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المؤلفون: James Signorovitch, S. Ward, Nathalie Goemans, Eugenio Mercuri, Erin McDonnell, Zhiwen Yao, Gautam Sajeev
المصدر: Neuromuscular Disorders. 27:S232
مصطلحات موضوعية: SIX MINUTE WALK, medicine.medical_specialty, business.industry, Duchenne muscular dystrophy, medicine.disease, Placebo, Clinical trial, Natural history, Physical medicine and rehabilitation, Neurology, Consistency (statistics), Pediatrics, Perinatology and Child Health, medicine, Physical therapy, In patient, Neurology (clinical), business, Genetics (clinical)
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::a5bc1e86978f0c6ec8f9a8e3cca9f398Test
https://doi.org/10.1016/j.nmd.2017.06.493Test -
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المؤلفون: C. Wardell, Nathalie Goemans, Eugenio Mercuri, T. Voit, G. Campion, Craig M. McDonald, R. Wilson
المصدر: Neuromuscular Disorders. 24:829-830
مصطلحات موضوعية: Pediatrics, medicine.medical_specialty, business.industry, Repeated measures design, Placebo, Confidence interval, Prolonged exposure, Walking distance, Standard error, Neurology, Pediatrics, Perinatology and Child Health, Ambulatory, Medicine, Population study, Neurology (clinical), business, Genetics (clinical)
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::f1f94a957fd5c86d92c2d3dd5bad4a30Test
https://doi.org/10.1016/j.nmd.2014.06.129Test -
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المؤلفون: E. Bertini, Anna Lusakowska, L. H. van den Berg, W. Hauke, Bruno Scherrer, P. Berna, C. André, Janbernd Kirschner, Nathalie Goemans, Eugenio Mercuri, Gianluca Vita, M. Mayer, Brigitte Estournet, Brigitte Chabrol, M. Walter, R. Pruss, S. Fontaine-Carbonel, Ulrike Schara, Ksenija Gorni, Claudio Bruno, Wolfgang Müller-Felber, Francesco Muntoni, Nicolas Deconinck, H. Roper, François Rivier, G. Comi, Jean-Marie Cuisset, Eric Dessaud, Hanns Lochmüller, V. Cuvier
المصدر: Neuromuscular Disorders. 24:920-921
مصطلحات موضوعية: medicine.medical_specialty, business.industry, Spinal muscular atrophy, medicine.disease, Placebo, SMA, Surgery, Pulmonary function testing, Clinical trial, chemistry.chemical_compound, Neurology, chemistry, Anesthesia, Pediatrics, Perinatology and Child Health, medicine, Clinical endpoint, Olesoxime, Neurology (clinical), Adverse effect, business, Genetics (clinical)
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::64e01fd40621b2987e5b259c21980ef2Test
https://doi.org/10.1016/j.nmd.2014.06.418Test -
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المؤلفون: T. Voit, C. Wardell, Nathalie Goemans, G. Campion, Eugenio Mercuri, R. Wilson, C. McDonald
المصدر: Neuromuscular Disorders. 24:922
مصطلحات موضوعية: Moderate to severe, medicine.medical_specialty, education.field_of_study, Proteinuria, business.industry, Disease progression, Population, Phases of clinical research, Placebo, Gastroenterology, Surgery, Walking distance, Neurology, Internal medicine, Pediatrics, Perinatology and Child Health, Medicine, Neurology (clinical), medicine.symptom, business, education, Mild disease, Genetics (clinical)
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::b5385ac1d904ef9910e18ec3d2d93465Test
https://doi.org/10.1016/j.nmd.2014.06.422Test -
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المؤلفون: Craig M. McDonald, R. Wilson, T. Voit, G. Campion, Nathalie Goemans, Eugenio Mercuri, C. Wardell
المصدر: Neuromuscular Disorders. 24:829
مصطلحات موضوعية: medicine.medical_specialty, education.field_of_study, business.industry, Beta-2 microglobulin, Gross motor skill, Population, Phases of clinical research, Placebo, Neurology, Disease severity, Internal medicine, Pediatrics, Perinatology and Child Health, Ambulatory, Clinical endpoint, Physical therapy, Medicine, Neurology (clinical), business, education, Genetics (clinical)
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::088faa28aa42a8982ec6c799ae7d1cb2Test
https://doi.org/10.1016/j.nmd.2014.06.128Test -
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المؤلفون: Hermien E. Kan, G. Campion, Erik H. Niks, B.H.A. Wokke, Nathalie Goemans, J.J.G. Verschuuren, Melissa T. Hooijmans
المصدر: Neuromuscular Disorders. 24:852
مصطلحات موضوعية: Muscle tissue, medicine.medical_specialty, business.industry, Duchenne muscular dystrophy, Urology, medicine.disease, Placebo, Exon skipping, Surgery, medicine.anatomical_structure, Neurology, Tibialis anterior muscle, Pediatrics, Perinatology and Child Health, medicine, Clinical endpoint, Biomarker (medicine), Neurology (clinical), business, Genetics (clinical), Drisapersen
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::a4191817da722bd72af1ea7da116a235Test
https://doi.org/10.1016/j.nmd.2014.06.199Test -
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المؤلفون: Nathalie Goemans, A. Morgan, F. Lawrence, R. Wilson, Eugenio Mercuri, L. Callendret, G. Campion, M. Eagle
المصدر: Neuromuscular Disorders. 23:773
مصطلحات موضوعية: medicine.medical_specialty, business.industry, Duchenne muscular dystrophy, Cardiorespiratory fitness, Placebo, medicine.disease, Pulmonary function testing, Clinical trial, Neurology, Quality of life, Concomitant, Pediatrics, Perinatology and Child Health, Physical therapy, Medicine, Neurology (clinical), business, Genetics (clinical), Natural history study
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::69a561f9d9f7039f46b7224116b3acbfTest
https://doi.org/10.1016/j.nmd.2013.06.482Test -
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المؤلفون: Stuart W. Peltz, Gary Elfring, K. Bushby, J. Barth, A. Reha, Craig M. McDonald, Eugenio Mercuri, Nathalie Goemans, Basil T. Darras, Francesco Muntoni
المصدر: Neuromuscular Disorders. 21:651
مصطلحات موضوعية: Pediatrics, medicine.medical_specialty, Neurology, business.industry, Pediatrics, Perinatology and Child Health, Nonsense mutation, Disease progression, Outcome measures, Medicine, Neurology (clinical), Placebo, business, Genetics (clinical)
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::31cac46a94695c6eba31ace942c82659Test
https://doi.org/10.1016/j.nmd.2011.06.793Test