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1دورية أكاديمية
المؤلفون: Aguisanda, Francis, Yeh, Charles D., Chen, Catherine Z., Rong Li, Beers, Jeanette, Jizhong Zou, Thorne, Natasha, Wei Zheng, Li, Rong, Zou, Jizhong, Zheng, Wei
المصدر: Orphanet Journal of Rare Diseases; 6/28/2017, Vol. 12, p1-13, 13p
مصطلحات موضوعية: STEM cells, WOLMAN disease, LIPIDOSES, GENETIC mutation, DRUGS
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2دورية أكاديمية
المؤلفون: Vu, Mylinh, Li, Rong, Baskfield, Amanda, Lu, Billy, Farkhondeh, Atena, Gorshkov, Kirill, Motabar, Omid, Beers, Jeanette, Chen, Guokai, Zou, Jizhong, Espejo-Mojica, Angela J., Rodríguez-López, Alexander, Alméciga-Díaz, Carlos J., Barrera, Luis A., Jiang, Xuntian, Ory, Daniel S., Marugan, Juan J., Zheng, Wei, Rodríguez-López, Alexander, Alméciga-Díaz, Carlos J
المصدر: Orphanet Journal of Rare Diseases; 9/17/2018, Vol. 13 Issue 1, pN.PAG-N.PAG, 1p
مصطلحات موضوعية: NEURAL stem cells, TAY-Sachs disease, GENETIC mutation, HEXOSAMINIDASE, PLURIPOTENT stem cells, CYCLODEXTRINS
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3دورية أكاديمية
المؤلفون: Sima, Ni, Li, Rong, Huang, Wei, Xu, Miao, Beers, Jeanette, Zou, Jizhong, Titus, Steven, Ottinger, Elizabeth A., Marugan, Juan J., Xie, Xing, Zheng, Wei
المصدر: Orphanet Journal of Rare Diseases; 4/10/2018, Vol. 13 Issue 1, pN.PAG-N.PAG, 1p
مصطلحات موضوعية: NEURONAL ceroid-lipofuscinosis, NEURAL stem cells, INFANT diseases, MEDICAL model, PLURIPOTENT stem cells, VITAMIN E, THERAPEUTICS