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المؤلفون: Eugenio Mercuri, Jean K. Mah, C. Tian, Hoda Abdel-Hamid, Craig M. McDonald, Craig Campbell, J. Statland, Michael Binks, Alesia Sadosky, Lawrence Charnas, Jeffrey P. Palmer, Michela Guglieri, Brenda L. Wong, Francesco Muntoni, Yasuhiro Takeshima, Kathryn R. Wagner, Sarah P. Sherlock, Shannon Marraffino, Anna Kostera-Pruszczyk, Enrico Bertini, Peter I. Karachunski, Russell J. Butterfield, Vivek S. Purohit, Chiara Fiorillo
المصدر: Paediatrics Publications
مصطلحات موضوعية: Male, Duchenne muscular dystrophy, 0301 basic medicine, Pediatrics, medicine.medical_specialty, Adolescent, Antibodies, Monoclonal, Humanized, 03 medical and health sciences, 0302 clinical medicine, Outcome Assessment, Health Care, medicine, Humans, In patient, Treatment Failure, Child, Genetics (clinical), business.industry, Myostatin, medicine.disease, Muscular Dystrophy, Duchenne, myostatin inhibitor, 030104 developmental biology, Neurology, 4-stair climb, Pediatrics, Perinatology and Child Health, Ambulatory, Exercise Test, Neurology (clinical), Open label, domagrozumab, business, 030217 neurology & neurosurgery
وصف الملف: application/pdf
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::8b3cbadea127d4ce51f63126e99cb373Test
https://doi.org/10.1016/j.nmd.2020.05.002Test -
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المؤلفون: Eugenio Mercuri, C. McDonald, Shannon Marraffino, Sarah P. Sherlock, Jean K. Mah, C. Tian, Russell J. Butterfield, Vivek S. Purohit, Kathryn R. Wagner, Michela Guglieri, Hoda Abdel-Hamid, Enrico Bertini, J. Statland, Peter I. Karachunski, Michael Binks, Craig Campbell, Alesia Sadosky, Lawrence Charnas, Brenda L. Wong, Jeffrey P. Palmer, Yasuhiro Takeshima, Chiara Fiorillo, Anna Kostera-Pruszczyk, Francesco Muntoni
المصدر: Neuromuscular Disorders. 31:167-168
مصطلحات موضوعية: medicine.medical_specialty, Physical medicine and rehabilitation, Neurology, business.industry, Duchenne muscular dystrophy, Pediatrics, Perinatology and Child Health, medicine, Neurology (clinical), Open label, medicine.disease, business, Genetics (clinical)
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::8143a42ed208dcffabb620ec8bc9d7adTest
https://doi.org/10.1016/j.nmd.2021.01.001Test -
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المؤلفون: Anna Kamińska, Birgit F. Steffensen, Marta Garami, S. Stringer, I. Tournev, Sunil Rodger, Lenka Pavlovská, Veronika Karcagi, Petr Vondráček, Velina Guergueltcheva, V. Antonova, K. Gramsch, J. Rahbek, Hanns Lochmüller, Lenka Mrázová, Janbernd Kirschner, Anna Lusakowska, A. Mahoney, Petr Brabec, K. Bushby, A. Wasylyszyn, Anna Kostera-Pruszczyk, Agnes Herczegfalvi, J. Vry, N. Catlin
المصدر: Neuromuscular Disorders. 22:886-887
مصطلحات موضوعية: medicine.medical_specialty, Cross-sectional study, business.industry, Duchenne muscular dystrophy, Age at diagnosis, Disease, medicine.disease, Pulmonary function testing, Quality of life (healthcare), Neurology, Family medicine, Pediatrics, Perinatology and Child Health, medicine, Physical therapy, Neurology (clinical), Quality of care, Muscular dystrophy, business, Genetics (clinical)
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::96251efcddad7fa500f59d74a050ec0cTest
https://doi.org/10.1016/j.nmd.2012.06.277Test -
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المؤلفون: Lenka Pavlovská, Janbernd Kirschner, J. Rahbek, Veronika Karcagi, Petr Vondráček, Marta Garami, Agnes Herczegfalvi, A. Stringer, K. Gramsch, J. Vry, A. Wasylyszyn, Hanns Lochmüller, Lenka Mrázová, I. Tournev, A. Mahoney, Sunil Rodger, Anna Kostera-Pruszczyk, Birgit F. Steffensen, Petr Brabec, N. Catlin, K. Bushby, Anna Lusakowska, Velina Guergueltcheva, V. Antonova, Anna Kamińska
المصدر: Neuromuscular Disorders. 22:880
مصطلحات موضوعية: medicine.medical_specialty, Pediatrics, business.industry, Duchenne muscular dystrophy, Research opportunities, medicine.disease, Clinical trial, Patient population, Overall response rate, Neurology, Quality of life, Care Standards, Family medicine, Pediatrics, Perinatology and Child Health, medicine, Neurology (clinical), Genetic diagnosis, business, Genetics (clinical)
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::02281a18605e102257b0b804f163040aTest
https://doi.org/10.1016/j.nmd.2012.06.255Test -
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المؤلفون: Velina Guergueltcheva, V. Antonova, K. Gramsch, Hanns Lochmüller, K. Bushby, Sunil Rodger, A. Højberg, S. Stringer, Veronika Karcagi, P. Brabek, Janbernd Kirschner, Agnes Herczegfalvi, Lenka Mrázová, Anna Kostera-Pruszczyk, J. Rahbek, A. Mahoney, Anna Lusakowska, N. Catlin, Birgit F. Steffensen, J. Vry, A. Wasylyszyn, P. Vondráèek
المصدر: Neuromuscular Disorders. 22:897
مصطلحات موضوعية: medicine.medical_specialty, education.field_of_study, Scope (project management), business.industry, Duchenne muscular dystrophy, Comparability, Population, Frequency of use, Health related, medicine.disease, Neurology, International Classification of Functioning, Disability and Health, Family medicine, Pediatrics, Perinatology and Child Health, medicine, Physical therapy, Cross-cultural, Neurology (clinical), education, business, Genetics (clinical)
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::dae4cba2f227635e66bec334066117aaTest
https://doi.org/10.1016/j.nmd.2012.06.310Test