-
1دورية أكاديمية
المؤلفون: Maria Grazia Biferi, Mathilde Cohen-Tannoudji, Andrea García-Silva, Olga Souto-Rodríguez, Irene Viéitez-González, Beatriz San-Millán-Tejado, Andrea Fernández-Carrera, Tania Pérez-Márquez, Susana Teijeira-Bautista, Soraya Barrera, Vanesa Domínguez, Thibaut Marais, África González-Fernández, Martine Barkats, Saida Ortolano
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 20, Iss , Pp 1-17 (2021)
مصطلحات موضوعية: Fabry disease, lysosomal storage disorders, adeno asociated virus-9, gene therapy, blood brain barrier, gene transfer, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
العلاقة: http://www.sciencedirect.com/science/article/pii/S2329050120302205Test; https://doaj.org/toc/2329-0501Test
-
2دورية أكاديمية
المؤلفون: Nicolas Vignier, Maria Chatzifrangkeskou, Luca Pinton, Hugo Wioland, Thibaut Marais, Mégane Lemaitre, Caroline Le Dour, Cécile Peccate, Déborah Cardoso, Alain Schmitt, Wei Wu, Maria-Grazia Biferi, Naïra Naouar, Coline Macquart, Maud Beuvin, Valérie Decostre, Gisèle Bonne, Guillaume Romet-Lemonne, Howard J. Worman, Francesco Saverio Tedesco, Antoine Jégou, Antoine Muchir
المصدر: Cell Reports, Vol 36, Iss 8, Pp 109601- (2021)
مصطلحات موضوعية: cofilin-1, ERK1/2 signaling, muscular dystrophy, skeletal muscle, sarcomeric organization, Biology (General), QH301-705.5
العلاقة: http://www.sciencedirect.com/science/article/pii/S2211124721010391Test; https://doaj.org/toc/2211-1247Test; https://doaj.org/article/c556bebb8808453e8abeba29fd9a8cdbTest
الإتاحة: https://doi.org/10.1016/j.celrep.2021.109601Test
https://doaj.org/article/c556bebb8808453e8abeba29fd9a8cdbTest