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1دورية أكاديمية
المؤلفون: Catlyn Cavender, Linley Mangini, Jeremy L Van Vleet, Carley Corado, Emma McCullagh, Heather L Gray-Edwards, Douglas R Martin, Brett E Crawford, Roger Lawrence
المصدر: PLoS ONE, Vol 15, Iss 12, p e0243006 (2020)
العلاقة: https://doi.org/10.1371/journal.pone.0243006Test; https://doaj.org/toc/1932-6203Test; https://doaj.org/article/107bc3d828c440d4a76bc745f2d101e6Test
الإتاحة: https://doi.org/10.1371/journal.pone.0243006Test
https://doaj.org/article/107bc3d828c440d4a76bc745f2d101e6Test -
2دورية أكاديمية
المؤلفون: Roger Lawrence, Jeremy L. Van Vleet, Linley Mangini, Adam Harris, Nathan Martin, Wyatt Clark, Sanjay Chandriani, Jonathan H. LeBowitz, Roberto Giugliani, Alessandra d'Azzo, Gouri Yogalingam, Brett E. Crawford
المصدر: Molecular Genetics and Metabolism Reports, Vol 21, Iss , Pp - (2019)
مصطلحات موضوعية: Medicine (General), R5-920, Biology (General), QH301-705.5
العلاقة: http://www.sciencedirect.com/science/article/pii/S2214426919301132Test; https://doaj.org/toc/2214-4269Test; https://doaj.org/article/a0f6f939f66e4358b688b3cdde4ec8b2Test
الإتاحة: https://doi.org/10.1016/j.ymgmr.2019.100524Test
https://doaj.org/article/a0f6f939f66e4358b688b3cdde4ec8b2Test -
3دورية أكاديمية
المؤلفون: Mika Aoyagi-Scharber, Danielle Crippen-Harmon, Roger Lawrence, Jon Vincelette, Gouri Yogalingam, Heather Prill, Bryan K. Yip, Brian Baridon, Catherine Vitelli, Amanda Lee, Olivia Gorostiza, Evan G. Adintori, Wesley C. Minto, Jeremy L. Van Vleet, Bridget Yates, Sara Rigney, Terri M. Christianson, Pascale M.N. Tiger, Melanie J. Lo, John Holtzinger, Paul A. Fitzpatrick, Jonathan H. LeBowitz, Sherry Bullens, Brett E. Crawford, Stuart Bunting
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 6, Iss C, Pp 43-53 (2017)
مصطلحات موضوعية: lysosomal storage disorder, mucopolysaccharidosis IIIB, MPS IIIB, Sanfilippo B, enzyme replacement therapy, intracerebroventricular delivery, glycosaminoglycan, neurodegeneration, mental retardation, Genetics, QH426-470, Cytology, QH573-671
العلاقة: http://www.sciencedirect.com/science/article/pii/S2329050117300748Test; https://doaj.org/toc/2329-0501Test; https://doaj.org/article/391415b4d80b4db49263e27fbcc2640aTest
الإتاحة: https://doi.org/10.1016/j.omtm.2017.05.009Test
https://doaj.org/article/391415b4d80b4db49263e27fbcc2640aTest