التفاصيل البيبلوغرافية
العنوان:
Onasemnogene abeparvovec in spinal muscular atrophy: predictors of efficacy and safety in naïve patients with spinal muscular atrophy and following switch from other therapiesResearch in context
المؤلفون:
Marika Pane , Beatrice Berti , Anna Capasso , Giorgia Coratti , Antonio Varone , Adele D’Amico , Sonia Messina , Riccardo Masson , Valeria Ada Sansone , Maria Alice Donati , Caterina Agosto , Claudio Bruno , Federica Ricci , Antonella Pini , Delio Gagliardi , Massimiliano Filosto , Stefania Corti , Daniela Leone , Concetta Palermo , Roberta Onesimo , Roberto De Sanctis , Martina Ricci , Ilaria Bitetti , Maria Sframeli , Claudia Dosi , Emilio Albamonte , Chiara Ticci , Noemi Brolatti , Enrico Bertini , Richard Finkel , Eugenio Mercuri , Maria Carmela Pera , Chiara Bravetti , Marco Piastra , Orazio Genovese , Gianpaolo Cicala , Nicola Forcina , Sara Carnicella , Giulia Stanca , Michele Sacchini , Michela Catteruccia , Michele Tosi , Renato Cutrera , Claudio Chierchi , Maria Beatrice Chiarini , Francesca Salmin , Marina Pedemonte , Alessandra Govoni , Irene Mizzoni , Simone Morando , Riccardo Zanin , Enrica Rolle , Eleonora Salomon , Melania Giannotta , Gaia Scarpini , Antonio Toscano , Eloisa Gitto , Roberto Materia , Rossella D’Alessandro
المصدر:
EClinicalMedicine, Vol 59, Iss , Pp 101997- (2023)
بيانات النشر:
Elsevier, 2023.
سنة النشر:
2023
المجموعة:
LCC:Medicine (General)
مصطلحات موضوعية:
Spinal muscular atrophy , Gene therapy , Follow-up , Longitudinal , Safety , Medicine (General) , R5-920
الوصف:
Summary: Background: Efficacy and safety of onasemnogene abeparvovec (OA) for Spinal Muscular Atrophy infants under 7 months and
نوع الوثيقة:
article
وصف الملف:
electronic resource
اللغة:
English
تدمد:
2589-5370
العلاقة:
http://www.sciencedirect.com/science/article/pii/S2589537023001748Test ; https://doaj.org/toc/2589-5370Test
DOI:
10.1016/j.eclinm.2023.101997
الوصول الحر:
https://doaj.org/article/40165d9821824625a9a6285a88f2fdbcTest
رقم الانضمام:
edsdoj.40165d9821824625a9a6285a88f2fdbc
قاعدة البيانات:
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