التفاصيل البيبلوغرافية
العنوان: |
Efficacy and safety results of the avalglucosidase alfa phase 3 COMET trial in late-onset Pompe disease patients |
المؤلفون: |
John W. Day, Tianyue Zhou, Mazen M. Dimachkie, Joao Lindolfo Borges, Sevim Erdem-Ozdamar, Anna Kostera-Pruszczyk, Shafeeq Ladha, Ozlem Goker-Alpan, Yin-Hsiu Chien, Tahseen Mozaffar, Shahram Attarian, Ans T. van der Ploeg, Priya S. Kishnani, Jordi Díaz-Manera, Kristina An Haack, Young Chul Choi, Olivier Huynh-Ba, Paula R. Clemens, Volker Straub, Mark Roberts, Françoise Bouhour, Hani Kushlaf, Antonio Toscano, Benedikt Schoser, Sergey Illarioshkin |
المصدر: |
Molecular Genetics and Metabolism. 132:S57 |
بيانات النشر: |
Elsevier BV, 2021. |
سنة النشر: |
2021 |
مصطلحات موضوعية: |
medicine.medical_specialty, Endocrinology, business.industry, Endocrinology, Diabetes and Metabolism, Internal medicine, Comet, Genetics, medicine, Late onset, business, Molecular Biology, Biochemistry, Gastroenterology |
تدمد: |
1096-7192 |
الوصول الحر: |
https://explore.openaire.eu/search/publication?articleId=doi_________::9d2e2f2605b089f40f1f662bd16eaaf5Test https://doi.org/10.1016/j.ymgme.2020.12.127Test |
حقوق: |
CLOSED |
رقم الانضمام: |
edsair.doi...........9d2e2f2605b089f40f1f662bd16eaaf5 |
قاعدة البيانات: |
OpenAIRE |