المؤلفون: Piera Smeriglio, Paul Langard, Giorgia Querin, Maria Grazia Biferi

المصدر: Journal of Personalized Medicine; Volume 10; Issue 3; Pages: 75

مصطلحات موضوعية: spinal muscular atrophy, adult patients, disease heterogeneity, Nusinersen, disease modifiers, functional outcomes, biomarkers, epigenetic changes, omics approaches

وصف الملف: application/pdf

العلاقة: Omics/Informatics; https://dx.doi.org/10.3390/jpm10030075Test

الإتاحة: https://doi.org/10.3390/jpm10030075Test

المؤلفون: Marisa Cappella, Chiara Ciotti, Mathilde Cohen-Tannoudji, Maria Grazia Biferi

المصدر: International Journal of Molecular Sciences; Volume 20; Issue 18; Pages: 4388

مصطلحات موضوعية: Gene therapy, antisense oligonucleotides, RNA interference, lentiviral vectors, AAV

جغرافية الموضوع: agris

وصف الملف: application/pdf

العلاقة: Molecular Pathology, Diagnostics, and Therapeutics; https://dx.doi.org/10.3390/ijms20184388Test

الإتاحة: https://doi.org/10.3390/ijms20184388Test