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1دورية أكاديمية
المؤلفون: Baranello, Giovanni, Mercuri, Eugenio, Stefania Bianchi Marzoli, Claudio Bruno, Marika Pane, Maria Carmela Pera, Giulia Maria Amorelli, Lorenzo Orazi, Giorgia Coratti, Roberto De Sanctis
المساهمون: Baranello, Giovanni, Darras, Basil T, Day, John W, Deconinck, Nicola, Klein, Andrea, Masson, Riccardo, Mercuri, Eugenio, Rose, Kristy, El-Khairi, Muna, Gerber, Marianne, Gorni, Ksenija, Khwaja, Omar, Kletzl, Heidemarie, Scalco, Renata S, Seabrook, Timothy, Fontoura, Paulo, Servais, Laurent, FIREFISH Working Group: Joseph, J Volpe, John, Posner, Armin, Koch, Ulrich, Kellner, Rosaline, Quinlivan, Irina, Balikova, Patricia, Delbeke, Inge, Joniau, Valentine, Tahon, Sylvia, Wittevrongel, Elke De Vos, Edmar, Zanoteli, Rodrigo de Holanda Mendonça, Ciro Matsui Jr, Ana Letícia Fornazieri Darcie, Cleide, Machado, Maria Kiyoko Oyamada, Daniel de Souza Costa, Joyce, Martini, Graziela, Polido, Juliana Rodrigues Iannicelli, Juliana Caires de Oliveira Achili Ferreira, Wang, Yi, Chaoping, Hu, Yiyun, Shi, Shuizhen, Zhou, Xiaomei, Zhu, Chen, Qian, Shen, Li, Ying, Xiao, Zhenxuan, Zhou, Hui, Li, Sujuan, Wang, Hui, Xiong, Tian, Sang, Cuijie, Wei, Jing, Wen, Yiwen, Cao, Wenzhu, Li, Lun, Qin, Nina, Barisic, Ivan, Celovec, Martina Galiot Delic, Petra Kristina Ivkić, Nenad, Vukojević, Ivana, Kern, Boris, Najdanovic, Marin, Skugor, Odile, Boespflug-Tanguy, Teresa, Gidaro, Andrea, Seferian, Emmanuel, Barreau, Elodie Da Cunha, Céline, Lambotin, Nabila, Mnafek, Helene, Peche, Stephanie, Gilabert, Allison, Grange, Charlotte, Lilien, Darko, Milascevic, Ariadna, Perticari, Shotaro, Tachibana, Emanuela, Pagliano, Bianchi Marzoli, Stefania, Diletta, Santarsiero, Myriam Garcia Sierra, Gemma, Tremolada, Maria Teresa Arnoldi, Marta, Vigano, Riccardo, Zanin, Claudio, Bruno, Noemi, Brolatti, Marina, Pedemonte, Enrico, Priolo, Giuseppe, Rao, Enrica, Spaletra, Lorenza, Sposetti, Elisa, Tassara, Simone, Morando, Paola, Tacchetti, Giacomo Pietro Comi, Alessandra, Govoni, Silvia Gabriella Osnaghi
مصطلحات موضوعية: Administration, Oral, Azo Compounds, Dose-Response Relationship, Drug, Female, Humans, Infant, Male, Neuromuscular Agents, Progression-Free Survival, Pyrimidines, RNA Splicing, Respiratory Insufficiency, Respiratory Tract Infections, Spinal Muscular Atrophies of Childhood, Survival of Motor Neuron 1 Protein, Settore MED/26 - NEUROLOGIA, Settore MED/39 - NEUROPSICHIATRIA INFANTILE
العلاقة: info:eu-repo/semantics/altIdentifier/pmid/33626251; info:eu-repo/semantics/altIdentifier/wos/WOS:000687279800011; volume:384; issue:10; firstpage:915; lastpage:923; numberofpages:9; issueyear:2021; journal:NEW ENGLAND JOURNAL OF MEDICINE; http://hdl.handle.net/10807/213685Test; info:eu-repo/semantics/altIdentifier/scopus/2-s2.0-85102430550
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2دورية أكاديمية
المؤلفون: Baranello, Giovanni, Eugenio Mercuri, Marika Pane, Maria Carmela Pera, Giulia Maria Amorelli, Lorenzo Orazi, Giorgia Coratti, Roberto De Sanctis
المساهمون: Darras, Basil T, Masson, Riccardo, Mazurkiewicz-Bełdzińska, Maria, Rose, Kristy, Xiong, Hui, Zanoteli, Edmar, Baranello, Giovanni, Bruno, Claudio, Vlodavets, Dmitry, Wang, Yi, El-Khairi, Muna, Gerber, Marianne, Gorni, Ksenija, Khwaja, Omar, Kletzl, Heidemarie, Scalco, Renata S, Fontoura, Paulo, Servais, Laurent, Joseph J, Volpe, John, Posner, Armin, Koch, Ulrich, Kellner, Rosaline, Quinlivan, Nicolas, Deconinck, Irina, Balikova, Patricia, Delbeke, Inge, Joniau, Valentine, Tahon, Sylvia, Wittevrongel, Elke De Vos, Rodrigo de Holanda Mendonça, Ciro Matsui Jr, Ana Letícia Fornazieri Darcie, Cleide, Machado, Maria Kiyoko Oyamada, Daniel de Souza Costa, Joyce, Martini, Graziela, Polido, Juliana Rodrigues Iannicelli, Juliana Caires de Oliveira Achili Ferreira, Chaoping, Hu, Yiyun, Shi, Shuizhen, Zhou, Xiaomei, Zhu, Chen, Qian, Shen, Li, Ying, Xiao, Zhenxuan, Zhou, Hui, Li, Sujuan, Wang, Tian, Sang, Cuijie, Wei, Jing, Wen, Yiwen, Cao, Wenzhu, Li, Lun, Qin, Nina, Barisic, Ivan, Celovec, Martina, Martina, Galiot, Delic, Petra Kristina Ivkić, Nenad, Vukojević, Ivana, Kern, Boris, Najdanovic, Marin, Skugor, Odile, Boespflug-Tanguy, Teresa, Gidaro, Andrea, Seferian, Emmanuel, Barreau, Elodie Da Cunha, Céline, Lambotin, Nabila, Mnafek, Helene, Peche, Stephanie, Gilabert, Allison, Grange, Charlotte, Lilien, Darko, Milascevic, Ariadna, Perticari, Shotaro, Tachibana, Emanuela, Pagliano, Stefania Bianchi Marzoli, Diletta, Santarsiero, Myriam Garcia Sierra, Gemma, Tremolada, Maria Teresa Arnoldi, Marta, Vigano, Riccardo, Zanin, Noemi, Brolatti, Marina, Pedemonte, Enrico, Priolo, Giuseppe, Rao, Enrica, Spaletra, Lorenza, Sposetti, Elisa, Tassara, Simone, Morando, Paola, Tacchetti, Giacomo Pietro Comi, Alessandra, Govoni, Silvia Gabriella Osnaghi, Valeria, Minorini
مصطلحات موضوعية: Azo Compounds, Female, Historically Controlled Study, Humans, Infant, Male, Motor Skills, Neuromuscular Agents, Progression-Free Survival, Pyrimidines, Severity of Illness Index, Spinal Muscular Atrophies of Childhood, Settore MED/26 - NEUROLOGIA, Settore MED/39 - NEUROPSICHIATRIA INFANTILE
العلاقة: info:eu-repo/semantics/altIdentifier/pmid/34320287; info:eu-repo/semantics/altIdentifier/wos/WOS:000684497600011; volume:385; issue:5; firstpage:427; lastpage:435; numberofpages:9; issueyear:2021; journal:NEW ENGLAND JOURNAL OF MEDICINE; http://hdl.handle.net/10807/213667Test; info:eu-repo/semantics/altIdentifier/scopus/2-s2.0-85111558253
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3دورية أكاديمية
المؤلفون: Giovanni Baranello, Eugenio Mercuri, Marika Pane, Maria Carmela Pera, Giulia Maria Amorelli, Lorenzo Orazi, Giorgia Coratti, Roberto De Sanctis
المساهمون: J Volpe, Joseph, Posner, John, Koch, Armin, Kellner, Ulrich, Quinlivan, Rosaline, Deconinck, Nicola, Balikova, Irina, Delbeke, Patricia, Joniau, Inge, Tahon, Valentine, Wittevrongel, Sylvia, De Vos, Elke, Zanoteli, Edmar, de Holanda Mendonça, Rodrigo, Matsui Jr, Ciro, Letícia Fornazieri Darcie, Ana, Machado, Cleide, Kiyoko Oyamada, Maria, de Souza Costa, Daniel, Martini, Joyce, Polido, Graziela, Rodrigues Iannicelli, Juliana, Caires de Oliveira Achili Ferreira, Juliana, Wang, Yi, Hu, Chaoping, Shi, Yiyun, Zhou, Shuizhen, Zhu, Xiaomei, Qian, Chen, Shen, Li, Xiao, Ying, Zhou, Zhenxuan, Li, Hui, Wang, Sujuan, Xiong, Hui, Sang, Tian, Wei, Cuijie, Wen, Jing, Cao, Yiwen, Li, Wenzhu, Qin, Lun, Barisic, Nina, Celovec, Ivan, Martina, Martina, Delic, Galiot, Kristina Ivkić, Petra, Vukojević, Nenad, Kern, Ivana, Najdanovic, Bori, Skugor, Marin, Servais, Laurent, Boespflug-Tanguy, Odile, Gidaro, Teresa, Seferian, Andrea, Barreau, Emmanuel, Da Cunha, Elodie, Lambotin, Céline, Mnafek, Nabila, Peche, Helene, Gilabert, Stephanie, Grange, Allison, Lilien, Charlotte, Milascevic, Darko, Perticari, Ariadna, Tachibana, Shotaro, Baranello, Giovanni, Masson, Riccardo, Pagliano, Emanuela, Bianchi Marzoli, Stefania, Santarsiero, Diletta, Garcia Sierra, Myriam, Tremolada, Gemma, Teresa Arnoldi, Maria, Vigano, Marta, Zanin, Riccardo, Bruno, Claudio, Brolatti, Noemi, Pedemonte, Marina, Priolo, Enrico, Rao, Giuseppe, Spaletra, Enrica, Sposetti, Lorenza, Tassara, Elisa, Morando, Simone, Tacchetti, Paola, Pietro Comi, Giacomo, Govoni, Alessandra, Gabriella Osnaghi, Silvia, Minorini, Valeria, Abbati, Francesca, Fassini, Federica, Foa, Michaela, Lopopolo, Amalia, Minuti, Elisa, Mercuri, Eugenio Maria, Pane, Marika, Palermo, Concetta, Pera, Maria Carmela, Amorelli, Giulia Maria, Barresi, Costanza
مصطلحات موضوعية: Azo Compounds, Female, Historically Controlled Study, Humans, Infant, Male, Motor Skills, Neuromuscular Agents, Progression-Free Survival, Pyrimidines, Severity of Illness Index, Spinal Muscular Atrophies of Childhood, Settore MED/26 - NEUROLOGIA, Settore MED/39 - NEUROPSICHIATRIA INFANTILE
العلاقة: info:eu-repo/semantics/altIdentifier/pmid/34320287; info:eu-repo/semantics/altIdentifier/wos/WOS:000684497600011; volume:385; issue:5; firstpage:427; lastpage:435; numberofpages:9; issueyear:2021; journal:NEW ENGLAND JOURNAL OF MEDICINE; http://hdl.handle.net/10807/213666Test; info:eu-repo/semantics/altIdentifier/scopus/2-s2.0-85111558253