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المؤلفون: L Servais, Ksenija Gorni, Janbernd Kirschner, Y. Cleary, Eugenio Mercuri, W. Yeung, Marianne Gerber, Craig Campbell, Nathalie Goemans, Heidemarie Kletzl, Jeppe Buchbjerg, Omar Khwaja, M Pera, Christian Czech, Giovanni Baranello
المصدر: Canadian Journal of Neurological Sciences / Journal Canadien des Sciences Neurologiques. 46:S31
مصطلحات موضوعية: Oncology, medicine.medical_specialty, business.industry, Survival of motor neuron, General Medicine, SMN1, Spinal muscular atrophy, SMA, Placebo, medicine.disease, nervous system diseases, nervous system, Neurology, Tolerability, Pharmacokinetics, Internal medicine, medicine, Neurology (clinical), Adverse effect, business
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::9a18015a9b40a6ff28a3f3702bb2b47dTest
https://doi.org/10.1017/cjn.2019.163Test -
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المؤلفون: John W. Day, Eugenio Mercuri, Nicolas Deconinck, L Servais, Heidemarie Kletzl, R. Masson, Marianne Gerber, Ksenija Gorni, Y. Cleary, C Cabalteja, Andrea Klein, T. Seabrook, M. El-Khairi, Basil T. Darras, Omar Khwaja, K. Gelblin, Christian Czech, Giovanni Baranello, C. Nguyen
المصدر: Canadian Journal of Neurological Sciences / Journal Canadien des Sciences Neurologiques. 46:S31
مصطلحات موضوعية: 0301 basic medicine, medicine.medical_specialty, business.industry, Survival of motor neuron, General Medicine, Spinal muscular atrophy, SMN1, 030105 genetics & heredity, SMA, Interim analysis, medicine.disease, Gastroenterology, Motor function, nervous system diseases, 03 medical and health sciences, 0302 clinical medicine, Neurology, Pharmacokinetics, Tolerability, Internal medicine, medicine, Neurology (clinical), business, 030217 neurology & neurosurgery
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::193a4e5d38d8fcc2daf66d9496b47a16Test
https://doi.org/10.1017/cjn.2019.164Test