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المؤلفون: Valeria A. Sansone, Marina Pedemonte, Roberto De Sanctis, Enrico Bertini, Claudio Bruno, Francesco Macagno, Michela Catteruccia, Eugenio Mercuri, Alessandra Di Bari, Fabrizio Rao, Adele D'Amico, Marika Pane, Renato Cutrera, Elisabetta Roma, Andrea Lizio, Sonia Messina, Emilio Albamonte, Giuseppe Vita, Alice Pirola, Marco Piastra, Carmela Maria Pera, Francesca Salmin, Maria Sframeli, Giorgia Coratti
المصدر: The Journal of Pediatrics. 219:223-228.e4
مصطلحات موضوعية: Male, Artificial ventilation, medicine.medical_specialty, medicine.medical_treatment, Oligonucleotides, Settore MED/10 - MALATTIE DELL'APPARATO RESPIRATORIO, Spinal Muscular Atrophies of Childhood, SMA1, Cohort Studies, 03 medical and health sciences, Settore MED/39 - NEUROPSICHIATRIA INFANTILE, 0302 clinical medicine, respiratory function, 030225 pediatrics, Internal medicine, medicine, Humans, Respiratory function, Longitudinal Studies, 030212 general & internal medicine, Prospective cohort study, Noninvasive Ventilation, business.industry, Respiration, nusinersen, ventilation, Infant, Spinal muscular atrophy, medicine.disease, Settore MED/26 - NEUROLOGIA, Settore MED/38 - PEDIATRIA GENERALE E SPECIALISTICA, Pediatrics, Perinatology and Child Health, Cohort, Breathing, Female, Nusinersen, business, Cohort study
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::6cb505e3ae92c12af798a472d4b0fb68Test
https://doi.org/10.1016/j.jpeds.2019.12.047Test -
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المؤلفون: Haluk Topaloglu, Janbernd Kirschner, Richard S. Finkel, Wuh-Liang Hwu, Kathryn J. Swoboda, Francy Shu, Julie A. Parsons, Russell J. Butterfield, Darryl C. De Vivo, Thomas O. Crawford, Richard Foster, Nancy L. Kuntz, Wildon Farwell, Yuh-Jyh Jong, T. Ben Omran, Stephanie Fradette, Ishir Bhan, Valeria A. Sansone, Monique M. Ryan, E. Bertini
المصدر: Journal of the Neurological Sciences. 405:250
مصطلحات موضوعية: medicine.medical_specialty, Neurology, business.industry, Interim, medicine, Nusinersen, Neurology (clinical), Spinal muscular atrophy, Stage (cooking), medicine.disease, SMA, business, Surgery
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::f3c5ff7e4c5814c1ec0cbc2f2410b2caTest
https://doi.org/10.1016/j.jns.2019.10.1276Test