Efficacy and safety results of the avalglucosidase alfa phase 3 COMET trial in late-onset Pompe disease patients

التفاصيل البيبلوغرافية
العنوان: Efficacy and safety results of the avalglucosidase alfa phase 3 COMET trial in late-onset Pompe disease patients
المؤلفون: John W. Day, Tianyue Zhou, Mazen M. Dimachkie, Joao Lindolfo Borges, Sevim Erdem-Ozdamar, Anna Kostera-Pruszczyk, Shafeeq Ladha, Ozlem Goker-Alpan, Yin-Hsiu Chien, Tahseen Mozaffar, Shahram Attarian, Ans T. van der Ploeg, Priya S. Kishnani, Jordi Díaz-Manera, Kristina An Haack, Young Chul Choi, Olivier Huynh-Ba, Paula R. Clemens, Volker Straub, Mark Roberts, Françoise Bouhour, Hani Kushlaf, Antonio Toscano, Benedikt Schoser, Sergey Illarioshkin
المصدر: Molecular Genetics and Metabolism. 132:S57
بيانات النشر: Elsevier BV, 2021.
سنة النشر: 2021
مصطلحات موضوعية: medicine.medical_specialty, Endocrinology, business.industry, Endocrinology, Diabetes and Metabolism, Internal medicine, Comet, Genetics, medicine, Late onset, business, Molecular Biology, Biochemistry, Gastroenterology
تدمد: 1096-7192
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_________::9d2e2f2605b089f40f1f662bd16eaaf5Test
https://doi.org/10.1016/j.ymgme.2020.12.127Test
حقوق: CLOSED
رقم الانضمام: edsair.doi...........9d2e2f2605b089f40f1f662bd16eaaf5
قاعدة البيانات: OpenAIRE