التفاصيل البيبلوغرافية
العنوان:
Onasemnogene abeparvovec in spinal muscular atrophy: predictors of efficacy and safety in naïve patients with spinal muscular atrophy and following switch from other therapies
المؤلفون:
Marika Pane , Beatrice Berti , Anna Capasso , Giorgia Coratti , Antonio Varone , Adele D’Amico , Sonia Messina , Riccardo Masson , Valeria Ada Sansone , Maria Alice Donati , Caterina Agosto , Claudio Bruno , Federica Ricci , Antonella Pini , Delio Gagliardi , Massimiliano Filosto , Stefania Corti , Daniela Leone , Concetta Palermo , Roberta Onesimo , Roberto De Sanctis , Martina Ricci , Ilaria Bitetti , Maria Sframeli , Claudia Dosi , Emilio Albamonte , Chiara Ticci , Noemi Brolatti , Enrico Bertini , Richard Finkel , Eugenio Mercuri , Maria Carmela Pera , Chiara Bravetti , Marco Piastra , Orazio Genovese , Gianpaolo Cicala , Nicola Forcina , Sara Carnicella , Giulia Stanca , Michele Sacchini , Michela Catteruccia , Michele Tosi , Renato Cutrera , Claudio Chierchi , Maria Beatrice Chiarini , Francesca Salmin , Marina Pedemonte , Alessandra Govoni , Irene Mizzoni , Simone Morando , Riccardo Zanin , Enrica Rolle , Eleonora Salomon , Melania Giannotta , Gaia Scarpini , Antonio Toscano , Eloisa Gitto , Roberto Materia , Rossella D’Alessandro
المصدر:
eClinicalMedicine . 59:101997
بيانات النشر:
Elsevier BV, 2023.
سنة النشر:
2023
مصطلحات موضوعية:
Gene therapy , Settore MED/39 - NEUROPSICHIATRIA INFANTILE , Settore MED/48 - SCIENZE INFERMIERISTICHE E TECNICHE NEURO-PSICHIATRICHE E RIABILITATIVE , Follow-up , Longitudinal , General Medicine , Safety , Spinal muscular atrophy
تدمد:
2589-5370
الوصول الحر:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::e7d35f824cff5a23c428dd70e02991dbTest https://doi.org/10.1016/j.eclinm.2023.101997Test
حقوق:
OPEN
رقم الانضمام:
edsair.doi.dedup.....e7d35f824cff5a23c428dd70e02991db
قاعدة البيانات:
OpenAIRE