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1
المساهمون: Ginocchio, V. M., Ferla, R., Auricchio, A., Brunetti-Pierri, N.
المصدر: Human gene therapy. 30(10)
مصطلحات موضوعية: Genetic enhancement, Genetic Vectors, inborn errors of metabolism, Gene delivery, Bioinformatics, medicine.disease_cause, Virus, 03 medical and health sciences, Liver disease, adeno-associated virus vector, 0302 clinical medicine, Genome editing, Genetics, Medicine, Animals, Humans, Molecular Biology, Adeno-associated virus, 030304 developmental biology, Gene Editing, 0303 health sciences, Newborn screening, Clinical Trials as Topic, business.industry, Liver Diseases, Lentivirus, Gene Transfer Techniques, AAV, Genetic Therapy, Dependovirus, medicine.disease, gene therapy, Clinical trial, Liver, 030220 oncology & carcinogenesis, Hepatocytes, Molecular Medicine, business, Metabolism, Inborn Errors
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::a0c32744e13353462f9455aeff7facd9Test
https://pubmed.ncbi.nlm.nih.gov/31517544Test -
2
المساهمون: Dimmock, D, BRUNETTI PIERRI, Nicola, Palmer, Dj, Beaudet, Al, Ng, P.
المصدر: Human Gene Therapy. 22:483-488
مصطلحات موضوعية: Crigler–Najjar syndrome, Bilirubin, Genetic enhancement, Genetic Vectors, Rats, Gunn, Pharmacology, Biology, medicine.disease_cause, digestive system, Adenoviridae, chemistry.chemical_compound, Transduction, Genetic, Gene Order, Genetics, medicine, Animals, Molecular Biology, Crigler-Najjar Syndrome, Hyperbilirubinemia, Unconjugated hyperbilirubinemia, Genetic Therapy, medicine.disease, Gunn rat, Uridine, Rats, Disease Models, Animal, Phenotype, Liver, chemistry, Injections, Intravenous, Immunology, Hydrodynamics, Molecular Medicine, Female, Brief Reports, Expression cassette
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::9adba95e6344486ee51b790b4cf6bdc5Test
https://doi.org/10.1089/hum.2010.167Test -
3
المؤلفون: Elizabeth P. Merricks, Stephanie McCorquodale, Timothy C. Nichols, Nicola Brunetti-Pierri, Donna Palmer, Philip Ng, Arthur L. Beaudet
المصدر: Human Gene Therapy. 16:811-820
مصطلحات موضوعية: Genetic enhancement, Genetic Vectors, medicine.disease_cause, Hemophilia B, Virus, Factor IX, Dogs, Genetics, Coagulopathy, medicine, Animals, Aspartate Aminotransferases, Vector (molecular biology), Creatine Kinase, Molecular Biology, biology, business.industry, Fissipedia, Alanine Transaminase, Genetic Therapy, Dependovirus, medicine.disease, biology.organism_classification, Phenotype, Blood Cell Count, Adenoviridae, Liver, Injections, Intravenous, Immunology, Systemic administration, Molecular Medicine, business, Helper Viruses
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::578041b3ca7d90252bf0c2460d028552Test
https://doi.org/10.1089/hum.2005.16.811Test