR, LONG-TERM SAFETY, NASAL POTENTIAL DIFFERENCE, CHLORIDE TRANSPORT DEFECT, AIRWAY EPITHELIAL-CELLS, PLURIPOTENT STEM-CELLS, PHASE 2B TRIAL, RECOMBINANT ADENOVIRUS, LENTIVIRAL VECTOR, CFTR GENE
العلاقة: Expert Opinion on Orphan Drugs; http://hdl.handle.net/10044/1/32253Test; https://dx.doi.org/10.1080/21678707.2016.1180974Test; MR/J014699/1; VIA 013
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2
المؤلفون: William E. Alton, Robyn V. Bell, Eric W.F.W. Alton, Uta Griesenbach, Michael C. Paul-Smith
المساهمون: Medical Research Council (MRC), Cystic Fibrosis Trust
مصطلحات موضوعية: 0301 basic medicine, CFTR GENE, medicine.medical_specialty, Genetic enhancement, Gene transfer, Disease, Cystic fibrosis, Viral vector, Cftr gene, lung, non-viral vector, CHLORIDE TRANSPORT DEFECT, NASAL POTENTIAL DIFFERENCE, 03 medical and health sciences, 0302 clinical medicine, medicine, PHASE 2B TRIAL, Pharmacology (medical), Pharmacology & Pharmacy, Intensive care medicine, Pharmacology, Toxicology and Pharmaceutics (miscellaneous), Lung function, Science & Technology, business.industry, Health Policy, viral vector, LONG-TERM SAFETY, medicine.disease, gene therapy, AIRWAY EPITHELIAL-CELLS, TRANSMEMBRANE CONDUCTANCE REGULATOR, 030104 developmental biology, 030220 oncology & carcinogenesis, Immunology, LENTIVIRAL VECTOR, Long term safety, business, Life Sciences & Biomedicine, PLURIPOTENT STEM-CELLS, RECOMBINANT ADENOVIRUS
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::762a211af48e785c281409a87a3d6819Test
http://hdl.handle.net/10044/1/32253Test