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1
المساهمون: Ginocchio, V. M., Ferla, R., Auricchio, A., Brunetti-Pierri, N.
المصدر: Human gene therapy. 30(10)
مصطلحات موضوعية: Genetic enhancement, Genetic Vectors, inborn errors of metabolism, Gene delivery, Bioinformatics, medicine.disease_cause, Virus, 03 medical and health sciences, Liver disease, adeno-associated virus vector, 0302 clinical medicine, Genome editing, Genetics, Medicine, Animals, Humans, Molecular Biology, Adeno-associated virus, 030304 developmental biology, Gene Editing, 0303 health sciences, Newborn screening, Clinical Trials as Topic, business.industry, Liver Diseases, Lentivirus, Gene Transfer Techniques, AAV, Genetic Therapy, Dependovirus, medicine.disease, gene therapy, Clinical trial, Liver, 030220 oncology & carcinogenesis, Hepatocytes, Molecular Medicine, business, Metabolism, Inborn Errors
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::a0c32744e13353462f9455aeff7facd9Test
https://pubmed.ncbi.nlm.nih.gov/31517544Test -
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المؤلفون: Pasquale Piccolo, Nicola Brunetti-Pierri
المساهمون: Piccolo, P, BRUNETTI PIERRI, Nicola
المصدر: Human Gene Therapy. 26:186-192
مصطلحات موضوعية: Genetics, Clinical Trials as Topic, Liver Diseases, Genetic enhancement, Genetic Vectors, Genetic Therapy, Biology, Bioinformatics, Genetic therapy, Liver metabolism, Metabolic Diseases, Animals, Humans, Molecular Medicine, Molecular Biology
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::cdd4c2c4d7fd71d1e26e635209e58edcTest
https://doi.org/10.1089/hum.2015.029Test -
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المساهمون: Dindot, S, Piccolo, P, Grove, N, Palmer, D, BRUNETTI PIERRI, Nicola
المصدر: Human Gene Therapy. 22:745-751
مصطلحات موضوعية: Male, Ependymal Cell, Transgene, Genetic enhancement, Genetic Vectors, Central nervous system, Neuroepithelial Cells, Gene Expression, Biology, Adenoviridae, Mice, Transduction (genetics), Cerebrospinal fluid, Transduction, Genetic, Ependyma, Genetics, medicine, Animals, Secretion, Transgenes, Molecular Biology, Injections, Spinal, Neurons, Brief Report, Genetic Therapy, Virology, Cell biology, Mice, Inbred C57BL, Neuroepithelial cell, medicine.anatomical_structure, Molecular Medicine, Helper Viruses
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::77a80a42cf7ee62a236c807fc03874efTest
https://doi.org/10.1089/hum.2010.147Test -
4
المساهمون: Dimmock, D, BRUNETTI PIERRI, Nicola, Palmer, Dj, Beaudet, Al, Ng, P.
المصدر: Human Gene Therapy. 22:483-488
مصطلحات موضوعية: Crigler–Najjar syndrome, Bilirubin, Genetic enhancement, Genetic Vectors, Rats, Gunn, Pharmacology, Biology, medicine.disease_cause, digestive system, Adenoviridae, chemistry.chemical_compound, Transduction, Genetic, Gene Order, Genetics, medicine, Animals, Molecular Biology, Crigler-Najjar Syndrome, Hyperbilirubinemia, Unconjugated hyperbilirubinemia, Genetic Therapy, medicine.disease, Gunn rat, Uridine, Rats, Disease Models, Animal, Phenotype, Liver, chemistry, Injections, Intravenous, Immunology, Hydrodynamics, Molecular Medicine, Female, Brief Reports, Expression cassette
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::9adba95e6344486ee51b790b4cf6bdc5Test
https://doi.org/10.1089/hum.2010.167Test -
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المؤلفون: Yu Zuo, Philip Ng, Rachel Edwards, Nicola Brunetti-Pierri, Donna Palmer, Nathan C Grove, Jun Teruya, Vincenzo Cerullo
المصدر: Human Gene Therapy. 20:479-485
مصطلحات موضوعية: Scientific Articles, Genetic enhancement, Genetic Vectors, Vectors in gene therapy, Hemophilia B, law.invention, Viral vector, Factor IX, Mice, Transduction (genetics), Protein replacement therapy, Therapeutic index, Transduction, Genetic, law, Genetics, Animals, Medicine, Molecular Biology, business.industry, Thrombosis, Genetic Therapy, Protein Structure, Tertiary, Mice, Inbred C57BL, Immunology, Recombinant DNA, Cancer research, Molecular Medicine, business, medicine.drug
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::227acb0e5bf16c4e278b0f436ce8bb7dTest
https://doi.org/10.1089/hum.2008.084Test -
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المؤلفون: Nicola Brunetti-Pierri, Milton J. Finegold, Thomas Ng, William G. Cioffi, Donna Palmer, Arthur L. Beaudet, K. Dee Carey, David A. Iannitti, Philip Ng
المصدر: Human Gene Therapy. 17:391-404
مصطلحات موضوعية: Transgene, Genetic enhancement, Genetic Vectors, Pharmacology, medicine.disease_cause, Inferior vena cava, Transduction (genetics), Drug Delivery Systems, Hepatic Artery, Transduction, Genetic, biology.animal, Genetics, medicine, Animals, Molecular Biology, Chronic toxicity, biology, Portal Vein, Adenoviruses, Human, Liver Diseases, Genetic Therapy, beta-Galactosidase, Immunohistochemistry, Adenoviridae, Liver, medicine.vein, Toxicity, Immunology, Molecular Medicine, Venae Cavae, Helper Viruses, Papio, Baboon
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::5d00cf4f479bddd002ec2bd30c130e65Test
https://doi.org/10.1089/hum.2006.17.391Test -
7
المؤلفون: Elizabeth P. Merricks, Stephanie McCorquodale, Timothy C. Nichols, Nicola Brunetti-Pierri, Donna Palmer, Philip Ng, Arthur L. Beaudet
المصدر: Human Gene Therapy. 16:811-820
مصطلحات موضوعية: Genetic enhancement, Genetic Vectors, medicine.disease_cause, Hemophilia B, Virus, Factor IX, Dogs, Genetics, Coagulopathy, medicine, Animals, Aspartate Aminotransferases, Vector (molecular biology), Creatine Kinase, Molecular Biology, biology, business.industry, Fissipedia, Alanine Transaminase, Genetic Therapy, Dependovirus, medicine.disease, biology.organism_classification, Phenotype, Blood Cell Count, Adenoviridae, Liver, Injections, Intravenous, Immunology, Systemic administration, Molecular Medicine, business, Helper Viruses
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::578041b3ca7d90252bf0c2460d028552Test
https://doi.org/10.1089/hum.2005.16.811Test -
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المؤلفون: Donna Palmer, Philip Ng, Nicola Brunetti-Pierri, Milton J. Finegold, K. Dee Carey, Arthur L. Beaudet
المصدر: Human Gene Therapy. 15:35-46
مصطلحات موضوعية: Male, Indoles, Transgene, Genetic enhancement, Genetic Vectors, medicine.disease_cause, Virus, Adenoviridae, Transduction (genetics), Genes, Reporter, Transduction, Genetic, biology.animal, Genetics, medicine, Animals, Transgenes, Lung, Molecular Biology, biology, Galactosides, Genetic Therapy, Acute toxicity, Liver, Toxicity, Immunology, Molecular Medicine, Spleen, Papio, Baboon
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::a1d234ccd632fa39c5a703345ce60b5dTest
https://doi.org/10.1089/10430340460732445Test -
9
المؤلفون: Alberto Auricchio, Libor Vítek, Rosa Maria Sepe, Nunzia Pastore, Jana Vanikova, Francesco Vetrini, Edoardo Nusco, Antony McDonagh, Nicola Brunetti-Pierri
المساهمون: Pastore, N, Nusco, E, Vaníkova, J, Sepe, Rm, Vetrini, F, Mcdonagh, A, Auricchio, Alberto, Vitek, L, BRUNETTI PIERRI, Nicola
المصدر: Scopus-Elsevier
مصطلحات موضوعية: Bilirubin, Genetic enhancement, Genetic Vectors, Rats, Gunn, Pharmacology, medicine.disease_cause, digestive system, Isozyme, Injections, Intramuscular, chemistry.chemical_compound, Transduction, Genetic, Genetics, medicine, Animals, Bile, Humans, Tissue Distribution, Glucuronosyltransferase, Muscle, Skeletal, Molecular Biology, Adeno-associated virus, Chromatography, High Pressure Liquid, Unconjugated hyperbilirubinemia, Hyperbilirubinemia, biology, Gene Transfer Techniques, Skeletal muscle, Genetic Therapy, Dependovirus, Gunn rat, Rats, Isoenzymes, medicine.anatomical_structure, chemistry, Biochemistry, biology.protein, Molecular Medicine, Creatine kinase
الوصول الحر: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::722321e69246dcc38cb4929711e5fb92Test
https://pubmed.ncbi.nlm.nih.gov/22765254Test