العنوان البديل: Application of adeno-associated virus-mediated gene therapy in lysosomal storage diseases. (English)

المؤلفون: 林雪芹, 王晓乐, 彭镜

المصدر: Chinese Journal of Contemporary Pediatrics; 11/15/2022, Vol. 24 Issue 11, p1281-1287, 7p

مصطلحات موضوعية: ENZYME replacement therapy, GENE therapy, LYSOSOMAL storage diseases, ADENO-associated virus, GENETIC disorders, METABOLIC disorders

المؤلفون: ZHANG Cheng

المصدر: Chinese Journal of Contemporary Neurology & Neurosurgery; Jun2019, Vol. 19 Issue 6, p382-384, 3p

مصطلحات موضوعية: THERAPEUTIC use of enzymes, NEUROMUSCULAR disease diagnosis, NEUROMUSCULAR diseases, ENZYMES, GENE therapy, GENETIC counseling, LYSOSOMAL storage diseases, NERVOUS system, PROFESSIONS, THERAPEUTICS

المؤلفون: GUAN Hong-zhi, CUI Li-ying

المصدر: Chinese Journal of Contemporary Neurology & Neurosurgery; May2014, Vol. 14 Issue 5, p378-381, 4p

مصطلحات موضوعية: LYSOSOMAL storage diseases, MEDICAL protocols, NEUROSURGERY, GLYCOGEN storage disease, NEUROLOGY, DIAGNOSIS, THERAPEUTICS