دورية أكاديمية
301 - A safety and efficacy study of lumasiran, an investigational RNA interference (RNAi) therapeutic, in adult and pediatric patients with primary hyperoxaluria type 1.
| العنوان: | 301 - A safety and efficacy study of lumasiran, an investigational RNA interference (RNAi) therapeutic, in adult and pediatric patients with primary hyperoxaluria type 1. |
|---|---|
| المؤلفون: | Frishberg, Y. (AUTHOR), Deschenes, G. (AUTHOR), Cochat, P. (AUTHOR), Magen, D. (AUTHOR), Groothoff, J. (AUTHOR), Hulton, S.A. (AUTHOR), Harambat, J. (AUTHOR), Van't Hoff, W. (AUTHOR), Hoppe, B. (AUTHOR), Lieske, J.C. (AUTHOR), McGregor, T.L. (AUTHOR), Tamimi, N. (AUTHOR), Haslett, P. (AUTHOR), Talamudupula, S. (AUTHOR), Erbe, D.V. (AUTHOR), Milliner, D.S. (AUTHOR) |
| المصدر: | European Urology Supplements. Mar2019, Vol. 18 Issue 1, pe388-e389. 2p. |
| مصطلحات موضوعية: | *RNA interference, *PEDIATRIC nephrology |
| قاعدة البيانات: | Academic Search Index |
| تدمد: | 15699056 |
|---|---|
| DOI: | 10.1016/S1569-9056(19)30291-X |