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1دورية أكاديمية
المؤلفون: Nickel, Miriam, Gissen, Paul, Greenaway, Rebecca, Cappelletti, Simona, Hamborg, Christiane, Ragni, Benedetta, Ribitzki, Tanja, Schulz, Angela, Tondo, Ilaria, Specchio, Nicola
المصدر: Neuropediatrics (2023) (In press).
مصطلحات موضوعية: Science & Technology, Life Sciences & Biomedicine, Clinical Neurology, Pediatrics, Neurosciences & Neurology, CLN2 disease, neuronal ceroid lipofuscinosis, language development, enzyme replacement therapy, cerliponase alfa
وصف الملف: application/pdf
العلاقة: https://discovery.ucl.ac.uk/id/eprint/10173923/1/s-0043-1770143.pdfTest; https://discovery.ucl.ac.uk/id/eprint/10173923Test/
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المؤلفون: Miriam Nickel, Christoph Schwering, Lena Marie Westermann, Eva Wibbeler, Susanne Lezius, Esther M. Maier, Simon Dulz, Angela Schulz
المصدر: Abstracts of the 46th Annual Meeting of the Society for Neuropediatrics.
مصطلحات موضوعية: medicine.medical_specialty, Standard of care, business.industry, medicine, Observational study, Disease, Cerliponase alfa, Intensive care medicine, business
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::ff175d50caae7603b1e91721c665e43eTest
https://doi.org/10.1055/s-0041-1739698Test -
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المؤلفون: H. Cahan, E. de los Reyes, D. Jacoby, Nicola Specchio, F. Genter, Ruth Williams, Paul Gissen, Angela Schulz
المصدر: Neuropediatrics. 47
مصطلحات موضوعية: 0301 basic medicine, Oncology, medicine.medical_specialty, business.industry, General Medicine, Disease, Cerliponase alfa, 03 medical and health sciences, 030104 developmental biology, 0302 clinical medicine, Interim, Internal medicine, Pediatrics, Perinatology and Child Health, Dose escalation, Medicine, Neurology (clinical), Open label, business, 030217 neurology & neurosurgery
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::9035729dd8fff4b41f0989072cad78e4Test
https://doi.org/10.1055/s-0036-1583718Test